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Clinical Trials on Aromatic Amino Acid Decarboxylase Deficiency
Total 554 results
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The University of Texas Medical Branch, GalvestonTerminated
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Boston Children's HospitalBioMarin PharmaceuticalCompleted
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NestléWithdrawn
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Universidade do PortoBioMarin Pharmaceutical; Centro Hospitalar do PortoCompleted
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University of British ColumbiaVitaflo International, LtdUnknown
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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Nutricia UK LtdWithdrawn
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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University of Wisconsin, MadisonBoston Children's HospitalCompletedPhenylketonuriaUnited States
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BioMarin PharmaceuticalTerminatedPhenylketonuriaItaly, Switzerland
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Emory UniversityBioMarin Pharmaceutical; Atlanta Clinical and Translational Science InstituteCompletedPhenylketonuriaUnited States
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Children's National Research InstituteGeorgetown UniversityWithdrawn
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Oregon Health and Science UniversityTerminated
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Merck KGaA, Darmstadt, GermanySmerud Medical Research International AS; Merck Serono NorwayCompleted
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BioMarin PharmaceuticalCompletedStudy of Phenoptin in Subjects With Phenylketonuria Who Participated in Protocols PKU-004 or PKU-006PhenylketonuriaUnited States
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The Kennedy Institute-National Eye ClinicSygekassernes HelsefondCompleted
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National Taiwan University HospitalUnknown
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BioMarin PharmaceuticalRecruitingPhenylketonuria (PKU)United States
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Shanghai Vitalgen BioPharma Co., Ltd.RecruitingGlutaric Acidemia Type I | Glutaric Aciduria Type IChina
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Guy's and St Thomas' NHS Foundation TrustUnknownCardiovascular Diseases | PhenylketonuriasUnited Kingdom
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Nutricia UK LtdCompletedPhenylketonurias | Hyperphenylalaninaemia, Type IUnited Kingdom
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University of Southern CaliforniaBioMarin PharmaceuticalCompleted
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Stanford UniversityBioMarin PharmaceuticalWithdrawnClassical Phenylketonuria(PKU)
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Karolinska InstitutetMidsona AB; Forskningsrådet för arbetsliv och socialvetenskap, FASCompletedOverweight and Obesity | Lifestyle-related Condition | Essential Fatty Acid DeficiencySweden
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BioMarin PharmaceuticalActive, not recruitingPhenylketonuria (PKU)United States, Germany
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BioMarin PharmaceuticalCompletedPhenylketonuria (PKU)United States
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BioMarin PharmaceuticalCompletedPhenylketonuria (PKU)United States
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University of British ColumbiaRare Disease Foundation, Vancouver, CanadaCompleted
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Brendan LeeCompleted
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University of GlasgowUnknownPhenylketonuria (PKU)United Kingdom
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University Hospital, ToursInstitut National de la Santé Et de la Recherche Médicale, FranceCompletedPKU | HyperphenylalaninemiaFrance
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Dr. Linda RandolphBioMarin PharmaceuticalTerminated
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National Institute of Allergy and Infectious Diseases...National Center for Advancing Translational Sciences (NCATS); Office of Rare... and other collaboratorsEnrolling by invitationOmenn Syndrome | Reticular Dysgenesis | Severe Combined Immunodeficiency (SCID) | XSCID | Leaky SCID | ADA SCIDUnited States, Canada
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Hydrocephalus and Neuroscience InstituteCompletedFolic Acid Deficiency | Neural Tube Defects | Spina Bifida | Anencephaly-Spina BifidaUnited States
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BioMarin PharmaceuticalRecruitingPhenylketonuria (PKU)United States, Germany, Italy
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Nutricia ResearchCompleted
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BioMarin PharmaceuticalActive, not recruiting
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BioMarin PharmaceuticalCompletedPhenylketonuria (PKU)United States, Turkey, Canada, France, Germany, Italy, United Kingdom
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Sutphin DrugsUnknownHereditary Tyrosinemia, Type IIndia
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Charite University, Berlin, GermanyJohannes Gutenberg University MainzCompletedPhenylketonuria | Endothelial Dysfunction
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Washington University School of MedicineUniversity of Missouri-Columbia; Northwestern University; Oregon Health and Science... and other collaboratorsTerminated
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Institut PasteurUniversity of Copenhagen; Institut CochinCompletedDiarrhea | InfantileFrance, New Caledonia, Central African Republic
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The Cleveland ClinicWithdrawnSeptic Shock | Shock, Septic | Lactic Acidosis | Thiamine DeficiencyUnited States
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University Children's Hospital, ZurichRecruitingUrea Cycle DisordersSwitzerland
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Center Trials & TreatmentOleg MartynenkoTerminatedCOVID-19 | SARS-CoV-2 | Furin | RGMc Processing | Paired Basic Amino Acid Cleaving Enzyme (PACE)India, United States, Ukraine
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University Hospital, ToursCompletedAdult Phenylketonuria Non Treated PatientsFrance
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Swedish Orphan BiovitrumCompletedHereditary Tyrosinemia, Type IBelgium, Denmark, France, Germany, Austria, Czechia, Finland, Hungary, Ireland, Italy, Netherlands, Norway, Poland, Portugal, Spain, Sweden, United Kingdom
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Cycle Pharmaceuticals Ltd.ParexelCompletedHereditary Tyrosinemia, Type ISouth Africa