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Clinical Trials on Ataxias, Hereditary
Total 3001 results
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S. Andrea HospitalAgenzia Italiana del FarmacoCompleted
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Neurophth Therapeutics IncRecruitingLeber Hereditary Optic Neuropathy (LHON)China, United States
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Wuhan Neurophth Biotechnology Limited CompanyRecruitingLeber's Hereditary Optic Neuropathy (LHON)China
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Medical College of WisconsinTerminatedLeber's Hereditary Optic Neuropathy (LHON)United States
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University Hospital, AngersUnknownLeber Hereditary Optic NeuropathyFrance
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Hugo W. Moser Research Institute at Kennedy Krieger...RecruitingLeukoencephalopathies | Genetic Disease | White Matter Disease | Ataxia, Cerebellar | LBSL | Leukoencephalopathy With Brainstem and Spinal Cord Involvement and Lactate ElevationUnited States
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Seoul National University HospitalCompletedEye Diseases | Retinal Degeneration | Retinal Diseases | Retinitis Pigmentosa | Eye Disease, HereditaryKorea, Republic of
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EuroBloodNet AssociationNot yet recruitingHereditary Red Blood Cell Disorder (Disorder)Denmark, Netherlands
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Applied Therapeutics, Inc.Active, not recruitingHereditary Neuropathy Caused by SORD DeficiencyUnited States, United Kingdom, Czechia, Italy
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Currax PharmaceuticalsHenry Ford HospitalCompleted
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Augusta UniversityTerminatedDyssynergiaUnited States
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Netherlands Institute for Innovative Ocular SurgeryAmnitrans Eyebank Rotterdam; Melles CorneaClinic RotterdamCompletedCorneal Dystrophies, HereditaryNetherlands
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Hospital de Olhos Sadalla Amin GhanemCompletedEye Diseases, Hereditary
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Netherlands Institute for Innovative Ocular SurgeryAmnitrans Eyebank RotterdamCompletedCorneal Dystrophies, HereditaryNetherlands
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University of California, San FranciscoUniversity of California, Berkeley; University of Wisconsin, Madison; National...Recruiting
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HAE Global Registry FoundationRecruitingHereditary Angioedema Type I and IIItaly
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KalVista Pharmaceuticals, Ltd.CompletedHereditary AngioedemaUnited States, Austria, Czechia, Germany, Hungary, Italy, Netherlands, North Macedonia, Poland, United Kingdom
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Bin LiHuazhong University of Science and TechnologyCompletedLeber Hereditary Optic NeuropathyChina
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Prothya BiosolutionsCompletedHereditary Angioedema Type I | Angioneurotic EdemaNetherlands
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Wolfson Medical CenterUnknown
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Hacettepe UniversityCompleted
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University Hospital, Clermont-FerrandRecruitingHereditary DysfibrinogenemiaFrance
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Alder Hey Children's NHS Foundation TrustUnknownAtaxia | Posterior Fossa TumorUnited Kingdom
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Hospices Civils de LyonNot yet recruitingAtaxia | Genetic Disease | Degenerative DiseaseFrance
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Massachusetts General HospitalCompletedHereditary Sensory and Autonomic Neuropathy Type IUnited States
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Centre Hospitalier Régional Metz-ThionvilleCompleted
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Price Vision GroupTerminatedFuchs' Endothelial DystrophyUnited States
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Singapore National Eye CentreUnknownFuchs' Endothelial DystrophySingapore
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Medical University of ViennaRecruiting
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Santhera PharmaceuticalsWithdrawnLeber's Hereditary Optic Neuropathy
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Massachusetts Eye and Ear InfirmaryCompletedFuchs' Endothelial DystrophyUnited States
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University of AarhusActive, not recruitingFuchs' Endothelial DystrophyDenmark
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Maastricht University Medical CenterZonMw: The Netherlands Organisation for Health Research and DevelopmentCompleted
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Oregon Health and Science UniversityTerminated
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National Taiwan University HospitalTerminatedMultiple System Atrophy | Ataxia, CerebellarTaiwan
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Santhera PharmaceuticalsNo longer availableLeber's Hereditary Optic Neuropathy
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Stealth BioTherapeutics Inc.CompletedLeber's Hereditary Optic NeuropathyUnited States
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Institut National de la Santé Et de la Recherche...UnknownAutoinflammatory Diseases, Hereditary
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Johns Hopkins UniversityRecruitingGranular Dystrophy, CornealUnited States
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Weill Medical College of Cornell UniversityRecruitingGynecologic Cancer | Hereditary Cancer SyndromeUnited States
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University Eye Hospital, FreiburgCompletedFuchs' Endothelial DystrophyGermany
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Argo SanteGenSight BiologicsCompleted
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Byron LamNational Eye Institute (NEI)Active, not recruitingLeber's Hereditary Optic NeuropathyUnited States
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Santhera PharmaceuticalsCompletedLeber's Hereditary Optic NeuropathyCanada, Germany, United Kingdom
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National Eye Institute (NEI)CompletedCorneal Dystrophies, Hereditary | Corneal DiseaseUnited States, China, Italy
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Hospices Civils de LyonUnknownAutoimmune Encephalitis | Imbic Encephalitis | Autoimmune Cerebellar Ataxia | Stiff-person SyndromeFrance
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Boston Children's HospitalCureAP4 FoundationRecruitingHereditary Spastic Paraplegia | SPG50 | SPG47 | SPG51 | SPG52 | AP4-related Hereditary Spastic Paraplegia | Early Onset Hereditary Spastic Paraplegia | SPG4 | SPG3A | SPG15 | SPG11United States
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Poznan University of Physical EducationCompletedAging Problems | Coordination ImpairmentPoland
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The Opole University of TechnologyCompletedVirtual Reality | Coordination ImpairmentPoland
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Moser, HeleneUnknownPelvic Floor DyssynergiaSwitzerland