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Clinical Trials on Atrofia muscular espinal tipo 2
Total 1513 results
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Institut de Myologie, FranceCompletedSpinal Muscular Atrophy
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WestatNational Institute of Neurological Disorders and Stroke (NINDS)TerminatedSpinal Muscular Atrophy Type IUnited States
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Vastra Gotaland RegionNot yet recruitingPulmonary Atresia With Intact Ventricular Septum
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Kun SunRecruitingSpinal Muscular Atrophy 1China
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Institut de Myologie, FranceRoche Pharma AGNot yet recruitingMuscular Atrophy, Spinal, Type II | Muscular Atrophy, Spinal, Type IIIFrance
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Novartis Gene TherapiesCompletedSpinal Muscular Atrophy 1United States
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Stanford UniversityCompletedMuscular Atrophy, SpinalUnited States
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Assistance Publique - Hôpitaux de ParisCompleted
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Meshalkin Research Institute of Pathology of CirculationCompletedPulmonary Atresia With Ventricular Septal Defect | Tetralogy of Fallot With Pulmonary AtresiaRussian Federation
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Centre Hospitalier Régional de la CitadelleCompletedSafety and Efficacy Study of Pyridostigmine on Patients With Spinal Muscular Atrophy Type 3 (EMOTAS)Spinal Muscular Atrophy Type 3Belgium
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Novartis Gene TherapiesPRA Health SciencesCompletedSpinal Muscular Atrophy Type IKorea, Republic of, Taiwan, Japan
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Stanford UniversityCompletedA Pilot Therapeutic Trial Using Hydroxyurea in Type II and Type III Spinal Muscular Atrophy PatientsMuscular Atrophy, SpinalUnited States
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University of UtahLeadiant Biosciences, Inc.; Families of Spinal Muscular AtrophyCompletedSpinal Muscular Atrophy Type IUnited States, Canada, Germany
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Columbia UniversityMuscular Dystrophy Association; Stevens Institute of TechnologyCompletedDuchenne Muscular Dystrophy | Spinal Muscular Atrophy Type 3United States
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Columbia UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedSpinal Muscular Atrophy Type 3 | Mitochondrial MyopathyUnited States
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Kaohsiung Medical University Chung-Ho Memorial...National Taiwan University Hospital; Mackay Memorial Hospital; Shin Kong Wu Ho-Su... and other collaboratorsCompletedNatural History of Type 1 Spinal Muscular Atrophy (SMA)
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Novartis PharmaceuticalsRecruitingSpinal Muscular Atrophy (SMA)Spain, Canada, Taiwan, Belgium, Malaysia, China, Japan, Italy, Singapore, United Kingdom, France, Australia, Thailand, Denmark, United States
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Hoffmann-La RocheCompletedHealthy Volunteer, Muscular Atrophy, SpinalSwitzerland
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Gillette Children's Specialty HealthcareCompletedCerebral Palsy | Muscular Dystrophy | Osteopenia | Rett Syndrome | Spinal Muscular Atrophy | Spina BifidaUnited States
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Moens MaartenVrije Universiteit BrusselRecruitingSpinal Cord Stimulation | Persistent Spinal Pain Syndrome Type 2Belgium
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University of Erlangen-Nürnberg Medical SchoolCompletedMuscular Diseases | Spinal Muscular AtrophyGermany
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University of Erlangen-Nürnberg Medical SchoolUnknownMuscular Diseases | Spinal Muscular AtrophyGermany
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MarsiBionicsFundacion para la Investigacion Biomedica del Hospital Universitario Ramon...CompletedSpinal Muscular Atrophy Type IISpain
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Alcyone Therapeutics, IncBiogenRecruitingScoliosis | Spinal Muscular Atrophy | Spine DeformityUnited States
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Holland Bloorview Kids Rehabilitation HospitalThe Hospital for Sick Children; University of Toronto; University of Ottawa; Social... and other collaboratorsCompletedCerebral Palsy | Muscular Dystrophy | Physical Disability | Spinal Cord Injury | Spina Bifida | Juvenile ArthritisCanada
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University of KansasCompletedStroke | Multiple Sclerosis | Cerebral Palsy | Arthritis | Muscular Dystrophy | Amputation | Spinal Cord Injury | Spina BifidaUnited States
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University Hospital, Strasbourg, FranceRecruitingFeasibility of Neonatal Screening for Spinal AmyotrophyFrance
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Emory UniversityCompletedPulmonary Valve Stenosis | Right Ventricle | Pulmonary Valve AtresiaUnited States
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LMU KlinikumCompletedHealthy | Myotonic Dystrophy Type 2 | Pompe Disease (Late-onset) | Spinal Muscular Atrophy Type 3 | Myotonic Dystrophy Type 1 (DM1) | Facioscapulohumeral Muscular Dystrophy 1 | Inclusion Body Myositis, SporadicGermany
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Hospices Civils de LyonNot yet recruitingSpinal Muscular AtrophyFrance
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Hoffmann-La RocheRecruiting
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingSpinal Muscular AtrophyItaly
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First Affiliated Hospital of Fujian Medical UniversityPeking Union Medical College Hospital; Fujian Medical University Union HospitalRecruiting
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Mahidol UniversityRecruitingSpinal Muscular AtrophyThailand
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Assistance Publique - Hôpitaux de ParisRecruitingSpinal Muscular AtrophyFrance
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Assistance Publique - Hôpitaux de ParisRecruiting
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Hoffmann-La RocheActive, not recruitingSpinal Muscular AtrophyBelgium, United States, United Kingdom, France, Poland, Italy, Switzerland, Netherlands, Germany
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Centre Hospitalier Universitaire de LiegeQueen Fabiola Children's University Hospital; Erasme University Hospital; Centre... and other collaboratorsActive, not recruiting
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Hoffmann-La RocheCompletedMuscular Atrophy, SpinalBelgium, United States, China, Spain, Japan, Canada, France, Poland, Brazil, Croatia, Italy, Russian Federation, Turkey, Germany, Serbia, United Kingdom
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Centre Hospitalier Universitaire de NiceActive, not recruitingSpinal Muscular AtrophyFrance
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BiogenCompletedSpinal Muscular AtrophyUnited States, Spain, Germany, United Kingdom, Australia, Japan, Canada, Belgium, France, Hong Kong, Italy, Korea, Republic of, Sweden, Turkey
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Novartis PharmaceuticalsCompleted
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BiogenActive, not recruitingMuscular Atrophy, SpinalUnited States, Spain, Germany, Italy, Israel
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Novartis PharmaceuticalsCompletedSpinal Muscular AtrophyBelgium, Germany, Italy, Russian Federation, Poland, Bulgaria, Denmark
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NYU Langone HealthWinthrop University HospitalWithdrawnSpinal Muscular AtrophyUnited States
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Catalyst Pharmaceuticals, Inc.CompletedMuscular Atrophy, SpinalItaly
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BiogenCompleted