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Clinical Trials on Atrophie musculaire spinale avec détresse respiratoire 1
Total 512 results
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Istanbul Medipol University HospitalActive, not recruitingMuscular Atrophy, SpinalTurkey
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University of UtahAbbott; Leadiant Biosciences, Inc.; Families of Spinal Muscular AtrophyCompletedSpinal Muscular AtrophyUnited States
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Columbia UniversityThe Spinal Muscular Atrophy FoundationCompleted
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University Medical Centre LjubljanaCompleted
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Ohio State UniversityBiogen; Cure SMACompleted
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Institut de Myologie, FranceCompletedSpinal Muscular AtrophyFrance
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Centre Hospitalier Régional de la CitadelleRoche Pharma AG; Biogen; AveXis, Inc.; Association Belge contre les Maladies neuro...CompletedSpinal Muscular AtrophyBelgium
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BiogenCompletedSpinal Muscular AtrophyUnited States
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BiogenCompletedSpinal Muscular AtrophyUnited States, Canada
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BiogenTerminatedSpinal Muscular AtrophyKorea, Republic of, United States, Spain, Canada, Germany, Australia, Japan, Sweden, Belgium, France, Italy, Turkey, United Kingdom
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BiogenTerminatedSpinal Muscular AtrophyUnited States, Germany
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United BioSource, LLCAveXis, Inc.Approved for marketing
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National Institute of Neurological Disorders and...Terminated
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Hoffmann-La RocheCompletedMuscular Atrophy, SpinalBelgium, United Kingdom, Germany, France, Italy, Netherlands, Poland
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University of Texas Southwestern Medical CenterCompleted
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Hoffmann-La RocheTerminatedMuscular Atrophy, SpinalFrance, Turkey, Canada, United States, Italy, Netherlands, Sweden, Switzerland, United Kingdom
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National Taiwan University HospitalCompleted
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University of UtahEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedSpinal Muscular AtrophyUnited States
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University of UtahAbbott; Leadiant Biosciences, Inc.; Families of Spinal Muscular AtrophyCompletedSpinal Muscular AtrophyUnited States, Canada
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University of Sao Paulo General HospitalCompletedSpinal Muscular AtrophyBrazil
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National Taiwan University HospitalUnknown
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National Taiwan University HospitalNational Science Council, TaiwanUnknownSpinal Muscular Atrophy | Spinal Cord Injury | MyelomeningoceleTaiwan
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Columbia UniversityGenentech, Inc.RecruitingSpinal Muscular AtrophyUnited States
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Biohaven Pharmaceuticals, Inc.Active, not recruitingNeuromuscular Diseases | Spinal Muscular Atrophy | SMAUnited States, Netherlands, United Kingdom, Spain, Czechia, Belgium, Germany, Italy, Poland
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Novartis Gene TherapiesTerminatedSpinal Muscular AtrophyUnited States
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Novartis Gene TherapiesCompletedSMAFrance, United Kingdom, Italy, Belgium
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Ankara City Hospital BilkentCompletedAnesthesia | Child, Only | Muscular Atrophy, SpinalTurkey
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IRCCS Burlo GarofoloRecruiting
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BiogenCompletedSpinal Muscular AtrophyGermany
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Centre d'Investigation Clinique et Technologique...CompletedSpinal Muscular Atrophy | Assessment, SelfFrance
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Columbia UniversityCompletedSpinal Muscular Atrophy | Neuromuscular DiseaseUnited States
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University Hospital, Strasbourg, FranceRecruitingFeasibility of Neonatal Screening for Spinal AmyotrophyFrance
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Charles University, Czech RepublicRecruiting
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Ain Shams UniversityUnknownMuscular Dystrophy | Polyneuropathies | Spinal Muscular Atrophy | Muscle Diseases | Myasthenic SyndromesEgypt
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CHU de ReimsRecruitingSpinal Muscular AtrophyFrance
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Grand Valley State UniversityActive, not recruitingCerebral Palsy | Spinal Cord Injuries | Spinal Muscular Atrophy | Genetic Disease | Spina Bifida | Development DelayUnited States
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Istanbul Medipol University HospitalEnrolling by invitationSpinal Muscular Atrophy | Muscle Tone PoorTurkey
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Massachusetts General HospitalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsUnknownSpinal Muscular AtrophyUnited States
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Newcastle UniversityRoche Pharma AG; Biogen; Adult SMA REACH; SMA REACH UKRecruiting
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Great Ormond Street Hospital for Children NHS Foundation...CompletedSpinal Muscular AtrophyUnited Kingdom
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National Institute of Neurological Disorders and...CompletedMotor Neuron Disease | Spinal and Bulbar Muscular Atrophy (SBMA)United States
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Nemours Children's ClinicCompleted
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Marmara UniversityCompletedCaregiver Burden | Spinal Muscular AtrophyTurkey
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Hospices Civils de LyonRecruitingSpinal Muscular AtrophyFrance
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University of GiessenRecruitingSpinal Muscular AtrophyGermany
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All India Institute of Medical Sciences, New DelhiRecruiting
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Novartis PharmaceuticalsCompletedMuscular Atrophy, SpinalBrazil, Argentina
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Istanbul Medipol University HospitalEnrolling by invitationQuality of Life | Neuromuscular Diseases | Spinal Muscular Atrophy | Pediatric DisorderTurkey
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Gianni SoraruMario Negri Institute for Pharmacological ResearchRecruitingSpinal and Bulbar Muscular AtrophyItaly
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Novartis PharmaceuticalsActive, not recruitingSpinal Muscular AtrophyJapan, Belgium, Spain, Canada, United States, Australia, Italy, France, Netherlands