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Clinical Trials on Atrophie musculaire spinale avec détresse respiratoire 1
Total 512 results
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Milton S. Hershey Medical CenterBioSensicsNot yet recruitingAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Progressive Muscular Atrophy
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IRCCS Eugenio MedeaRecruiting
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Oslo University HospitalUniversity of Oslo; Haukeland University HospitalRecruitingMyotonic Dystrophy 1Norway
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Université de SherbrookeRare Disease FoundationCompletedMyotonic Dystrophy 1Canada
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LMU KlinikumCompleted
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Cynthia GagnonFondation du Grand défi Pierre LavoieCompletedEffects of a Multiple Component Training Program on Muscles in Adults With Myotonic Dystrophy Type 1Myotonic Dystrophy 1Canada
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Avidity Biosciences, Inc.Active, not recruitingNervous System Diseases | Genetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Neurodegenerative Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Heredodegenerative Disorders, Nervous System | Myotonic Dystrophy | Myotonic Disorders | Myotonic Dystrophy... and other conditionsUnited States
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Centre Hospitalier Universitaire de NiceRecruitingType 1 Facioscapulohumeral Muscular DystrophyFrance
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Duke UniversityCReATe Consortium (funded by NIH/NCATS/NINDS)CompletedAmyotrophic Lateral Sclerosis | Progressive Muscular AtrophyUnited States
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Vertex Pharmaceuticals IncorporatedRecruitingMyotonic Dystrophy Type 1 (DM1)United Kingdom, Canada, Australia
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Dyne TherapeuticsRecruitingMyotonic Dystrophy Type 1 (DM1)United Kingdom, France, Netherlands, Italy, Germany, New Zealand
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University of OklahomaCompletedCerebral Palsy | Spinal Muscular Atrophy | Arthrogryposis | Other Central Nervous System or Musculoskeletal DisordersUnited States
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Université du Québec à ChicoutimiRecruitingMyotonic Dystrophy Type 1 (DM1)Canada
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Ning Wang, MD., PhD.Recruiting
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University of OsloOslo University Hospital; Vikersund Rehabilitation CenterCompletedMyotonic Dystrophy Type 1 (DM1)Norway
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Expansion Therapeutics, Inc.CompletedMyotonic Dystrophy | Myotonic Dystrophy, Type 1 (DM1)United States
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Massachusetts General HospitalNorthwestern University; University of Florida; University of Minnesota; Henry... and other collaboratorsRecruitingALS | Kennedy Disease | MND (Motor Neurone DIsease) | PLS | PMA - Progressive Muscular Atrophy | PBP - Progressive Bulbar PalsyUnited States, Italy
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Duke UniversityUCB PharmaCompletedMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Progressive Muscular AtrophyUnited States
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University of AlbertaMcGill University; University of Toronto; Laval University; Simon Fraser UniversityRecruitingAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Frontotemporal Degeneration | Progressive Muscular AtrophyCanada
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Lupin Ltd.WithdrawnMyotonic Dystrophy Type 1 and Type 2
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Children's Healthcare of AtlantaWithdrawnScoliosis | Duchenne's Muscular DystrophyUnited States
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University of MiamiFloridaRecruitingInsulin Resistance | Spinal Cord Injuries | Tetraplegia | Muscle Loss | Paraplegia | Atrophy, MuscularUnited States
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CENTOGENE GmbH RostockCompletedScoliosis | Muscular Atrophy | Duchenne Muscular Dystrophy | Lordosis | Muscular Weakness | Increased Lordosis/Scoliosis | Hyporeflexia | Red-Green Color BlindnessEgypt, India, Albania, Pakistan, Georgia, Lebanon, Romania, Sri Lanka
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LMU KlinikumRecruitingPompe Disease (Late-onset) | FSHD | Spinal Muscular Atrophy Type 3 | Inclusion Body MyositisGermany
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University of Sao Paulo General HospitalAgência Brasileira de Desenvolvimento Industrial (Brazilian Agency For Industrial...Not yet recruitingBrain Injuries | Spinal Cord Injuries | Muscle AtrophyBrazil
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Thomas Jefferson UniversityRecruitingStroke | Cerebral Palsy | Amyotrophic Lateral Sclerosis | Muscular Dystrophies | Spinal Cord Injuries | Hemiparesis | Spinal Muscular Atrophy | Quadriplegia | Arthrogryposis | Neurologic Diseases | Charcot-Marie-Tooth | Weakness of Extremities as Sequela of Stroke | Weakness Due to Upper Motor Neuron Dysfunction | Arm ParalysisUnited States
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Assistance Publique - Hôpitaux de ParisAssociation Française contre les Myopathies (AFM), ParisUnknownRespiratory Insufficiency | Myopathy | Muscular WeaknessFrance
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Stem Cells ArabiaUnknownMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Progressive Muscular Atrophy | Progressive Bulbar Palsies
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Ohio State UniversityGilead SciencesCompletedMyotonic Dystrophy 1 | Myotonia Congenita | Paramyotonia CongenitaUnited States
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National Institute of Respiratory Diseases, MexicoUnknownMyotonic Dystrophy 1 | Steinert DiseaseMexico
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National Institute of Neurological Disorders and...TerminatedMyotonic Dystrophy Type-1 | Myotonic Dystrophy Type-2United States
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IRCCS San Camillo, Venezia, ItalyCompletedMyotonic Dystrophy Type 1 (DM1)
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Johns Hopkins UniversityMassachusetts General Hospital; Washington University School of Medicine; Emory... and other collaboratorsCompletedMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Progressive Muscular Atrophy | Healthy Controls | Flail Arm ALS | Monomelic Amyotrophy | Asymptomatic ALS Gene CarriersUnited States
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Myotonic Dystrophy FoundationRecruitingMyotonic Dystrophy | Myotonic Dystrophy 1 | Steinert's Disease | Congenital Myotonic Dystrophy | PROMM (Proximal Myotonic Myopathy) | Steinert Disease | Dystrophia Myotonica 1 | Myotonic Dystrophy 2 | Dystrophia Myotonica | Dystrophia Myotonica 2 | Myotonia Dystrophica | Myotonic Dystrophy, Congenital | Myotonic... and other conditionsUnited States
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McMaster UniversityNot yet recruiting
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Centre Hospitalier Universitaire de NiceWithdrawn
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AMO Pharma LimitedCompletedMyotonic Dystrophy 1United Kingdom
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Assistance Publique - Hôpitaux de ParisRecherche Clinique Paris Descartes Necker Cochin Sainte Anne; AFM-Téléthon...Recruiting
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ARTHEx Biotech S.L.Recruiting
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Arrowhead PharmaceuticalsRecruitingMyotonic Dystrophy 1New Zealand, Australia
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Istituto Auxologico ItalianoFondazione Serena Onlus - Centro Clinico NeMO MilanoCompletedMyotonic Dystrophy 1Italy
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University of Dublin, Trinity CollegeMotor Neurone Disease Association, UK; Irish Research Council, IE; Thierry Latran... and other collaboratorsRecruitingMultiple Sclerosis | Primary Lateral Sclerosis | Postpoliomyelitis Syndrome | Motor Neuron Disease, Amyotrophic Lateral Sclerosis | Motor Neuron Disease Progressive Spinal Muscle AtrophyIreland
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Huashan HospitalEnrolling by invitation
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Ohio State UniversityCompletedSpinal Cord Injuries | Metabolic Disease | Skeletal Muscle AtrophyUnited States
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Holland Bloorview Kids Rehabilitation HospitalThe Hospital for Sick Children; University of Toronto; University of Ottawa; Social... and other collaboratorsCompletedCerebral Palsy | Muscular Dystrophy | Physical Disability | Spinal Cord Injury | Spina Bifida | Juvenile ArthritisCanada
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Massachusetts General HospitalRecruiting
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University of KansasCompletedStroke | Multiple Sclerosis | Cerebral Palsy | Arthritis | Muscular Dystrophy | Amputation | Spinal Cord Injury | Spina BifidaUnited States
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Ionis Pharmaceuticals, Inc.CompletedMyotonic Dystrophy Type 1United States
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Newcastle-upon-Tyne Hospitals NHS TrustCompletedMyotonic Dystrophy Type 1United Kingdom
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University of RochesterCompletedMyotonic DystrophyUnited States