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Clinical Trials on Autosomal Recessive Degenerative and Progressive Cerebellar Ataxia
Total 610 results
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Medical University of ViennaUniversity of Zurich; Centre Hospitalier Universitaire Dijon; Fundacion Clinic... and other collaboratorsNot yet recruiting
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CSL BehringCompletedCommon Variable Immunodeficiency | X-linked Agammaglobulinemia | Autosomal Recessive AgammaglobulinemiaGermany, United Kingdom, France, Italy, Poland, Romania, Spain, Sweden, Switzerland
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National Medical Research Center for Therapy and...Moscow State University of Medicine and DentistryRecruitingMedication Adherence | Adherence, Medication | Treatment Adherence | Familial Hypercholesterolemia | Motivational Interviewing | Adherence, Patient | Treatment Adherence and Compliance | Patient Compliance | Adherence | Hypercholesterolemia, Familial | Patient Adherence | Hypercholesterolemia, Autosomal Dominant and other conditionsRussian Federation
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University Hospital, AntwerpHasselt University; University Hospital, Ghent; AZ Sint-Jan AV; National MS Center... and other collaboratorsRecruitingMultiple Sclerosis | Primary Progressive Multiple Sclerosis | Secondary-progressive Multiple SclerosisBelgium
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Kubota Vision Inc.Not yet recruitingMyopia | Vision Disorders | Myopia, Progressive
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University of Texas at AustinUniversity of California, San Francisco; National Institute on Deafness and...Active, not recruitingPrimary Progressive Aphasia | Aphasia | Semantic Dementia | Logopenic Progressive Aphasia | Semantic Memory Disorder | Nonfluent Aphasia, Progressive | Aphasia, ProgressiveUnited States
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University of California, San FranciscoNational Institute of Neurological Disorders and Stroke (NINDS); National Center... and other collaboratorsCompletedAmyotrophic Lateral Sclerosis (ALS) | Progressive Supranuclear Palsy (PSP) | Corticobasal Degeneration (CBD) | FTLD | Frontotemporal Dementia (FTD) | PPA Syndrome | Behavioral Variant Frontotemporal Dementia (bvFTD) | Semantic Variant Primary Progressive Aphasia (svPPA) | Nonfluent Variant Primary Progressive... and other conditionsUnited States, Canada
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Johns Hopkins UniversityNational Institute on Aging (NIA)RecruitingPrimary Progressive Aphasia | Logopenic Progressive Aphasia | Non-Fluent Primary Progressive AphasiaUnited States, Canada
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University of PennsylvaniaUnited States Department of Defense; National Institutes of Health (NIH); National... and other collaboratorsRecruitingFrontotemporal Degeneration(FTD) | Primary Progressive Aphasia(PPA) | Familial Frontotemporal Lobar Degeneration (fFTLD) | Amyotrophic Lateral Sclerosis(ALS) | Lewy Body Disease(LBD) | Progressive Supranuclear Palsy(PSP) | Corticobasal Syndrome(CBS) | Posterior Cortical Atrophy(PCA) | Alzheimer's Disease(AD)United States
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University of Texas at AustinHospital Clinic of Barcelona; Fundació Institut de Recerca de l'Hospital de...RecruitingNeurocognitive Disorders | Neurodegenerative Diseases | Dementia | Alzheimer Disease | Language Disorders | Communication Disorders | Primary Progressive Aphasia | Aphasia | Speech Disorders | Frontotemporal Lobar Degeneration | Dysarthria | Apraxia, Motor | Dementia, Frontotemporal | Bilingual AphasiaSpain, United States
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University of California, San FranciscoTau Consortium; CBD SolutionsCompletedProgressive Supranuclear Palsy (PSP) | Corticobasal Degeneration (CBD) | Corticobasal Syndrome (CBS) | Primary Four Repeat Tauopathies (4RT)United States
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Medical University of ViennaUniversity of Zurich; Centre Hospitalier Universitaire Dijon; Fundacion Clinic... and other collaboratorsNot yet recruitingAge-Related Macular Degeneration | Geographic Atrophy
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H. Lee Moffitt Cancer Center and Research InstituteRecruitingLynch Syndrome | Pancreatic Ductal Adenocarcinoma | Chronic Pancreatitis | Pancreatic Cyst | Ataxia Telangiectasia | FAP | Peutz-Jeghers Syndrome | PALB2 Gene Mutation | BRCA Mutation | Fatty Pancreas | Genetic Pancreatic Cancer | Genetic Pancreatitis | Familial Atypical Multiple Mole-MelanomaUnited States
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Massachusetts General HospitalCompletedLogopenic Variant Primary Progressive Aphasia | Non-Fluent Primary Progressive AphasiaUnited States
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Clinic for Special ChildrenRecruitingMyopathy | Myopathy; Hereditary | Myopathies, Nemaline | TNNT1-associated Myopathy | Infantile-onset Nemaline Rod Myopathy | Myopathy, Rod | Amish Nemaline Myopathy | Nemaline Myopathy 5 | NEM5 | Genetic Muscle Disease | Recessive Hereditary Disorder (Autosomal) | ANMUnited States
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Association for Innovation and Biomedical Research...European Vision Institute Clinical Research NetworkActive, not recruitingAtrophy | Age Related Macular Degeneration | Prediction | Intermediate AMDPortugal, France, Germany, Ireland, Italy, Netherlands, Spain, Switzerland, United Kingdom
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Krystal Biotech, Inc.Active, not recruitingTGM-1 Related Autosomal Recessive Congenital IchthyosisUnited States
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National Institute of Mental Health (NIMH)CompletedAutism | Minocycline | Regressive AutismUnited States
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University of California, San FranciscoCompletedProgressive Supranuclear Palsy | Corticobasal Degeneration Syndrome | Progressive Nonfluent Aphasia | Predicted Tauopathies, Including | Frontotemporal Dementia With Parkinsonism Linked to Chromosome 17United States
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University of California, San FranciscoHalo NeuroscienceWithdrawnCorticobasal Degeneration | Progressive Supranuclear Palsy | Behavioral Variant of Frontotemporal Dementia | Primary Progressive Nonfluent Aphasia | Nonfluent Aphasia, Progressive | Primary Progressive Non Fluent Aphasia
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Assistance Publique - Hôpitaux de ParisNot yet recruitingAutosomal Recessive Congenital Ichthyosis | Epidermolytic IchthyosisFrance
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University of California, San FranciscoTerminatedNonfluent Aphasia, Progressive | Primary Tauopathies | Corticobasal Degeneration Syndrome | Frontotemporal Lobar Degeneration With Tau Inclusions | MAPT Mutation Carriers, Symptomatic | Traumatic Encephalopathy SyndromeUnited States
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University Hospital, MontpellierMinistry of Health, FranceCompletedAutosomal Dominant Retinitis PigmentosaFrance
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Massachusetts General HospitalNational Institute on Deafness and Other Communication Disorders (NIDCD)RecruitingLogopenic Variant Primary Progressive Aphasia | Non-fluent Variant Primary Progressive Aphasia | Semantic Variant Primary Progressive AphasiaUnited States
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Juan PascualNational Institute of Neurological Disorders and Stroke (NINDS)CompletedGlucose Metabolism Disorders | Epilepsy | Glucose Transporter Type 1 Deficiency Syndrome | Glut1 Deficiency Syndrome 1, Autosomal Recessive | Glucose Transporter Protein Type 1 Deficiency Syndrome | Glucose Transport Defect | GLUT1DS1United States
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University of Texas Southwestern Medical CenterNational Institute of Neurological Disorders and Stroke (NINDS)Active, not recruitingGlucose Metabolism Disorders | Epilepsy | Glucose Transporter Type 1 Deficiency Syndrome | Glut1 Deficiency Syndrome 1, Autosomal Recessive | Glucose Transporter Protein Type 1 Deficiency Syndrome | Glucose Transport Defect | GLUT1DS1United States
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Washington University School of MedicineAssociation of Frontotemporal Degeneration; Tau ConsortiumCompletedProgressive Supranuclear Palsy (PSP) | Corticobasal Degeneration (CBD) | Frontotemporal Dementia (FTD MAPT Mutation)United States
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Okuvision GmbHCompletedPrimary Open Angle Glaucoma | Retinal Vein Occlusion | Retinitis Pigmentosa | Retinal Artery Occlusion | Dry Age Related Macular Degeneration | Hereditary Macular Degeneration | Macula Off | Treated Retina Detachment | Non-Arthritic-Anterior-Ischemic Optic-Neuropathy | Hereditary Autosomal Dominant Optic... and other conditions
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University of ArkansasWithdrawnPancreatic Neoplasms | Colorectal Neoplasms, Hereditary Nonpolyposis | BRCA1 Gene Mutation | BRCA2 Gene Mutation | Hereditary Pancreatitis | Ataxia Telangiectasia | Peutz-Jegher's Syndrome | Familial Atypical Mole-Malignant Melanoma SyndromeUnited States
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University of ManitobaRecruitingLogopenic Progressive AphasiaCanada
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Johns Hopkins UniversityNational Institute on Aging (NIA)RecruitingPrimary Progressive Aphasia | Logopenic Progressive AphasiaUnited States
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University of PittsburghCompletedPulmonary Hypertension | Friedreich Ataxia | Iron-sulfur Cluster DeficiencyUnited States
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QLT Inc.CompletedRetinitis Pigmentosa (RP)Canada, Ireland
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Montreal Heart InstituteActive, not recruitingNeurodegenerative Diseases | Primary Progressive Aphasia | Semantic Dementia | Logopenic Progressive Aphasia | Non-fluent AphasiaCanada
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BaycrestCanadian Institutes of Health Research (CIHR)CompletedPrimary Progressive Aphasia | Semantic Dementia | Nonfluent Progressive AphasiaCanada
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ShireTerminatedRetinitis PigmentosaUnited States
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Jose Luis Urcelay SeguraUnknownAmyotrophic Lateral SclerosisSpain
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University of Colorado, DenverNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)CompletedPolycystic Kidney, Autosomal DominantUnited States
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Hugo W. Moser Research Institute at Kennedy Krieger...RecruitingNeurodegenerative Diseases | Ataxia | Cerebellar Ataxia | Leukodystrophy | Adrenomyeloneuropathy | LBSL | Leukoencephalopathy With Brainstem and Spinal Cord Involvement and Lactate Elevation | Leukoencephalopathy With Brain Stem and Spinal Cord Involvement and High Lactate Syndrome (Disorder)United States
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University of British ColumbiaTerminatedPrimary Progressive Nonfluent AphasiaCanada
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Axon Neuroscience SEUnknownPrimary Progressive Nonfluent AphasiaGermany
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Northwestern UniversityNational Institute on Aging (NIA)RecruitingPrimary Progressive Aphasia With Suspected Alzheimer's DiseaseUnited States
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University of California, San FranciscoNational Institutes of Health (NIH); National Institute on Aging (NIA)Active, not recruitingCorticobasal Degeneration | Progressive Supranuclear PalsyUnited States
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Avid RadiopharmaceuticalsCompletedCorticobasal Degeneration | Progressive Supranuclear PalsyUnited States
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Amoneta Diagnostics SASAssistance Publique - Hôpitaux de Paris; University Hospital, Geneva; University... and other collaboratorsUnknownFrontotemporal Lobar Degeneration | Progressive Supranuclear Palsy (PSP) | Dementia With Lewy Bodies (DLB) | Corticobasal Degeneration (CBD) | Alzheimer Disease (AD) | Parkinson Disease Dementia (PDD)Belgium, France, Italy, Switzerland, Turkey
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Johns Hopkins UniversityNational Institutes of Health (NIH); National Institute on Deafness and Other...CompletedPrimary Progressive Aphasia | MCI | FTDUnited States
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University of Texas at AustinUniversity of California, San FranciscoActive, not recruitingPrimary Progressive AphasiaUnited States
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Johns Hopkins UniversityCompletedPrimary Progressive Aphasia | PPAUnited States
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Hospital San Carlos, MadridUniversidad Complutense de MadridCompleted
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Assistance Publique - Hôpitaux de ParisUnknown