- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Barth Syndrome
Total 55517 results
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Drexel UniversityJohns Hopkins University; National Institute on Aging (NIA); University of California...Active, not recruitingDementia | Alzheimer Disease | Frontotemporal Dementia | Vascular Dementia | Dementia With Lewy Bodies | Caregiver Stress Syndrome | Caregiver BurnoutUnited States
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ShionogiCompletedSepsis | Gram-negative Bacterial Infections | Bloodstream Infections (BSI) | Complicated Intra-abdominal Infection (cIAI) | Hospital Acquired Pneumonia (HAP) | Ventilator-acquired Pneumonia | Complicated Urinary Tract Infection (cUTI)Spain, Belgium, Latvia, Russian Federation, Estonia, Georgia, Hungary, Thailand, Ukraine
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O'Dorisio, M SNational Cancer Institute (NCI)CompletedSarcoma | Unspecified Childhood Solid Tumor, Protocol Specific | Brain and Central Nervous System Tumors | Neuroblastoma | Pheochromocytoma | Islet Cell Tumor | Gastrointestinal Carcinoid TumorUnited States
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Northwestern UniversityNational Cancer Institute (NCI)CompletedQuality of Life | Gastric Cancer | Colorectal Cancer | Small Intestine Cancer | Gastrointestinal Stromal Tumor | Constipation, Impaction, and Bowel Obstruction | Gastrointestinal Carcinoid TumorUnited States
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Adam KittaiRecruitingRecurrent Transformed Non-Hodgkin Lymphoma | Recurrent Transformed B-Cell Non-Hodgkin Lymphoma | Refractory Transformed Non-Hodgkin Lymphoma | Refractory Transformed B-cell Non-Hodgkin Lymphoma | Transformed Chronic Lymphocytic Leukemia to Diffuse Large B-Cell Lymphoma | Recurrent Transformed... and other conditionsUnited States
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Novartis PharmaceuticalsAvailablePrimary Myelofibrosis (PMF) | Polycythemia Vera (PV) | Post Polycythemia Myelofibrosis (PPV MF) | Thrombocythemia Myelofibrosis (PET-MF) | Severe/Very Severe COVID-19 Illness | Steroid Refractory Acute Graft Versus Host Disease (SR aGVHD) | Steroid Refractory Chronic Graft Versus Host Disease...
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University of California, San FranciscoNational Institutes of Health (NIH); National Institute on Aging (NIA)Active, not recruitingProgressive Supranuclear Palsy (PSP) | Corticobasal Degeneration (CBD) | Nonfluent Variant Primary Progressive Aphasia (nfvPPA) | Corticobasal Syndrome (CBS) | Cortical-basal Ganglionic Degeneration (CBGD) | Oligosymptomatic/Variant Progressive Supranuclear Palsy (o/vPSP)United States, Canada
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Centre Hospitalier Universitaire DijonUnknownHeart Failure | Multiple Sclerosis | Hemophilia | Chronic Respiratory Failure | Horton's Disease | Chronic Coronary Syndrome | AMD and Macular Edema | Malignant HemopathyFrance
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Prehospital Center, Region ZealandNot yet recruitingDrowning | Drowning; Anoxia | Drowning, Near | Drowning; Asphyxia | Drowning and Nonfatal Submersion | Drowning or Immersion of Unknown Intent | Drowning and Submersion, Undetermined Intent | Drowning and Submersion While in Bath-Tub | Drowning and Submersion While in Natural Water | Drowning and Submersion... and other conditionsDenmark
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Prehospital Center, Region ZealandNot yet recruitingDrowning | Drowning; Anoxia | Drowning, Near | Drowning; Asphyxia | Drowning or Immersion of Unknown Intent | Drowning and Submersion, Undetermined Intent | Drowning and Submersion While in Bath-Tub | Drowning and Submersion While in Natural Water | Drowning and Submersion Due to Sailboat Sinking | Drowning... and other conditionsDenmark
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Central Hospital, Nancy, FranceRecruiting
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University of CambridgeSanofiRecruiting
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Fundacion para la Investigacion Biomedica del Hospital...Fundación Mutua MadrileñaRecruiting
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Fondazione Don Carlo Gnocchi OnlusAssociazione Italiana Glicogenosi (AIG); Associazione Riabilitatori Insufficienza... and other collaboratorsRecruitingGlycogen Storage Disease Type II | Pompe Disease (Late-onset)Italy
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Lille Catholic UniversityVariant Bio, Inc.RecruitingRenal Insufficiency, Chronic | GoutNew Caledonia
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Assistance Publique - Hôpitaux de ParisRecruitingLung Diseases | Neuromuscular Diseases | Scoliosis | Congenital Diaphragmatic Hernia | Cardiac Diseases | Diaphragmatic Impairment | Respiratory Muscle ImpairmentFrance
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I.M. Sechenov First Moscow State Medical UniversityRecruitingVestibular Migraine | Meniere Disease | Vestibular Neuritis | Benign Paroxysmal Positional Vertigo (BPPV) | Central Positional VertigoRussian Federation
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Assistance Publique - Hôpitaux de ParisNot yet recruitingX-linked Hypophosphatemia (XLH)
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Baylor College of MedicineChildren's Hospital of Philadelphia; Children's Hospital Colorado; Seattle Children... and other collaboratorsRecruitingOrnithine Transcarbamylase Deficiency | Urea Cycle Disorder | Argininosuccinic Aciduria | Hyperargininemia | Citrullinemia 1 | ARGI Deficiency | ASL Deficiency | ASS DeficiencyUnited States
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyRecruitingEnd Stage Renal Disease | Primary Hyperoxaluria Type 2 | Primary Hyperoxaluria Type 1Germany, Spain, United States, United Kingdom, Italy, United Arab Emirates, Lebanon, Morocco, France, Romania
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University of Illinois at ChicagoGlobal Blood TherapeuticsRecruitingSickle Cell Disease | Sickle Cell NephropathyUnited States
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Centre Hospitalier National d'Ophtalmologie des...RecruitingStroke | Glaucoma | Hypertension | Diabetes | Retinal Degeneration | Macular Edema | Retinitis Pigmentosa | Trauma | Dry Eye | Keratoconus | Retinal Detachment | Corneal Dystrophy | Vascular Inflammation | Macular Dystrophy | Maculopathy, Age RelatedFrance
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University Hospital, AngersRecruiting
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University of Alabama at BirminghamMassachusetts General HospitalRecruitingCovid19 | Sinusitis | Cystic Fibrosis | COPD | PCD - Primary Ciliary DyskinesiaUnited States
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National Human Genome Research Institute (NHGRI)Enrolling by invitationParkinson Disease | Gaucher Disease | Lysosomal Storage DisordersUnited States
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Aesculap AGActive, not recruitingRheumatoid Arthritis | Hip Dysplasia | Fractures, Hip | Necrosis, Femur Head | Coxarthrosis; Primary | Coxarthrosis; Post-TraumaticGermany
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Centre Hospitalier Universitaire de NīmesCompletedStroke | Hemorrhage | Cerebral Amyloid AngiopathyFrance
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Haiyan WangCompletedEnd Stage Renal Disease | Arteriovenous FistulaChina
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Erasmus Medical CenterStichting TAAIActive, not recruitingLung Diseases | Cystic Fibrosis | Infections, Bacterial | Congenital Disorders | Lung Inflammation | Lung Infection | Lung Disease; Cystic | Lung Disease; Cystic, Congenital | Inflammation Lungs | Exacerbation, SymptomNetherlands
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Chiesi Farmaceutici S.p.A.Active, not recruitingFabry DiseaseBelgium, United States, United Kingdom, Italy, Czechia, Denmark, Norway
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Zimmer BiometTerminatedOsteoarthritis | Rheumatoid Arthritis | Avascular Necrosis | Femur Fracture | Trochanteric Fractures | Pseudarthrosis | Pseudoarthrosis | Functional Deformities | Revision of Endoprosthesis-treated Hips | Fracture, Proximal Humeral | Provision of Non-endoprosthetic Previous Operations of the Hip Joint (e.g... and other conditionsGermany
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Oslo University HospitalActive, not recruiting
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Assistance Publique - Hôpitaux de ParisShire International GmbHCompleted
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Kyowa Kirin Co., Ltd.CompletedX-linked Hypophosphatemic Rickets/OsteomalaciaJapan
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National Institute of Neurological Disorders and...CompletedMotor Neuron Disease | Spinal and Bulbar Muscular Atrophy (SBMA)United States
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Auburn UniversityCompletedAlzheimer Disease | Cerebral Amyloid AngiopathyUnited States
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UCB BIOSCIENCES, Inc.Syneos Health; ParexelTerminatedRheumatoid Arthritis (RA) | Crohn's Disease (CD) | Psoriatic Arthritis (PsA) | Axial Spondyloarthritis and Ankylosing SpondylitisUnited States
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Inozyme PharmaEngage Health Inc.; GACI GlobalCompletedGeneralized Arterial Calcification in Infancy | Autosomal Recessive Hypophosphatemic Rickets Type 2United States
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ShireTerminatedMetabolic Diseases | Brain Diseases | Central Nervous System Diseases | Nervous System Diseases | Demyelinating Diseases | Genetic Diseases, Inborn | Metabolism, Inborn Errors | Lysosomal Storage Diseases | Lipid Metabolism Disorders | Sphingolipidoses | Hereditary Central Nervous System Demyelinating Diseases and other conditionsUnited States, Denmark, France, Argentina, Belgium, Brazil, Canada, Germany, Japan, Turkey
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Children's Mercy Hospital Kansas CityCompletedHypophosphatemic Rickets, X-Linked DominantUnited States
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Universitaire Ziekenhuizen KU LeuvenCompletedDiabetes | Allergy | Chronic Kidney Disease | Cystic Fibrosis | Heart DiseaseBelgium
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University of FloridaWithdrawnDiabetes Mellitus | Hematologic Diseases | Cancer | Chronic Disease | Cystic Fibrosis | Narrative Medicine | Terminal Illness | Rheumatologic Disorder | Oncologic DisordersUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedChronic Kidney Disease | Sickle Cell Disease | Pulmonary HypertensionUnited States
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The George Washington University Biostatistics...Eunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedCerebral Palsy | Intraventricular Hemorrhage | Pulmonary Edema | Periventricular Leukomalacia | Abruptio PlacentaeUnited States
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NextGen Company LimitedMoscow State University of Medicine and Dentistry; Burnasyan Federal Medical...UnknownJaw Fractures | Alveolar Bone Atrophy | Maxillofacial Bone Defects | Maxillofacial Bone Deformities | Bone Neoplasm, Benign | Disorders of Teeth and JawRussian Federation
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Kyowa Kirin Co., Ltd.CompletedX-linked Hypophosphatemic Rickets/OsteomalaciaJapan, Korea, Republic of
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Charite University, Berlin, GermanyCompletedMigraine With Aura | CADASIL | Cerebral Microangiopathy | ICA StenosisGermany
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Mei changlinUnknownHypertension | Autosomal Dominant Polycystic Kidney DiseaseChina
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National MPS SocietyMediResource Inc.TerminatedMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidoses | Mucopolysaccharidosis VI | Mucopolysaccharidosis IVUnited States
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University Hospital, BordeauxCompletedPain | Fabry's DiseaseFrance