- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Barth Syndrome
Total 55699 results
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Kyowa Kirin, Inc.CompletedX-Linked HypophosphatemiaUnited States
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Kyowa Kirin Pharmaceutical Development LtdCompletedX-linked Hypophosphatemia (XLH)Sweden, Spain, United Kingdom, Italy, Austria, France
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Amicus TherapeuticsEngage Health Inc.CompletedFabry DiseaseUnited States
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VA Office of Research and DevelopmentCompletedChronic Kidney Diseases | GoutUnited States
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Karolinska University HospitalKarolinska InstitutetWithdrawnHepatitis B | Hepatitis A | Tuberculosis | Cystic FibrosisSweden
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Grand Valley State UniversityActive, not recruitingCerebral Palsy | Spinal Cord Injuries | Spinal Muscular Atrophy | Genetic Disease | Spina Bifida | Development DelayUnited States
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Erasme University HospitalCompletedArteriovenous Fistula | Aneurysmal Subarachnoid Hemorrhage | Vasospasm, Intracranial | Stenosis | Ruptured Cerebral Aneurysm | Arteriovenous Malformations, CerebralBelgium
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University Hospital, GhentUniversitaire Ziekenhuizen KU Leuven; University of Liege; Universitair Ziekenhuis... and other collaboratorsActive, not recruitingInfertility | Adhesion | Hysteroscopy | Myoma;Uterus | Uterine Septum | Polyp Uterus | Retained Products of ConceptionBelgium
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Mandos LLCTerminatedNiemann-Pick Type C DiseaseUnited States
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Tan Tock Seng HospitalCompletedPlantar Fasciitis | Achilles Tendinopathy | Insertional Achilles Tendinopathy | Metatarsalgia | Pes Cavus | Subtle Cavus Foot | Mechanical Foot Pains | Strain of Peroneal Tendon | Pes Cavus, Bilateral | Pes CavovarusSingapore
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Fresenius Medical Care Deutschland GmbHUniversity of Lisbon; Lisbon School of NursingCompletedChronic Kidney Diseases | Hemodialysis | Hemodialysis Access Failure | Arteriovenous Fistula | Vascular Access ComplicationPortugal
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Stanford UniversityNational Cancer Institute (NCI); Harvard UniversityCompletedCerebral Palsy | Childhood Cancer | Congenital Heart Disease | Chronic Lung Disease | Congenital Metabolic Disorder | GastrostomyUnited States
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Yale UniversityCompleted
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University Hospital, BordeauxCompletedChronic Pain | Fabry's DiseaseFrance
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Allena PharmaceuticalsTerminatedChronic Kidney Diseases | Hyperuricemia | GoutUnited States
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Alice MimsKaryopharm Therapeutics IncCompletedRecurrent Adult Acute Myeloid Leukemia | Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities | Adult Acute Myeloid Leukemia With Del(5q) | Adult Acute Myeloid Leukemia With Inv(16)(p13;q22) | Adult Acute Myeloid Leukemia With t(16;16)(p13;q22) | Adult Acute Myeloid Leukemia With t(8... and other conditionsUnited States
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Seoul National University HospitalColoplast A/SEnrolling by invitationUrinary Incontinence | Neurogenic Bowel | Fecal Incontinence | Neurogenic Bladder | Spina Bifida | Fecal ImpactionKorea, Republic of
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Centre Hospitalier Universitaire de NiceCompleted
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CENTOGENE GmbH RostockWithdrawnSplenomegaly | Hepatomegaly | Ceramidase Deficiency | Farber's LipogranulomatosisGermany, India, Egypt
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CENTOGENE GmbH RostockWithdrawnMuscle Weakness | Peripheral NeuropathyEgypt, Germany, India, Sri Lanka
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Onofre, Aurora Pujol, M.D.Completed
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SanofiApproved for marketing
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VenoStentActive, not recruitingVascular Diseases | Urologic Diseases | Chronic Kidney Diseases | Renal Insufficiency | Renal Failure | End Stage Renal Disease | Hemodialysis Access Failure | Fistula | Arteriovenous Malformations | Vascular Malformations | End Stage Kidney Disease | Arteriovenous Fistula | Renal Failure Chronic | Vascular Fistula | Catheter Complications and other conditionsParaguay
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisBrazil, France, Italy, United States, Germany, United Kingdom
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Idorsia Pharmaceuticals Ltd.CompletedGM2 Gangliosidosis | GM1 Gangliosidosis | Tay-Sachs Disease | Sandhoff Disease | Gaucher Disease, Type 2 | AB Variant Gangliosidosis GM2United States, Spain, Germany, Italy, Belgium, Brazil, France, Portugal, Switzerland, United Kingdom
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Cadent TherapeuticsWithdrawnSpinocerebellar Ataxia Type 3 | Spinocerebellar Ataxias | Spinocerebellar Ataxia Type 1 | Spinocerebellar Ataxia Type 2 | Spinocerebellar Ataxia Type 6 | Spinocerebellar Ataxia Type 10 | Spinocerebellar Ataxia Type 7 | Spinocerebellar Ataxia Type 8 | Spinocerebellar Ataxia Type 17 | ARCA1 - Autosomal Recessive...United States
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Beyond Air Inc.UnknownCystic Fibrosis | Mycobacterium Avium Complex | Non-Tuberculous Mycobacterial Pneumonia | Mycobacterial Pneumonia | Mycobacterium Abscessus InfectionAustralia
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Hugo W. Moser Research Institute at Kennedy Krieger...TerminatedAdrenoleukodystrophyUnited States
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Roswell Park Cancer InstituteCelgene CorporationCompletedRecurrent Adult Acute Myeloid Leukemia | Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities | Adult Acute Myeloid Leukemia With Del(5q) | Adult Acute Myeloid Leukemia With Inv(16)(p13;q22) | Adult Acute Myeloid Leukemia With t(16;16)(p13;q22) | Adult Acute Myeloid Leukemia With t(8... and other conditionsUnited States
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Bin LiUnknownAcute LHON | Onset Within Three Months | Onset Between 3 to 6 Months | Onset Between 6 to 12 Months | Onset Between 12 to 24 Months | Onset Between 24 to 60 Months | Onset Over 60 MonthsChina
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Yale UniversityNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)CompletedHyperparathyroidism | Hypophosphatemia, FamilialUnited States
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Sumithira VasuCompletedRecurrent Adult Acute Myeloid Leukemia | Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities | Adult Acute Myeloid Leukemia With Del(5q) | Adult Acute Myeloid Leukemia With Inv(16)(p13;q22) | Adult Acute Myeloid Leukemia With t(16;16)(p13;q22) | Adult Acute Myeloid Leukemia With t(8... and other conditionsUnited States
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Enzyvant Therapeutics GmBHCompletedFarber Disease | Farber's Disease | Farber Lipogranulomatosis | Acid Ceramidase Deficiency | Ceramidase Deficiency | N-Laurylsphingosine Deacylase Deficiency | ASAH1 MutationUnited States, Egypt, Canada, Italy, Turkey, Argentina, Germany, India, Sweden
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Onofre, Aurora Pujol, M.D.Instituto de Salud Carlos III; Fundacion Hesperia; ELA España AssociationCompletedAdrenomyeloneuropathy | X-linked AdrenoleukodystrophySpain
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Georgetown UniversityCompletedDiabetic Foot Ulcers | Equinus DeformityUnited States
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Onofre, Aurora Pujol, M.D.Ministerio de Sanidad, Servicios Sociales e Igualdad; Fundacion HesperiaCompleted
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Hugo W. Moser Research Institute at Kennedy Krieger...European Leukodystrophy AssociationCompletedX-linked AdrenoleukodystrophyUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAnemia, Sickle Cell | Blood Disease | Chlamydia Infections | Cerebrovascular Accident
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University Health Network, TorontoCompletedTrigeminal Neuralgia | Schwannoma | Arteriovenous MalformationCanada
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University of AarhusUnknownGlycogen Storage Disease Type 2 | Dystrophia MyotonicaDenmark
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Medical College and Hospital KolkataCompletedBenign Breast Disease | Mastalgia | Fibroadenoma | Fibrocystic Disease of BreastIndia
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Genzyme, a Sanofi CompanyCompletedPompe Disease (Late-onset) | Glycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Glycogenosis 2United States, France, Netherlands
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Baylor Research InstituteNational Institute of Neurological Disorders and Stroke (NINDS)Completed
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The University of Texas Health Science Center,...CompletedGastroesophageal Reflux Disease | Bronchopulmonary DysplasiaUnited States
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Shaare Zedek Medical CenterUnknownHepatitis C | Gaucher DiseaseIsrael
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Bayside HealthUniversity of MelbourneCompletedCystic Fibrosis | Chronic Obstructive Pulmonary Disease (COPD)Australia
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Universität Duisburg-EssenWeinmann Geräte für Medizin GmbH + Co. KGCompletedDuchenne Muscular Dystrophy | Spinal Muscular Atrophy | Chronic Respiratory InsufficiencyGermany
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novoGICompletedLymphoma | Colorectal Neoplasms | Endometriosis | Crohn Disease | Colitis, Ulcerative | Intestinal Polyposis | Ileostomy - Stoma | Intestinal Volvulus | Colostomy | Diverticulum, Colon | Rectal ProlapseUnited States
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Johannes Gutenberg University MainzUnknownMucopolysaccharidosis | Fabry DiseaseGermany
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ActelionCompleted