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Clinical Trials on Beta-Propeller Protein-Associated Neurodegeneration
Total 197 results
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LMU KlinikumSeventh Framework Programme; NBIA AllianceRecruitingNeurodegeneration With Brain Iron Accumulation (NBIA) | Pantothenate Kinase-associated Neurodegeneration (PKAN) | Aceruloplasminemia | Beta-Propeller Protein-Associated Neurodegeneration (BPAN) | Mitochondrial Membrane Protein Associated Neurodegeneration (MPAN) | Fatty Acid Hydroxylase-associated... and other conditionsCanada, Czechia, Germany, Italy, Netherlands, Poland, Serbia, Spain
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University of PennsylvaniaWashington University School of MedicineCompleted
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Susan J. HayflickOregon Health and Science University; Oregon Clinical and Translational Research...CompletedPantothenate Kinase-associated Neurodegeneration (PKAN)United States
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Akdeniz UniversityCompletedPeriodontitis | Gingival Crevicular Fluid | Interleukin 1-beta | Bactericidal Permeability ProteinTurkey
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Life Molecular Imaging SACompletedAlzheimer Disease | Amyloid Beta-ProteinUnited States, Switzerland, Australia, Germany, Japan
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CelgeneRecruitingBeta-thalassemia | Myelodysplastic Syndromes (MDS) | Myeloproliferative Neoplasm(MPN)-Associated MyelofibrosisUnited States, Japan, Israel, United Kingdom, Turkey, Greece, France, Australia, Belgium, Bulgaria, Canada, Germany, Italy, Malaysia, Spain, Sweden, Taiwan, Thailand, Tunisia, China, Lebanon, Netherlands
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Life Molecular Imaging SACompletedAlzheimer Disease | Amyloid Beta-ProteinAustralia
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Susan J. HayflickOregon Health and Science UniversityRecruitingNeurodegeneration With Brain Iron Accumulation (NBIA)United States
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University Hospital, BordeauxInstitut National de la Santé Et de la Recherche Médicale, FranceCompletedNeurodegeneration With Brain Iron Accumulation (NBIA)France
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Ente Ospedaliero Ospedali GallieraActive, not recruitingIron Overload | Neurodegenerative DiseaseItaly
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ApoPharmaFood and Drug Administration (FDA)CompletedPantothenate Kinase-Associated NeurodegenerationUnited States, Germany, Italy, United Kingdom
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Chiesi Canada CorpNo longer availablePantothenate Kinase-Associated Neurodegeneration
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Travere Therapeutics, Inc.TerminatedPantothenate Kinase-Associated NeurodegenerationUnited States, Canada, Czechia, France, Germany, Italy, Norway, Poland, Spain
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ApoPharmaCompletedPantothenate Kinase-Associated NeurodegenerationUnited States, Germany, Italy, United Kingdom
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Oregon Health and Science UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsActive, not recruitingPantothenate Kinase-Associated NeurodegenerationUnited States
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University College, LondonUnknownMitochondrial Diseases | Dystonia, Familial | Sporadic Dystonia | Parkinson Disease, Juvenile | Neurodegeneration With Brain Iron Accumulation 5
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Life Molecular Imaging SACompletedDown Syndrome | Amyloid Beta-proteinUnited States
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Brigham and Women's HospitalBoston University; University of Pennsylvania; University of Michigan; Duke University and other collaboratorsCompletedAlzheimer Disease | Education | Neuroimaging | Risk Assessment | Neuropsychological Tests | Amyloid Beta-PeptidesUnited States
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University of Novi SadMerck Sharp & Dohme LLCRecruitingMetabolic Syndrome | Aging | HIV I Infection | HIV Associated LipodystrophySerbia
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National Cancer Institute (NCI)RecruitingMesothelioma | BRCA1-Associated Protein-1 (BAP1) Mutations | Malignant Mesothelioma (MM) | Early-stage Mesothelioma | Subclinical Mesothelioma | Early-stage BAP1-associated MalignanciesUnited States
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Institut de Sante Publique, d'Epidemiologie et...CompletedAlzheimer Disease or Associated Disorder | Mild to Moderately Severe DementiaFrance
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Karuna TherapeuticsRecruitingPsychosis Associated With Alzheimer's DiseaseUnited States, Spain, Slovakia, Bulgaria, France, Czechia, Italy, Serbia, Germany, Croatia
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Karuna TherapeuticsEnrolling by invitationPsychosis Associated With Alzheimer's DiseaseUnited States
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SunovionCompletedMotor OFF Episodes Associated With Parkinson's DiseaseSpain, United Kingdom, Germany, Italy, Austria, France
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Karuna TherapeuticsRecruitingPsychosis Associated With Alzheimer's DiseaseUnited States, Korea, Republic of, Chile, Greece, Poland
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Taipei Medical University Shuang Ho HospitalCompletedAmyotrophic Lateral Sclerosis | ALS Functional Ration Scale | TAR-DNA-binding Protein-43 | Tamoxifen | mTORTaiwan
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Washington University School of MedicineKaryopharm Therapeutics IncRecruitingMultiple Myeloma | Myeloma-Associated AmyloidosisUnited States
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Spark TherapeuticsCompletedHematologic Diseases | Blood Coagulation Disorders, Inherited | Coagulation Protein Disorders | Hemorrhagic Disorders | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Gene Therapy | Blood Coagulation Disorder | Gene Transfer | Adeno-Associated Virus (AAV) | Factor VIII (FVIII) | Factor VIII (FVIII)... and other conditionsUnited States
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University of WashingtonMillennium Pharmaceuticals, Inc.Active, not recruitingFollicular Lymphoma | Waldenstrom Macroglobulinemia | Mantle Cell Lymphoma | Marginal Zone Lymphoma | Chronic Lymphocytic Leukemia | Lymphoplasmacytic Lymphoma | Small Lymphocytic Lymphoma | Recurrent Extranodal Marginal Zone Lymphoma of Mucosa-Associated Lymphoid Tissue | Refractory Extranodal Marginal...United States
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Beth Israel Deaconess Medical CenterMichael J. Fox Foundation for Parkinson's ResearchCompletedVoice Quality and Voice Loudness Associated With Parkinson's DiseaseUnited States
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Catalyst BiosciencesTerminatedPrevious Diagnosis With a Complement-mediated Disease and/or With Clinical Manifestations Reasonably Associated With Complement Factor I DeficiencyUnited States
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BiogenRecruitingAmyotrophic Lateral Sclerosis Associated With a SOD1 Gene MutationUnited States, Canada, Spain, Australia, Germany, Italy, Japan, Korea, Republic of, United Kingdom, Belgium, Brazil, France, Poland, Sweden
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InSightecRecruitingTremor Associated With Tremor Dominant Parkinson's DiseaseUnited States
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Otsuka Pharmaceutical Development & Commercialization...H. Lundbeck A/SCompletedAlzheimer Dementia | Agitation Associated With Alzheimer's DementiaUnited States
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Otsuka Pharmaceutical Development & Commercialization...H. Lundbeck A/SCompletedNervous System Diseases | Alzheimer's Disease | Mental Disorder | Agitation Associated With | Alzheimer's TypeSpain, United States, Germany, Croatia, Serbia, Russian Federation, Ukraine
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University of ValenciaRecruitingCerebrospinal Fluid Levels of Amyloid Beta 1-42, H-tau and Phospho-tau Proteins | Cognitive Impairment and Its Evolution After Hydrocephalus Treatment | Motor Impairment and Its Evolution After Hydrocephalus Treatment | Ventricular Size and Its Evolution After Implantation of a Ventriculoperitoneal...Spain
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University of BernNovartis; University Hospital Inselspital, Berne; Schweizerische Multiple Sklerose... and other collaboratorsRecruitingMultiple Sclerosis | Optic Neuritis | Neuromyelitis Optica Spectrum Disorder | CNS Sarcoidosis | CNS Vasculitis | Transverse Myelitis | Rasmussen Encephalitis | Acute Disseminated Encephalomyelitis | Anti-NMDAR Encephalitis | Anti-GAD65 Associated Autoimmune Encephalitis | Anti-AMPAR-1/2 Associated Autoimmune... and other conditionsSwitzerland
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Guangzhou University of Traditional Chinese MedicineGuangzhou Cadre Health Management CenterRecruitingAlzheimer Disease, Early Onset | Protein; DiseaseChina
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Otsuka Pharmaceutical Co., Ltd.CompletedAgitation Associated With Dementia of the Alzheimer's TypeJapan
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Otsuka Pharmaceutical Co., Ltd.CompletedAgitation Associated With Dementia of the Alzheimer's TypeJapan
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Otsuka Pharmaceutical Development & Commercialization...H. Lundbeck A/SCompletedNervous System Diseases | Alzheimer's Disease | Mental Disorder | Agitation Associated With | Alzheimer's TypeFrance, United States, Bulgaria, Slovenia, United Kingdom, Russian Federation, Ukraine, Finland, Canada
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Luye Pharma Group Ltd.Not yet recruitingNegative Symptoms of Schizophrenia | Hallucinations and Delusions Associated With Alzheimer's Disease Psychosis | Hallucinations and Delusions Associated With Parkinson Disease PsychosisChina
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Otsuka Pharmaceutical Co., Ltd.TerminatedAgitation Associated With Dementia of the Alzheimer's TypeJapan
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Otsuka Pharmaceutical Development & Commercialization...H. Lundbeck A/SCompletedNervous System Diseases | Mental Disorder | Alzheimer's Type | Agitation Associated With Alzheimer's DiseaseUnited States, Germany, France, Bulgaria, Spain, Slovenia, Croatia, Serbia, Russian Federation, Ukraine, Canada, United Kingdom
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Solvay PharmaceuticalsTerminatedPsychosis and Behavioral Disturbances Associated With Dementia of the Alzheimer's TypeUnited States, Czech Republic, Estonia, Israel, Poland
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National Cancer Institute (NCI)RecruitingMesothelioma | Familial Cancer | BRCA1-Associated Protein-1 (BAP1) Mutations | Tumor Predisposition Syndrome (TPDS)United States
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University Hospital, BordeauxRecruitingIntellectual Disability | Cystic Fibrosis | Neurodegeneration With Brain Iron Accumulation (NBIA) | Congenital Heart Defect | Albinism | Rubinstein-Taybi Syndrome | Periventricular Nodular HeterotopiaFrance
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Helse Stavanger HFKing's College London; Lund UniversityCompletedDementia With Lewy Bodies | Dementia Associated With Parkinson's DiseaseUnited Kingdom, Norway, Sweden
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Chelsea TherapeuticsCompletedMultiple System Atrophy | Neurogenic Orthostatic Hypotension | Dopamine Beta Hydroxylase Deficiency | Non-Diabetic Autonomic NeuropathyUnited States, Australia, Canada, New Zealand
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PersonGen BioTherapeutics (Suzhou) Co., Ltd.Anhui Provincial HospitalUnknownFollicular Lymphoma | B Cell Lymphoma | Mantle Cell Lymphoma | Diffuse Large B Cell Lymphoma | Plasma Cell Neoplasm | Extranodal Marginal Zone Lymphoma of Mucosa-Associated Lymphoid Tissue | Primary Cutaneous Follicle Centre LymphomaChina