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Clinical Trials on Birth Defects in New Zealand
Total 3654 results
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Incyte CorporationRecruitingAtopic DermatitisGermany, Poland, United States, Spain, United Kingdom, Italy, Belgium, Canada, Netherlands, Australia, Bulgaria, France, Switzerland, Hungary, Korea, Republic of
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ShireCompletedHereditary AngioedemaUnited States
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Pharnext SACompletedPhase III Trial Assessing the Efficacy and Safety of PXT3003 in CMT1A Patients (PLEO-CMT) (PLEO-CMT)Charcot-Marie-Tooth Disease Type 1AUnited States, United Kingdom, Belgium, Canada, France, Netherlands, Spain, Germany
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ShireCompletedHereditary Angioedema (HAE)United States, Jordan, Italy
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Alnylam PharmaceuticalsCompletedAmyloid Neuropathies | Amyloid Neuropathies, Familial | Amyloidosis, Hereditary | Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC) | Amyloidosis, Hereditary, Transthyretin-Related | Familial Transthyretin Cardiac AmyloidosisUnited States, France, Italy, Spain, Canada, Germany, Belgium, Sweden, United Kingdom
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Enyo PharmaRecruitingAlport SyndromeGermany, Spain, United States, France
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OrphalanCompletedWilson DiseaseUnited States, United Kingdom, Belgium, Brazil, Denmark, France, Germany, Italy, Poland
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TakedaCompletedLennox Gastaut Syndrome (LGS)United States, China, Canada, France, Hungary, Australia, Poland, Spain, Japan, Belgium, Greece, Serbia, Germany, Italy, Latvia, Netherlands, Russian Federation, Ukraine
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The Medicines CompanyCompletedElevated Cholesterol | Heterozygous Familial HypercholesterolemiaUnited States, Canada, Czechia, Denmark, Netherlands, South Africa, Spain, Sweden
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Cure HHTUniversity of Colorado, Denver; Massachusetts General Hospital; Mayo Clinic; Children... and other collaboratorsRecruitingArteriovenous Malformations | Epistaxis | Hereditary Hemorrhagic Telangiectasia | GastroIntestinal Bleeding | Telangiectasia | Vascular Malformation | Cerebral Arteriovenous MalformationsUnited States
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National Cancer Institute (NCI)CompletedNeurofibroma, Plexiform | Neurofibromatosis Type IUnited States, Germany
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Baxalta now part of ShireCompletedVon Willebrand DiseaseUnited States, Germany, United Kingdom, Italy, Austria, Canada
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PfizerCompletedHyperlipidemia | Hypercholesterolemia, FamilialAustralia, Canada, United States, France, South Africa, Sweden, Norway, Denmark, Iceland
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Medivation, Inc.PfizerCompletedHuntington DiseaseGermany, Canada, United States, Denmark, United Kingdom, Australia, Sweden
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Academic and Community Cancer Research UnitedNational Cancer Institute (NCI)RecruitingBile Duct Adenocarcinoma | Fanconi Anemia Complementation Group Gene Mutation | Metastatic Bile Duct Carcinoma | PTEN Gene DeletionUnited States
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American Society of Clinical OncologyBristol-Myers Squibb; Eli Lilly and Company; Bayer; Merck Sharp & Dohme LLC; Pfizer; AstraZene... and other collaboratorsRecruitingLymphoma, Non-Hodgkin | Multiple Myeloma | Advanced Solid TumorsUnited States
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ShireCompletedHereditary AngioedemaUnited States
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PfizerActive, not recruitingHemophilia A | Hemophilia BUnited States, Spain, Canada, China, Korea, Republic of, Hong Kong, Serbia, Taiwan, Turkey, France, Oman, Saudi Arabia, Japan, India, South Africa, Mexico, Croatia, Italy, Bulgaria, Russian Federation
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JW PharmaceuticalLEO PharmaCompletedAtopic DermatitisUnited States, Canada, Czechia, Germany, Poland, Spain, Australia, Japan
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisUnited States, Belgium, Brazil, France, Germany, Italy, United Kingdom
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Baxalta now part of ShireTakeda Development Center Americas, Inc.; Baxalta Innovations GmbH, now part...Active, not recruitingHemophilia AUnited States, Spain, Hungary, Italy, Germany, Austria, France
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Scott R. Plotkin, MD, PhDTakeda; National Comprehensive Cancer Network; The Children's Tumor FoundationRecruitingEpendymoma | Meningioma | Neurofibromatosis Type 2 | Vestibular Schwannoma | Non-vestibular SchwannomaUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FVII DeficiencySlovakia, Israel, Spain, India, Iran, Islamic Republic of, Pakistan, Turkey, Germany, Serbia, Italy, Greece, Thailand, France, United States, Hong Kong, Venezuela
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Ionis Pharmaceuticals, Inc.Active, not recruitingFamilial Chylomicronemia SyndromeSpain, United Kingdom, France, Canada, United States, Italy, Netherlands, Norway, Portugal, Slovakia, Sweden
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Wave Life Sciences Ltd.TerminatedHuntington DiseaseDenmark, Australia, Canada, France, United Kingdom, Germany, Poland
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Horizon Therapeutics, LLCCompletedUrea Cycle DisorderUnited States, Canada
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Harmony Biosciences, LLCActive, not recruitingMyotonic Dystrophy 1 | Excessive Daytime SleepinessUnited States, Canada
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PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, Duchenne | Musculoskeletal DiseaseUnited States, Taiwan, India, Korea, Republic of, Thailand, Australia, Brazil, Bulgaria, Canada, China, Hong Kong, Malaysia, Mexico, Poland, Puerto Rico, Russian Federation, Turkey, Japan
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Columbia UniversityNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMitochondrial Diseases | Mitochondrial Disorders | Mitochondrial Genetic Disorders | Disorder of Mitochondrial Respiratory Chain Complexes | Deletion and Duplication of Mitochondrial DNAUnited States, Canada
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National Cancer Institute (NCI)CompletedNeurofibromatosis 1 | Neurofibroma, PlexiformUnited States
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Baxalta now part of ShireBaxalta Innovations GmbH, now part of ShireCompletedHemophilia ACzechia, Switzerland, Denmark, Canada, Australia, Austria, France, United Kingdom, Italy, Sweden, Belgium, Brazil, China, Colombia, Greece, Hungary, Norway, Poland, Portugal, Russian Federation, Slovenia, Spain
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University of California, San FranciscoNational Institute of Neurological Disorders and Stroke (NINDS)CompletedEpilepsy | Infantile Spasms | Lennox-Gastaut Syndrome | Polymicrogyria | Localization-related Epilepsy | Periventricular HeterotopiasUnited States, Argentina, Australia
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Ultragenyx Pharmaceutical IncPRA Health SciencesRecruitingSly Syndrome | Mucopolysaccharidosis VII | MPS VII | MPS 7United States, Germany, Brazil, Argentina, France, Netherlands, Portugal, Spain, Turkey
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Novo Nordisk A/SCompletedHaemophilia A | Haemophilia BUnited States
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University of Alabama at BirminghamCompletedNeurofibromatosis | Plexiform Neurofibromas | NF1United States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AFrance, United States, Denmark, Netherlands, Sweden, Spain, Germany, Switzerland, Taiwan, Japan, United Kingdom, Croatia, Italy, Malaysia, Brazil, Australia, Hungary, Israel, Turkey, Puerto Rico, Norway, Korea, Republic of, Bulgaria, Russian...
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Regeneron PharmaceuticalsSanofiCompletedDermatitis, AtopicUnited States, Germany, Poland, Canada, Czechia, United Kingdom
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LEO PharmaCompletedAtopic DermatitisUnited States, Japan, France, Germany, Spain
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Mitsubishi Tanabe Pharma America Inc.Active, not recruitingEPP | XLPUnited States, Germany, Japan, Spain, Italy, Sweden, Australia, Canada, Norway, United Kingdom
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Bioverativ, a Sanofi companyActive, not recruitingHemophilia AUnited States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, China, France, Germany, Greece, Hungary, Ireland, Italy, Japan, Korea, Republic of, Netherlands, Spain, Sweden, Switzerland, Taiwan, Turkey, United Kingdom
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Genzyme, a Sanofi CompanyCRL/MedinetTerminatedFabry Disease | Chronic Kidney Disease, Stage IV (Severe)United States
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AmgenAstraZenecaTerminatedAtopic DermatitisUnited Kingdom, Spain, Australia, Hungary, Switzerland, United States, Germany, Korea, Republic of, Canada, Czechia, Poland, Japan, Estonia, Latvia, Ukraine
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PellePharm, Inc.CompletedBasal Cell Nevus SyndromeUnited States, Spain, Germany, United Kingdom, Italy, France, Belgium, Canada, Denmark, Netherlands
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Centre hospitalier de l'Université de Montréal...Centre Hospitalier Régional et Universitaire de BrestRecruitingArteriovenous Malformations | Unruptured Brain Arteriovenous Malformation | Ruptured Brain Arteriovenous Malformation | AVM | BAVMFrance, United States, Canada, Brazil, Chile, Colombia
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National Institute of Allergy and Infectious Diseases...National Heart, Lung, and Blood Institute (NHLBI); Gilead Sciences; University... and other collaboratorsCompleted
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Allakos Inc.TerminatedAtopic DermatitisUnited States, Germany
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SanofiRegeneron PharmaceuticalsCompletedAtopic DermatitisFrance, United States, Australia, Germany, Israel, Italy, Spain, Switzerland, United Arab Emirates, United Kingdom
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Regeneron PharmaceuticalsSanofiTerminatedAtopic DermatitisUnited States, Korea, Republic of, Belgium, Czechia, Germany, Poland, Spain
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Alpha-1 FoundationCompletedChronic Obstructive Pulmonary Disease | Alpha-1 Antitrypsin DeficiencyUnited States, Puerto Rico
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Alnylam PharmaceuticalsCompletedPrimary Hyperoxaluria Type 1 (PH1)United States, France, United Kingdom, Switzerland, Netherlands, Israel, Germany, United Arab Emirates