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Clinical Trials on Bone Marrow Failure
Total 37539 results
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National Heart, Lung, and Blood Institute (NHLBI)CompletedNeutropenia | Pancytopenia | Aplastic Anemia | Severe Aplastic AnemiaUnited States
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Children's Hospital Medical Center, CincinnatiFDA Office of Orphan Products DevelopmentCompleted
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Assistance Publique - Hôpitaux de ParisNot yet recruitingRefractory Idiopathic Aplastic Anemia | Haploidentical Allogeneic Hematopoietic Stem Cell Transplantation
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Memorial Sloan Kettering Cancer CenterActive, not recruiting
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Federal Research Institute of Pediatric Hematology...CompletedLeukemia, Myeloid, Acute | Opportunistic Infections | Graft vs Host Disease | Precursor T-Cell Lymphoblastic Leukemia-Lymphoma | Bone Marrow Failure Syndromes | Immune Deficiency DiseaseRussian Federation
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Masonic Cancer Center, University of MinnesotaRecruitingAplastic Anemia | Dyskeratosis CongenitaUnited States
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Masonic Cancer Center, University of MinnesotaCompletedAplastic Anemia | Dyskeratosis CongenitaUnited States
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Assistance Publique - Hôpitaux de ParisNot yet recruitingSevere Aplastic Anemia | Idiopathic Aplastic Anemia | Moderate Aplastic Anemia Requiring Transfusions
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National University Hospital, SingaporeUnknownHaematological Malignancies | Acquired Aplastic AnaemiaSingapore
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Novartis PharmaceuticalsTerminatedAplastic AnemiaRussian Federation
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Novartis PharmaceuticalsCompleted
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National Cancer Institute (NCI)RecruitingFanconi Anemia | Dyskeratosis Congenita | Diamond Blackfan Anemia | Shwachman Diamond Syndrome | Inherited Bone Marrow Failure Syndrome, Aplastic AnemiaUnited States
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Fondazione Italiana Sindromi Mielodisplastiche-ETSCompletedMyelofibrosis | Aplastic Anemia | MyelodysplasiaItaly
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National Heart, Lung, and Blood Institute (NHLBI)CompletedNeutropenia | Pancytopenia | Aplastic Anemia | Severe Aplastic AnemiaUnited States
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David Rizzieri, MDCompletedSickle Cell Anemia | Pure Red Cell Aplasia | Paroxysmal Nocturnal Hemoglobinuria (PNH) | Severe Aplastic AnemiaUnited States
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City of Hope Medical CenterNational Cancer Institute (NCI)RecruitingRecurrent Severe Aplastic Anemia | Refractory Severe Aplastic AnemiaUnited States
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Cellphire Therapeutics, Inc.Department of Health and Human ServicesTerminatedMyelodysplastic Syndromes | Myeloproliferative Disorders | Thrombocytopenia | Hematologic Malignancy | Bone Marrow Aplasia | Platelet RefractorinessUnited States, Israel, Norway
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Sidney Kimmel Comprehensive Cancer Center at Johns...RecruitingPrimary Immune Deficiency Disorder | Bone Marrow Failure | Immune Deficiency DiseaseUnited States
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Paul SzabolcsRecruitingIdiopathic Pulmonary Fibrosis | Emphysema or COPDUnited States
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St. Jude Children's Research HospitalCompletedAnemia, Aplastic | Diamond-Blackfan Anemia | Amegakaryocytic Thrombocytopenia | Kostmann SyndromeUnited States
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UNC Lineberger Comprehensive Cancer CenterRecruitingBone Marrow Transplantation | Bone Marrow DiseaseUnited States
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingSevere Aplastic AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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Seoul National University HospitalMinistry of Food and Drug Safety, KoreaUnknownAcute Leukemia | Severe Aplastic Anemia | Chronic LeukemiaKorea, Republic of
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary Anemias | Systemic Juvenile Idiopathic Arthritis (sJIA)United States
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European Institute of OncologyRecruitingLymphoma | Leukemia | Aplastic Anemia | Leukemia, Acute | Leukemia, ChronicItaly
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University of UtahNovartisCompletedSevere Aplastic Anemia | Moderate Aplastic Anemia | Very Severe Aplastic AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedThrombocytopenia | Neutropenia | Pancytopenia | ImmunosuppresionUnited States
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Xiaofan ZhuAvailableFanconi Anemia | Autosomal or Sex Linked Recessive Genetic Disease | Bone Marrow Hematopoiesis Failure, Multiple Congenital Abnormalities, and Susceptibility to Neoplastic Diseases. | Hematopoiesis Maintainance.China
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Masonic Cancer Center, University of MinnesotaCompletedDiamond-Blackfan Anemia | Shwachman-Diamond Syndrome | Kostmann's NeutropeniaUnited States
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Boston Children's HospitalMassachusetts General Hospital; Mayo Clinic; Karolinska University Hospital; Baylor... and other collaboratorsActive, not recruitingAplastic Anemia | Dyskeratosis Congenita | Hoyeraal Hreidarsson Syndrome | Revesz SyndromeUnited States, Norway, Sweden
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Memorial Sloan Kettering Cancer CenterBoston Children's Hospital; Fred Hutchinson Cancer Center; Children's Hospital... and other collaboratorsCompletedLeukemia | Myelodysplastic Syndrome | Aplastic AnemiaUnited States
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Institute of Hematology & Blood Diseases HospitalUnknownUrination Disorders | Thrombosis | Proteinuria | Anemia, Hemolytic | Hemoglobinuria, Paroxysmal | Hemoglobinuria | Paroxysmal Nocturnal Hemoglobinuria | Bone Marrow Failure | Aplastic Anemia,China
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Northwestern Memorial HospitalUnknownAplastic Anemia | Graft Versus Host DiseaseUnited States
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University College, LondonBloodwiseCompletedHodgkin's Lymphoma | Non-Hodgkin's Lymphoma | Myelodysplastic Syndrome | Acute Myeloid Leukaemia | Chronic Lymphocytic Leukaemia | Acute Lymphoblastic Leukaemia | Chronic Myeloid Leukaemia | Acquired Bone Marrow Failure Syndromes | Other Haematological Malignancies; Unrelated HSCT IndicatedUnited Kingdom
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Washington University School of MedicineShwachman Diamond Syndrome Foundation; Barnes-Jewish HospitalRecruiting
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Stanford UniversityUniversity of Alabama at Birmingham; University of MinnesotaCompletedSickle Cell Disease | Thalassemia | Diamond-Blackfan AnemiaUnited States
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Institute of Hematology & Blood Diseases HospitalUnknownUrination Disorders | Thrombosis | Proteinuria | Anemia, Hemolytic | Hemoglobinuria, Paroxysmal | Hemoglobinuria | Paroxysmal Nocturnal Hemoglobinuria | Bone Marrow Failure | Aplastic Anemia,China
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M.D. Anderson Cancer CenterGenzyme, a Sanofi CompanyCompletedMyelodysplastic Syndrome | Aplastic AnemiaUnited States
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Peking University People's HospitalNot yet recruitingMyelodysplastic Syndromes | Acute Leukemia | Severe Aplastic Anemia
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Alberta Children's HospitalStollery Children's HospitalTerminatedChildhood Cancer | Aplastic Anemia | Metabolic DisordersCanada
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Regeneron PharmaceuticalsRecruitingSevere Aplastic Anemia (SAA)United States, France, Korea, Republic of, United Kingdom
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BioLineRx, Ltd.CompletedAplastic Anemia | Hypoplastic Myelodysplastic SyndromeUnited States
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Zimmer BiometCompletedBone Marrow Edema | Bone Marrow LesionsGermany, Netherlands, Italy, Spain, United Kingdom
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Paul SzabolcsRecruitingSickle Cell Anemia | Diamond-blackfan Anemia | Beta-thalassemia MajorUnited States
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Boston Children's HospitalCompleted
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Masonic Cancer Center, University of MinnesotaCompletedFanconi AnemiaUnited States
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Hospital Universitari Vall d'Hebron Research InstituteCIEMAT; CIBERERCompleted
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National Heart, Lung, and Blood Institute (NHLBI)Children's Hospital Medical Center, CincinnatiCompletedFanconi AnemiaUnited States