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Clinical Trials on Brain Diseases, Metabolic
Total 380448 results
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National Institute of Neurological Disorders and...CompletedType 2 Gaucher DiseaseUnited States
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Exsar CorporationSuspendedType I Gaucher DiseaseUnited States
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University of PisaCompletedTo Determine the Effect of GLP1 on Cognitive Function, Brain Glucose Metabolism and Neuroplasticity.Glucose Metabolism Disorders | Obesity | Degenerative Brain DisorderItaly
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Taysha Gene Therapies, Inc.Withdrawn
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Xinhua Hospital, Shanghai Jiao Tong University...Shanghai Vitalgen BioPharma Co., Ltd.RecruitingType II Gaucher DiseaseChina
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Prevail TherapeuticsEli Lilly and CompanyRecruitingGaucher Disease | Gaucher Disease, Type 1United States, Spain, Germany
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Shaare Zedek Medical CenterRecruiting
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Prevail TherapeuticsEli Lilly and CompanyActive, not recruitingGaucher Disease, Type 2United States, United Kingdom
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AVROBIOTerminatedGaucher DiseaseUnited States, Canada
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SanofiCompletedGaucher's DiseaseUnited States
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Hadassah Medical OrganizationCompleted
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AVROBIOTerminatedType 1 Gaucher DiseaseUnited States, Canada
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Shaare Zedek Medical CenterCompletedGaucher Disease, Type 1Israel
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Ari ZimranPfizerActive, not recruitingGaucher Disease, Type 3Israel, Turkey, India
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CEN BiotechTakeda; BioClinica, Inc.Completed
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ShireCompletedGaucher Disease, Type 1United States, Israel, Argentina, India, Korea, Republic of, Paraguay, Poland, Russian Federation, Spain, Tunisia, United Kingdom
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ShireCompletedGaucher DiseaseUnited States, Israel, United Kingdom, Poland, Spain
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ShireApproved for marketingGaucher Disease, Type 1United States
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University Research Foundation for Lysosomal Storage...University of PittsburghCompletedGaucher DiseaseUnited States
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Shaare Zedek Medical CenterCompletedGaucher Disease Type 1Israel
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Nantes University HospitalCompletedPatients With Gaucher's DiseaseFrance
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National Institute of Mental Health (NIMH)Completed
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Luca RonfaniUniversity of TriesteCompletedUrea Cycle Disorders, Inborn | Other Metabolic DiseasesItaly
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PTC TherapeuticsCompletedLeigh SyndromeUnited States
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Aadi Bioscience, Inc.Withdrawn
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Shoshana VilkGenzyme, a Sanofi CompanyCompletedGaucher Disease | Patient Reported OutcomeIsrael
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Yassin Abdelghaffar Charity Center for Liver Disease...Society of Friends of Liver Patients in the Arab World (SLPAW)RecruitingHereditary Tyrosinemia, Type IEgypt
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Children's National Research InstituteBoston Children's HospitalRecruitingUrea Cycle DisordersUnited States
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University of Missouri-ColumbiaCompleted
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University Hospital, ToursCompletedPhenylketonuriaFrance
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Emory UniversityPatient-Centered Outcomes Research InstituteCompleted
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Cycle Pharmaceuticals Ltd.ParexelCompletedHereditary Tyrosinemia, Type ISouth Africa
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University of ZurichCompletedPhenylketonuria (PKU) and HyperphenylalaninemiaSwitzerland
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Swedish Orphan BiovitrumCompletedHereditary Tyrosinemia, Type IGermany, United Kingdom, France
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Cytonet GmbH & Co. KGCRS Clinical Research Services Mannheim GmbHCompleted
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Orphanetics Pharma Entwicklungs GmbHTerminatedPhenylalanine Hydroxylase Deficiencies
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National Center for Research Resources (NCRR)University of TexasCompleted
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Nutricia ResearchCompletedInborn Errors of Metabolism | Urea Cycle DisorderUnited States
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Horizon Pharma Ireland, Ltd., Dublin IrelandCompletedUrea Cycle DisordersUnited States
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Cytonet GmbH & Co. KGTerminatedUrea Cycle DisordersUnited States, Canada
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National Institute of Neurological Disorders and...CompletedGaucher DiseaseUnited States
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SanofiCompleted
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AVROBIOWithdrawn
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Amicus TherapeuticsCompletedGaucher Disease | Gaucher Disease, Type 1 | Type 1 Gaucher DiseaseUnited Kingdom, United States
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University Children's Hospital, ZurichRecruitingUrea Cycle DisordersSwitzerland
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University Hospital, ToursCompletedAdult Phenylketonuria Non Treated PatientsFrance
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Swedish Orphan BiovitrumCompletedHereditary Tyrosinemia, Type IBelgium, Denmark, France, Germany, Austria, Czechia, Finland, Hungary, Ireland, Italy, Netherlands, Norway, Poland, Portugal, Spain, Sweden, United Kingdom
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Cycle Pharmaceuticals Ltd.ParexelCompletedHereditary Tyrosinemia, Type ISouth Africa
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CENTOGENE GmbH RostockWithdrawnMetabolic Disorders | Tyrosinosis | Hepatorenal Tyrosinemia | Fumarylacetoacetase Deficiency | Fah DeficiencyGermany, Sri Lanka, India