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Clinical Trials on Bulbo-Spinal Atrophy, X-Linked
Total 1852 results
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Guido A. Davidzon, MD, SMWithdrawn
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Tetra Discovery PartnersCompletedFragile X Syndrome | Fra(X) Syndrome | FXSUnited States
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Lantu BiopharmaNot yet recruitingSpinal Muscular Atrophy
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Robert Jones and Agnes Hunt Orthopaedic and District...University Hospital Birmingham NHS Foundation TrustRecruitingSpinal Muscular AtrophyUnited Kingdom
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Hoffmann-La RocheRecruitingMuscular Atrophy, SpinalGermany, United States, Belgium
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NMD Pharma A/SRecruitingSpinal Muscular AtrophyUnited States, Spain, Belgium, Denmark, Germany, Netherlands, Italy, Canada
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Fondazione Policlinico Universitario Agostino Gemelli...Recruiting
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Fondazione Policlinico Universitario Agostino Gemelli...Bambino Gesù Hospital and Research Institute; University of Messina; University... and other collaboratorsRecruitingSpinal Muscular AtrophyItaly
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Holland Bloorview Kids Rehabilitation HospitalRecruiting
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BiogenRecruitingSpinal Muscular AtrophyUnited States, Germany, Italy, Hungary, Japan
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BiogenActive, not recruitingMuscular Atrophy, SpinalChina, United States, Netherlands, Spain, Korea, Republic of, Taiwan, Australia, Canada, Chile, Saudi Arabia, Poland, Israel, Brazil, Russian Federation, Hungary, Japan, United Kingdom, Italy, Germany, Estonia, Greece, Mexico, Colombia and more
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Ohio State UniversityCure SMAActive, not recruitingSpinal Muscular AtrophyUnited States
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Hoffmann-La RocheActive, not recruitingMuscular Atrophy, SpinalUnited States, Belgium, Brazil, Russian Federation, Australia, Taiwan, Poland
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BiogenEnrolling by invitationMuscular Atrophy, SpinalUnited States, Spain, Taiwan, Chile, Saudi Arabia, Brazil, Russian Federation, Mexico, Germany, Estonia, Japan, Canada, Colombia, Lebanon, Poland, Italy, China
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Clinic for Special ChildrenGenentech, Inc.Active, not recruitingSpinal Muscular AtrophyUnited States
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Hoffmann-La RocheCompletedMuscular Atrophy, SpinalBelgium, United States, China, Spain, Japan, France, Brazil, Croatia, Italy, Russian Federation, Saudi Arabia, Serbia, Switzerland, Turkey, Ukraine, Poland
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Novartis Gene TherapiesPRA Health SciencesCompletedSpinal Muscular AtrophyUnited States, United Kingdom, Australia, Belgium, Canada, Japan
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Hospital Israelita Albert EinsteinMinistry of Health, BrazilCompletedSpinal Muscular AtrophyBrazil
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BiogenCompletedSpinal Muscular AtrophyUnited States, Germany, Spain, Canada, France, Hong Kong, Italy, Japan, Korea, Republic of, Sweden
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BiogenCompleted
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Hospices Civils de LyonUnknownResponsiveness and Validation Study of MFM-20 in SMA Patients Treated With Nusinersen (RetroNusiMFM)Spinal Muscular AtrophyFrance
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Genentech, Inc.Approved for marketingMuscular Atrophy, SpinalUnited States
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University Hospital, RouenSociety GENOMIC VISIONTerminatedSpinal Muscular AtrophyFrance
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Hoffmann-La RocheCompleted
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University of UtahAbbott; Families of Spinal Muscular AtrophyCompletedSpinal Muscular AtrophyUnited States
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Rigshospitalet, DenmarkCompleted
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HealthCore-NERIThe Spinal Muscular Atrophy FoundationCompletedSpinal Muscular AtrophyUnited States, Canada
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Centro Universitário Augusto MottaCompletedSpinal Muscular Atrophy
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Hangzhou Jiayin Biotech LtdRecruitingSpinal Muscular Atrophy Type IChina
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Assistance Publique Hopitaux De MarseilleRecruitingSpinal Muscular AtrophyFrance
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Novartis Gene TherapiesActive, not recruitingSpinal Muscular Atrophy 1United States
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Institut de Myologie, FranceCompletedSpinal Muscular Atrophy
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WestatNational Institute of Neurological Disorders and Stroke (NINDS)TerminatedSpinal Muscular Atrophy Type IUnited States
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Columbia UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedSpinal Muscular Atrophy Type 3 | Mitochondrial MyopathyUnited States
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Kun SunRecruitingSpinal Muscular Atrophy 1China
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Institut de Myologie, FranceRoche Pharma AGNot yet recruitingMuscular Atrophy, Spinal, Type II | Muscular Atrophy, Spinal, Type IIIFrance
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Novartis Gene TherapiesCompletedSpinal Muscular Atrophy 1United States
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Stanford UniversityCompletedMuscular Atrophy, SpinalUnited States
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Assistance Publique - Hôpitaux de ParisCompleted
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IRCCS San RaffaeleFondazione TelethonRecruitingChronic Granulomatous Disease X-linked (X-CGD)Italy
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GeneCradle IncRecruiting
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Charitable Foundation Children with Spinal Muscular...WithdrawnSpinal Muscular Atrophy | Neuromuscular DisordersUkraine
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University Hospital, Basel, SwitzerlandCompletedLumbar Spinal Stenosis (LSS)Switzerland
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University of OxfordOxford Brookes University; Oxford University Hospitals NHS Trust; Scholar Rock... and other collaboratorsNot yet recruiting
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McGill University Health Centre/Research Institute...Not yet recruiting
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Rigshospitalet, DenmarkRecruitingSpinal Muscular AtrophyDenmark
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National Taiwan University HospitalNot yet recruiting
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Fondazione Policlinico Universitario Agostino Gemelli...IRCCS Eugenio Medea; Azienda Ospedaliera Universitaria Policlinico "G. Martino... and other collaboratorsNot yet recruitingSpinal Muscular Atrophy
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Hoffmann-La RocheRecruiting
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GeneCradle IncRecruitingSpinal Muscular AtrophyChina