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Clinical Trials on C1 Esterase Inhibitor, Deficiency of
Total 430 results
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...CompletedSevere Combined Immunodeficiency | Adenosine Deaminase Deficiency | Immune System Disorder | Autosomal Recessive Disorder | Purine-Nucleoside Phosphorylase Deficiency | Severe Combined Immunodeficiency With Absence of T and B Cells | X-Linked Severe Combined ImmunodeficiencyUnited States
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Centre Leon BerardCompletedColorectal Cancer | Non Small Cell Lung Cancer | Head and Neck Squamous Cell Carcinoma | Epidermal Growth Factor Receptor InhibitorFrance
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University of PittsburghNational Cancer Institute (NCI)TerminatedCOPD | Deficiency of Vitamin D3United States
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Zagazig UniversityCompletedVitamin D Deficiency | Sickle Cell Disease | Bone Mineral Density | Health Related Quality of Life | Hand Grip StrengthEgypt
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University of North Carolina, Chapel HillUniversity of California, Davis; Bill and Melinda Gates Foundation; Thrasher... and other collaboratorsCompletedEfficacy of Caterpillar Cereal for Complementary Feeding in the Democratic Republic of Congo (CAT02)Malnutrition | Iron Deficiency Anemia | Stunting of Growth | Neurodevelopmental Impairment | Infectious Diseases MorbidityCongo
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Apollomics (Australia) Pty. Ltd.Novotech (Australia) Pty Limited; Apollomics Inc. (formerly CBT Pharmaceuticals...CompletedSolid Tumor | Microsatellite Instability | Mismatch Repair Deficiency | Cancer of Unknown Primary SiteAustralia
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Universidade Federal FluminenseActive, not recruitingDysbiosis | Anemia of Chronic Kidney Disease | Chronic Renal Disease | Iron-Deficiency AnemiaBrazil
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China-Japan Friendship HospitalRecruitingIron Deficiency | Heart Failure With Reduced Ejection Fraction | Acute Heart FailureChina
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Hospices Civils de LyonCompletedChildren With a Deficiency of Alpha-1 AntitrypsinFrance
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China-Japan Friendship HospitalRecruitingHeart Failure With Preserved Ejection Fraction | Acute Heart Failure | Iron DeficienciesChina
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Zimmer BiometActive, not recruitingOsteoarthritis of the Shoulder | Post-Traumatic Arthritis | Arthropathy of Shoulder Region | Grossly Deficient Rotator Cuff | Rheumatoid Arthritis Without Humeral Metaphyseal DefectsUnited States
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China Academy of Chinese Medical SciencesUnknownEfficiency of Genuine Regional and Non-genuine Regional Rhizoma Atractylodis in Treating FD
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Technical University of MunichUniversity Medicine Greifswald; Fresenius Kabi; Berlin Institute of HealthRecruitingQuality of Life | Muscle Atrophy | Metabolic Disturbance | ICU Acquired Weakness | Energy Malnutrition Protein | Morphological and Microscopic FindingsGermany
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Insel Gruppe AG, University Hospital BernRecruitingMultiple Sclerosis | Fatigue | HypogammaglobulinemiaSwitzerland
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Keryx BiopharmaceuticalsCompletedAnemia of Chronic Kidney DiseaseIsrael
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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Stanford UniversityBoston Children's Hospital; Ann & Robert H Lurie Children's Hospital of Chicago and other collaboratorsEnrolling by invitationOxygen Deficiency | Hypoventilation | Desaturation of Blood | Anesthesia; Adverse EffectUnited States
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Stanford UniversityCompletedOxygen Deficiency | Hypoventilation | Desaturation of Blood | Anesthesia; Adverse EffectUnited States
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Central Hospital, Nancy, FranceUnknownGLILD in a Population of Children and Young AdultsFrance
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University of AthensUnknownStress, Physiological | Cytomegalovirus Viraemia | Receptor, Hormonal; Disorder | Other Deficiency of Cell-mediated ImmunityGreece
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Gazi UniversityRecruitingPrimary Immunodeficiency DiseasesTurkey
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Victoria Arija ValCarlos III Health Institute; Catalan Institute of Health; University Rovira i... and other collaboratorsCompletedAnemia Ferropenic | Risk of Hemoconcentration (Iron Levels >130g/L)Spain
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Joslin Diabetes CenterAbbottCompletedVitamin D Deficiency | Chronic Kidney Disease | Coronary Calcification | Disorders of Calcium and Bone MetabolismUnited States
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Grace Science, LLCRecruitingNGLY1 DeficiencyUnited States
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Southern California College of Optometry at Marshall...RecruitingAqueous Tear Deficiency | Meibomian Gland Dysfunction of Bilateral Eyes (Disorder)United States
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Evangelisches Krankenhaus DüsseldorfOlympusCompletedCrohn's Disease | Gastrointestinal Hemorrhage | Disorder of Small Intestine | Iron Deficiency Anaemia | Small Bowel Tumors | Intestinal Polyposis Syndrome | Coeliac DiseaseBelgium, Germany
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Marmara UniversityCompletedQuality of Life | Celiac Disease | Nutritional DeficiencyTurkey
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Inozyme PharmaRecruitingGeneralized Arterial Calcification of Infancy | Autosomal Recessive Hypophosphatemic Rickets | Ectonucleotide Pyrophosphatase/Phosphodiesterase1 DeficiencyUnited States, United Kingdom, Canada
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Merck KGaA, Darmstadt, GermanyMerck Serono S.A., GenevaCompletedTurner Syndrome | Idiopathic Growth Hormone DeficiencySpain, France, Canada, United Kingdom, Czech Republic, Argentina, Germany, Italy, Sweden
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Inozyme PharmaActive, not recruitingGeneralized Arterial Calcification of Infancy | Autosomal Recessive Hypophosphatemic Rickets | Ectonucleotide Pyrophosphatase/phosphodiesterase1 DeficiencyUnited States, Canada, Germany, France, United Kingdom
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University of California, San FranciscoCompletedSickle Cell Disease | Hemoglobinopathies | Fanconi Anemia | Thalassemia | Hematologic Malignancies | Immune Deficiency | Nonmalignant Diseases | Genetic Inborn Errors of MetabolismUnited States
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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Spark TherapeuticsCompletedHematologic Diseases | Blood Coagulation Disorders, Inherited | Coagulation Protein Disorders | Hemorrhagic Disorders | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Gene Therapy | Blood Coagulation Disorder | Gene Transfer | Adeno-Associated Virus (AAV) | Factor VIII (FVIII) | Factor VIII (FVIII)... and other conditionsUnited States
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Zimmer BiometEnrolling by invitationOsteoarthritis of the Shoulder | Arthropathy of Shoulder Region | Grossly Deficient Rotator Cuff | Rheumatoid Arthritis Without Humeral Metaphyseal Defects | Post-Traumatic ArthitisUnited States
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Göteborg UniversityThe Health & Medical Care Committee of the Regional Executive Board, Region...CompletedQuality of Life | Mouth Diseases | Secretion; Salivary Gland, DeficientSweden
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Assistance Publique - Hôpitaux de ParisRecruitingPediatric Patients | Any Type of Severe Combined Immunodeficiency (SCID) | Partial HLA Incompatible Allogeneic Hematopoietic Stem Cell Transplantation (HSCT)France
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Hospital St. Joseph, Marseille, FranceWithdrawnFibrillation, Atrial | To Evaluate the Intraoperative Efficiency of the AIFIB Software in the Detection of Atrial Fibrillation Driver During an Ablation ProcedureFrance, Netherlands
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OctapharmaCompletedPrimary ImmunodeficiencyUnited Kingdom, Australia, Germany, Italy
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Galderma R&DRecruitingWeight Loss | Skin Laxity | Photoaging | Photodamaged Skin | Volume Deficiency of the MidfaceUnited States
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Mostafa Hassanein, MscCompletedACL Injury | Knee Deformity | ACL - Anterior Cruciate Ligament Deficiency | Varus Deformity of Tibia (Disorder)Egypt
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University Hospital HeidelbergGerman Cancer Research CenterCompletedType2 Diabetes | Fatty Acid Deficiency | Alteration of Mitochondrial MembraneGermany
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Prof Gérard WAEBERCentre Hospitalier Universitaire Vaudois; University of Lausanne; Center for...TerminatedIron-deficiency | Safety Issues | Metabolic Disorder, Glucose | Iron Toxicity | Glucose Metabolism Disorders (Including Diabetes Mellitus) | Metabolic Side Effects of DrugsSwitzerland
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Zhejiang UniversityHangzhou Hunter Biotechnology IncorporationRecruitingPrecise Prediction of Therapy EfficiencyChina
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University of RijekaCompletedQuality of Life | Pain | Multiple Sclerosis | Fatigue | Physical Activity | Physical Disability | Motivation | Disability Physical | Energy Supply; Deficiency | Mental Status Change | Mental Impairment | Disabilities PsychologicalCroatia
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National Human Genome Research Institute (NHGRI)Withdrawn
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Eunice Kennedy Shriver National Institute of Child...RecruitingNiemann-Pick Disease Type C1 | Juvenile Neuronal Ceroid Lipofuscinosis | Smith-Lemli-Opitz Syndrome | Creatine Transporter DeficiencyUnited States
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Ferring PharmaceuticalsCompletedTurner's Syndrome | Human Growth Hormone DeficiencyFrance
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Tehran University of Medical SciencesBoston UniversityNot yet recruitingMultiple Sclerosis, Relapsing-Remitting | Vitamin D3 Deficiency | Adult ALL
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OctapharmaCompletedPrimary Immunodeficiency (PID)France
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Inozyme PharmaNot yet recruitingGeneralized Arterial Calcification of Infancy | Autosomal Recessive Hypophosphatemic Rickets | Ectonucleotide Pyrophosphatase/phosphodiesterase1 Deficiency | ATP-Binding Cassette Subfamily C Member 6 Deficiency