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Clinical Trials on Ceroid Storage Disease
Total 379556 results
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Duke UniversityCompleted
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Amicus TherapeuticsTerminatedLate-onset Pompe DiseaseUnited States, Canada, Australia, Belgium
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BioMarin PharmaceuticalTerminatedLate-onset Pompe DiseaseUnited States, United Kingdom, Germany, France, Italy, Portugal, Belgium, Netherlands
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Huashan HospitalNot yet recruitingPompe Disease (Late-onset)China
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Rambam Health Care CampusRecruitingPompe Disease Infantile-OnsetIsrael
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Astellas Gene TherapiesRecruitingPompe Disease (Late-onset)United States, United Kingdom
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Amicus TherapeuticsRecruitingPompe Disease (Late-onset)United States, Taiwan, Japan, Australia, Canada
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Genzyme, a Sanofi CompanyRecruitingGlycogen Storage Disease Type II | Pompe DiseaseHungary, Croatia, Serbia, United States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, Chile, China, Colombia, Denmark, France, Germany, Greece, Hong Kong, India, Indonesia, Israel, Italy, Japan, Jordan, Korea, Republic of, Kuwait and more
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Amicus TherapeuticsActive, not recruitingPompe Disease (Late-onset)United States, Germany, Taiwan, Belgium, Australia, Slovenia, Spain, Netherlands, Hungary, Japan, Austria, United Kingdom, France, Argentina, Canada, Sweden, Denmark, New Zealand, Greece, Korea, Republic of, Bosnia and Herzegovina, Ita... and more
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Duke UniversityGenzyme, a Sanofi CompanyActive, not recruitingPompe Disease (Late-onset) | Pompe Disease | GAA DeficiencyUnited States
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Amicus TherapeuticsAvailablePompe Disease Infantile-OnsetTaiwan, United States, Italy
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BioMarin PharmaceuticalTerminatedLate-onset Pompe DiseaseUnited States, United Kingdom
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Duke UniversityWithdrawnPompe Disease (Late-onset)United States
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Rambam Health Care CampusCompletedEnzyme Replacement Therapy in Pompe Disease
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Pompe Disease Infantile-OnsetUnited States, France, South Africa
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Chengdu Kanghong Biotech Co., Ltd.UnknownChoroid Neovascularization Secondary to Degenerative MyopiaChina
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Children's Hospital of Orange CountyUltragenyx Pharmaceutical IncRecruitingInflammation | Mucopolysaccharidoses | Cardiac Disease | Carotid DiseaseUnited States
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Marmara UniversityCompletedFluid Responsiveness | Common Carotid ArteryTurkey
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Hopital FochCompletedPulmonary Surgical Procedures | Recovery PeriodFrance
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Sefako Makgatho Health Sciences UniversityCompletedQuality of Recovery | Anesthesia Recovery PeriodSouth Africa
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Columbia UniversityMayo Clinic; University of California, Los Angeles; University of Maryland; University... and other collaboratorsRecruitingCognitive Impairment | Internal Carotid Artery StenosisUnited States, Canada
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Aesculap AGEnrolling by invitationCarotid Artery Stenosis | Iliac Artery Stenosis | Femoral Artery StenosisGermany
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Technische Universität DresdenKlinikum Chemnitz gGmbHUnknown
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Assiut UniversityUnknownSteroid Dependent and Steroid Resistent Nephrotic Syndrome
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Genzyme, a Sanofi CompanyCompletedPompe DiseaseBelgium, United States, Czechia, Germany, Italy, Taiwan
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University of FloridaAmicus TherapeuticsTerminatedPompe Disease | Hypersensitivity Reaction
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Rambam Health Care CampusUnknown
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University of MinnesotaWithdrawn
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Azienda Ospedaliera di PerugiaUniversity Of PerugiaUnknownCarotid Artery DiseaseItaly
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VPDiagnosticsNational Institutes of Health (NIH)UnknownAtherosclerotic Disease, CarotidUnited States
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Glycogenosis 2United States
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Genzyme, a Sanofi CompanyApproved for marketingGlycogen Storage Disease Type II | Glycogenosis 2
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University of UtahCompletedPost-operative Craniotomy Patients | Carotid Endarterectomy and Carotid Artery Stenosis Patients | Post-op Spine Patients Admitted to the NCCU | Endovascular Patients Undergoing Intracranial Intervention | Traumatic Brain Injuries NPO for at Least 12 HoursUnited States
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Scott McnallyAmerican Heart AssociationActive, not recruitingInflammation | Cognitive Impairment | Carotid Artery PlaqueUnited States
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University Hospital, Motolprofessor Josef Veselka; associate professor Petr Hájek; Martin HorváthCompletedCarotid Atherosclerosis | Restenosis | Carotid Artery Stenting | Near Infrared Spectroscopy | Atherosclerotic PlaqueCzechia
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Beijing HospitalUnknownCarotid Artery StenosisChina
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Meshalkin Research Institute of Pathology of CirculationCompletedStroke | Bleeding | Carotid Stenosis | Carotid Atherosclerosis | Ischemic AttackRussian Federation
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Russian Cardiology Research and Production CenterTerminatedStroke | Atherosclerosis | Carotid Artery StenosisRussian Federation
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Assaf-Harofeh Medical CenterRecruitingOvarian Dermoid CystIsrael
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University of ManitobaCo-Investigator - Dr. Cheryl Rockman-GreenbergCompletedHypoglycemia | Glycogen Storage Disorder Type 1 | Cornstarch | GlycosadeCanada
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University Hospital, MotolUnknownCarotid Occlusion IntoleranceCzech Republic
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Genzyme, a Sanofi CompanyCompletedPompe Disease (Late-onset) | Glycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Glycogenosis 2Netherlands
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Genzyme, a Sanofi CompanyCompletedPompe Disease (Late-onset) | Glycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Glycogenosis 2France
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Genzyme, a Sanofi CompanyCompletedPompe Disease (Late-onset) | Glycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Glycogenosis 2United States, France, Netherlands
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Queen's UniversityCompletedChest Pain | Carotid Artery Plaque | Acute Coronary SyndromeCanada
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Seoul National University Childrens HospitalUnknownSteroid Resistant Nephrotic Syndrome | Steroid Dependent Nephrotic SyndromeKorea, Republic of
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B.P. Koirala Institute of Health SciencesNepal Health Research CouncilCompleted
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Central Hospital, Nancy, FranceRecruitingPompe's Disease Juvenile OnsetFrance
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Next Science TMJacksonville Center For Clinical ResearchWithdrawnKeloid Scar Following SurgeryUnited States
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University of ManitobaCompletedInternal Carotid Artery StenosisCanada