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Clinical Trials on Cholesterol Ester Storage Disease
Total 7679 results
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Duke UniversityGenzyme, a Sanofi CompanyCompleted
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Duke UniversityCompletedPompe DiseaseUnited States
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Duke UniversityCompleted
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Dwight Koeberl, M.D., Ph.D.Completed
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University of California, IrvineGenzyme, a Sanofi CompanyCompletedPompe DiseaseUnited States
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Amicus TherapeuticsTerminated
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University of FloridaTerminated
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O & O Alpan LLCCompleted
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Genzyme, a Sanofi CompanyCompleted
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type IIUnited States, France, Netherlands
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National Taiwan University HospitalUnknown
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Children's Healthcare of AtlantaTerminatedCongenital Disorders
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Genzyme, a Sanofi CompanyApproved for marketingGlycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Glycogenosis 2 | Pompe Disease (Late-Onset)United States
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Wake Forest UniversityActive, not recruitingDepression | Hypertension | Diabetes | Elevated CholesterolUnited States
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United Arab Emirates UniversityMohammed Bin Rashid University of Medicine and Health SciencesCompletedCardiovascular Risk Factor | Pre Diabetes | High Blood Pressure | Elevated LDL CholesterolUnited Arab Emirates
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SanofiRecruitingGlycogen Storage Disease Type IIBelgium, United States, Italy, Spain, Taiwan, United Kingdom, Netherlands, France, Germany
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Genzyme, a Sanofi CompanyActive, not recruitingGlycogen Storage Disease Type IIFrance
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type IIChina
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Duke UniversityNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)CompletedGlycogen Storage Disease Type IIUnited States
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Columbia UniversityWithdrawnGlycogen Storage Disease Type IIUnited States
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Libbs Farmacêutica LTDACompletedArterial Hypertension | Blood Glucose, High | Cholesterol; LipidosisBrazil
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NewAmsterdam PharmaActive, not recruitingDyslipidemias | Hypercholesterolemia | Hyperlipoproteinemias | Lipid Metabolism, Inborn Errors | Familial Hypercholesterolemia | Metabolic Disease | High Cholesterol | Genetic Disease, Inborn | Lipid Metabolism DisorderUnited States, Canada, Czechia, Georgia, Netherlands, Norway, Poland, South Africa, Spain, United Kingdom
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NewAmsterdam PharmaRecruitingDyslipidemias | Hypercholesterolemia | Familial Hypercholesterolemia | High Cholesterol | ASCVDUnited States
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Centre Hospitalier de CayenneCompleted
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Ohio State UniversityCompletedHypertension | Diabetes | Weight Loss | Smoking Reduction | Sedentary Behavior | Diet, Healthy | High CholesterolUnited States
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Astellas Gene TherapiesRecruitingPompe Disease (Late-onset)United States, Spain, France, Taiwan, Italy, Australia
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Amicus TherapeuticsCompletedPompe Disease (Late-onset)United States, Australia, Korea, Republic of, Japan, Taiwan, Belgium, Slovenia, New Zealand, United Kingdom, France, Argentina, Canada, Spain, Bosnia and Herzegovina, Germany, Sweden, Hungary, Austria, Bulgaria, Denmark, Greece, I... and more
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Duke UniversityCompleted
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Amicus TherapeuticsTerminatedLate-onset Pompe DiseaseUnited States, Canada, Australia, Belgium
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BioMarin PharmaceuticalTerminatedLate-onset Pompe DiseaseUnited States, United Kingdom, Germany, France, Italy, Portugal, Belgium, Netherlands
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Instituto Materno Infantil Prof. Fernando FigueiraFederal University of Paraíba; Professor Fernando Figueira Integral Medicine...CompletedHypoglycemia | Blood Pressure | Nitrate | Lactate | Heart Rate and Rhythm Disorders | Cholesterol (Total and HDL) | Abnormality in Fetal Heart Rate or Rhythm, Unspecified as to Episode of CareBrazil
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Huashan HospitalNot yet recruitingPompe Disease (Late-onset)China
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Rambam Health Care CampusRecruitingPompe Disease Infantile-OnsetIsrael
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Astellas Gene TherapiesRecruitingPompe Disease (Late-onset)United States, United Kingdom
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Amicus TherapeuticsRecruitingPompe Disease (Late-onset)United States, Japan, Taiwan, Australia, Canada, Italy, Germany
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Genzyme, a Sanofi CompanyRecruitingGlycogen Storage Disease Type II | Pompe DiseaseHungary, Croatia, Serbia, United States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, Chile, China, Colombia, Denmark, France, Germany, Greece, Hong Kong, India, Indonesia, Israel, Italy, Japan, Jordan, Korea, Republic of, Kuwait and more
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Amicus TherapeuticsActive, not recruitingPompe Disease (Late-onset)United States, Germany, Taiwan, Belgium, Australia, Slovenia, Spain, Netherlands, Hungary, Japan, Austria, United Kingdom, France, Argentina, Canada, Sweden, Denmark, New Zealand, Greece, Korea, Republic of, Bosnia and Herzegovina, Ita... and more
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Duke UniversityGenzyme, a Sanofi CompanyActive, not recruitingPompe Disease (Late-onset) | Pompe Disease | GAA DeficiencyUnited States
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Amicus TherapeuticsAvailablePompe Disease Infantile-OnsetTaiwan, United States, Italy
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BioMarin PharmaceuticalTerminatedLate-onset Pompe DiseaseUnited States, United Kingdom
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Duke UniversityWithdrawnPompe Disease (Late-onset)United States
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Rambam Health Care CampusCompletedEnzyme Replacement Therapy in Pompe Disease
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Pompe Disease Infantile-OnsetUnited States, France, South Africa
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Amicus TherapeuticsRecruitingPompe DiseaseUnited States, United Kingdom, Germany
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Duke UniversitySanofiRecruiting
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Duke UniversityGenzyme, a Sanofi CompanyRecruitingPompe DiseaseUnited States
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Genzyme, a Sanofi CompanyCompleted
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Valerion Therapeutics, LLCTerminatedPompe DiseaseUnited States, United Kingdom
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University of FloridaNational Heart, Lung, and Blood Institute (NHLBI)CompletedPompe DiseaseUnited States
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BioMarin PharmaceuticalCompletedPompe DiseaseUnited States, United Kingdom, France, Australia, Germany