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Clinical Trials on Cholesteryl Ester Storage Disease in Brazil
Total 130 results
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AlexionRecruitingWolman Disease | Cholesterol Ester Storage Disease | Lysosomal Acid Lipase Deficiency | Acid Cholesteryl Ester Hydrolase Deficiency, Type 2 | Acid Lipase Deficiency | LIPA Deficiency | LAL-DeficiencyFrance, Belgium, United States, Spain, Germany, Greece, Israel, Italy, Slovenia, United Kingdom, Brazil, Canada, Denmark, Australia, Croatia, Czechia, Ireland, Mexico, Netherlands, Poland, Portugal, Saudi Arabia
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase DeficiencySpain, Germany, Italy, United States, Croatia, Canada, Russian Federation, Denmark, United Kingdom, Belgium, Mexico, Australia, Netherlands, Brazil, Turkey
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Hospital de Clinicas de Porto AlegreConselho Nacional de Desenvolvimento Científico e Tecnológico; Fundação Médica...CompletedGlycogen Storage Disease Type IBrazil
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Libbs Farmacêutica LTDACompletedArterial Hypertension | Blood Glucose, High | Cholesterol; LipidosisBrazil
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Instituto Materno Infantil Prof. Fernando FigueiraFederal University of Paraíba; Professor Fernando Figueira Integral Medicine...CompletedHypoglycemia | Blood Pressure | Nitrate | Lactate | Heart Rate and Rhythm Disorders | Cholesterol (Total and HDL) | Abnormality in Fetal Heart Rate or Rhythm, Unspecified as to Episode of CareBrazil
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University of Sao Paulo General HospitalPfizerRecruiting
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University of Campinas, BrazilCompletedEnd-stage Renal DiseaseBrazil
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Amicus TherapeuticsCompletedFabry DiseaseAustralia, Brazil
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Faculdade de Ciências Médicas da Santa Casa de...CompletedHyperphosphatemia | End-stage Renal DiseaseBrazil
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Ultragenyx Pharmaceutical IncActive, not recruitingGlycogen Storage Disease Type IAUnited States, Brazil, Canada, Denmark, Germany, Italy, Netherlands, Spain
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AC Camargo Cancer CenterUnknownColon Cancer Stage IIb | Rectum Cancer, Adenocarcinoma | Colon Cancer Stage IIIa | Colon Cancer Stage IIIc | Colon Cancer Stage IIIbBrazil
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Instituto do Cancer do Estado de São PauloUnknown
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University of Campinas, BrazilRecruitingEnd-stage Kidney DiseaseBrazil
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ArmaGen, IncCompletedMucopolysaccharidosis IBrazil
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University of Sao Paulo General HospitalCompletedEnd-stage Renal Disease | Myocardial StunningBrazil
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ArmaGen, IncCompletedMucopolysaccharidosis IBrazil
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Horizon Pharma USA, Inc.Completed
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Universidade Católica de PelotasCompleted
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis IBrazil, Russian Federation
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Azafaros A.G.Active, not recruitingNiemann-Pick Disease, Type C | GM2 GangliosidosisBrazil
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AVROBIOTerminatedFabry DiseaseAustralia, Brazil
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Universidade Federal de PernambucoCompleted
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TakedaCompletedMucopolysaccharidosis (MPS)Brazil
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BioMarin PharmaceuticalTerminatedLate-onset Pompe Patients Untreated or Treated With rhGAASpain, Slovenia, Serbia, Korea, Republic of, Greece, Australia, Singapore, Brazil, Canada, Taiwan, Ireland, Poland, Romania
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Hospital Israelita Albert EinsteinUnknownEnd Stage Liver Disease | Hepatic EncephalopathyBrazil
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Universidade Federal FluminenseNot yet recruitingInflammation | Chronic Kidney Diseases | Inflammatory Response | Oxidative Stress | Chronic Kidney Disease stage4 | Chronic Kidney Disease stage3 | Chronic Kidney Disease Stage 3B | Intestinal Microbiota | Chronic Kidney Disease Stage 3ABrazil
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University of PennsylvaniaPassage Bio, Inc.RecruitingGM1 GangliosidosisUnited States, Turkey, Brazil, Canada, United Kingdom
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University of Sao PauloActive, not recruitingRectal Cancer | Rectal Cancer Stage IBrazil
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Hospital do CoracaoPfizerRecruitingMetastatic Breast Cancer | Breast Cancer Stage IVBrazil
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Instituto do Cancer do Estado de São PauloRecruiting
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Instituto do Cancer do Estado de São PauloCompleted
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JCR Pharmaceuticals Co., Ltd.Completed
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REGENXBIO Inc.Enrolling by invitation
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JCR Pharmaceuticals Co., Ltd.Active, not recruitingMucopolysaccharidosis IIBrazil
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AC Camargo Cancer CenterTerminatedTrastuzumab to Patients With Advanced Gastric Cancer With HER2 Positive Expression in CTC (GASTHER2)Gastric Cancer Stage IVBrazil
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Helady Pinheiro, MD, PhDNovartisTerminatedEnd Stage Renal Failure With Renal TransplantBrazil
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Grupo de Estudos Multicentricos em Onco-HematologiaUnknownMultiple Myeloma Stage IBrazil
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Amicus TherapeuticsCompletedFabry DiseaseJapan, Taiwan, Turkey, United States, Brazil
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Amicus TherapeuticsCompletedFabry DiseaseUnited States, Australia, France, United Kingdom, Brazil, Canada
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II;Pompe's DiseaseCzechia, Taiwan, Belgium, Germany, Korea, Republic of, United States, Argentina, Australia, Austria, Brazil, Canada, Denmark, France, Hungary, Italy, Japan, Mexico, Netherlands, Poland, Portugal, Russian Federation, Spain, Switzerland, Turk... and more
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Universidade Federal de Santa MariaUnknownPeriodontitis | Chronic Kidney Disease Stage 5Brazil
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LYSOGENECompletedMucopolysaccharidosis IIIAGermany, Brazil, United Kingdom, France, Netherlands
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Hospital de Clinicas de Porto AlegreUnknownKidney Failure, Chronic | End-Stage Renal DiseaseBrazil
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Universidade de Passo FundoFederal University of Rio Grande do SulCompletedHemodialysis | End Stage Renal Disease | Blood PressureBrazil
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Hospital Israelita Albert EinsteinCompletedNon-small Cell Lung Cancer Stage IBrazil
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Azafaros A.G.Active, not recruitingGM1 Gangliosidosis | Tay-Sachs Disease | Sandhoff DiseaseUnited States, Brazil, France, Germany, Italy, United Kingdom
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JCR Pharmaceuticals Co., Ltd.Active, not recruitingMucopolysaccharidosis IUnited States, Brazil, Japan
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AVROBIOTerminatedFabry DiseaseUnited States, Australia, Brazil
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Amicus TherapeuticsTerminatedFabry DiseaseUnited Kingdom, United States, Australia, Brazil, France
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JCR Pharmaceuticals Co., Ltd.CompletedMucopolysaccharidosis IUnited States, Brazil, Japan