- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Complement Deficiencies in United States
Total 1013 results
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Prothena Biosciences Ltd.RecruitingLight Chain (AL) AmyloidosisUnited States, Korea, Republic of, Australia, Denmark, France, Italy, Spain, Israel, Taiwan, Austria, Canada, Czechia, Germany, Greece, Hungary, Japan, Netherlands, Poland, Portugal, Turkey, United Kingdom, Belgium, Ireland
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Hospital for Special Surgery, New YorkActive, not recruiting
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Oncopeptides ABPRA Health SciencesTerminatedAL AmyloidosisSpain, United Kingdom, Germany, Norway, Israel, France, United States, Czechia, Greece
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Massachusetts General HospitalThe Salah Foundation; MGH cure ALS FundCompletedAmyotrophic Lateral SclerosisUnited States
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University of MiamiCompleted
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Neuraltus Pharmaceuticals, Inc.CompletedAmyotrophic Lateral SclerosisUnited States
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Massachusetts General HospitalALS AssociationCompleted
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Washington University School of MedicineMassachusetts General HospitalSuspendedAmyotrophic Lateral Sclerosis, Familial | Amyotrophic Lateral Sclerosis, SporadicUnited States
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Tammie L. S. Benzinger, MD, PhDCompletedAmyotrophic Lateral Sclerosis (ALS)United States
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Mayo ClinicRecruitingAortic Stenosis | Transthyretin Amyloidosis | Transthyretin Cardiac Amyloidosis | Transthyretin Amyloid CardiomyopathyUnited States
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Tufts Medical CenterCompletedMinimal Residual Disease as a Possible Predictive Factor for Relapse in Patients With AL AmyloidosisAmyloidosis | Primary AmyloidosisUnited States
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Memorial Sloan Kettering Cancer CenterVanderbilt University Medical Center; Tufts Medical CenterActive, not recruiting
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Prothena Biosciences Ltd.CompletedPrimary AmyloidosisUnited States
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Flex Pharma, Inc.WithdrawnAmyotrophic Lateral Sclerosis | FasciculationUnited States
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Emory UniversityALS AssociationCompletedAmyotrophic Lateral Sclerosis (ALS)United States
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CSL BehringCompletedHereditary AngioedemaCanada, Australia, Germany, United States, Israel
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National Institute of Neurological Disorders and...RecruitingAmyotrophic Lateral Sclerosis Type 4 | Inherited Neurological Disorders of RNA ProcessingUnited States
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Massachusetts General HospitalALS Therapy Development InstituteCompleted
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BioCryst PharmaceuticalsCompletedHereditary Angioedema | HAEFrance, United Kingdom, Germany, United States, Belgium, Hungary, Italy, Canada
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Brainstorm-Cell TherapeuticsNo longer availableAmyotrophic Lateral SclerosisUnited States
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ShireCompletedHereditary AngioedemaUnited States
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Columbia UniversityRecruitingNeurodegenerative Diseases | Amyotrophic Lateral Sclerosis | Alzheimer DiseaseUnited States
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National Institute of Allergy and Infectious Diseases...Active, not recruitingPGM3 Deficiency | Eosinophilic and/or Atopic Dermatitis | OSMR Deficiency | Primary Localized Cutaneous Amyloidosis | Hereditary Alpha-tryptasemiaUnited States
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Boston Medical CenterCompletedMultiple MyelomaUnited States
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BioMarin PharmaceuticalActive, not recruitingHereditary Angioedema | HAESpain, United States, Australia
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TakedaRecruitingHereditary Angioedema (HAE)United Kingdom
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Memorial Sloan Kettering Cancer CenterJanssen Scientific Affairs, LLCActive, not recruitingMultiple Myeloma | AL AmyloidosisUnited States
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Barrow Neurological InstituteArizona State UniversityCompletedAmyotrophic Lateral Sclerosis | ALS | Lou Gehrig DiseaseUnited States
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Vaishali SanchorawalaCelgene CorporationCompletedMultiple MyelomaUnited States
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Boston Medical CenterCompletedMultiple MyelomaUnited States
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ShireCompletedHereditary AngioedemaUnited States, Canada, Germany, Hungary, Spain
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Novo Nordisk A/SActive, not recruitingTransthyretin Amyloid Cardiomyopathy (ATTR CM)United States, Netherlands, Spain, Portugal, Canada, Czechia, France, Germany, Italy, Japan
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Intellia TherapeuticsNot yet recruitingHereditary AngioedemaFrance, New Zealand, United Kingdom
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University of FloridaCompletedNeuromuscular Diseases | Amyotrophic Lateral Sclerosis (ALS)United States
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The Cleveland ClinicCompletedAmyloidosis | Spinal Stenosis | Amyloid | Transthyretin Amyloidosis | Primary Amyloidosis of Light Chain TypeUnited States
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M.D. Anderson Cancer CenterCompletedMultiple Myeloma | Primary AmyloidosisUnited States
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Novo Nordisk A/SRecruitingTransthyretin Amyloid Cardiomyopathy (ATTR CM)United States, Netherlands, Germany, Canada, Czechia, France, Italy, Portugal, Spain
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Washington University School of MedicineEnrolling by invitationMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Lou Gehrig Disease | Familial Amyotrophic Lateral Sclerosis | Motor Neuron Disease, FamilialUnited States
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Alnylam PharmaceuticalsNo longer availableTransthyretin-mediated Amyloidosis With Cardiomyopathy | ATTR Amyloidosis With CardiomyopathyUnited States
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BioCryst PharmaceuticalsCompletedHereditary AngioedemaGermany, United Kingdom
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Barrow Neurological InstituteMassachusetts General Hospital; Genentech, Inc.; ALS Association; Barrow Neurological...CompletedMotor Neuron Disease | Amyotrophic Lateral Sclerosis | ALS | Lou Gehrig's DiseaseUnited States
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ShireCompletedHereditary Angioedema (HAE)United States, Jordan, Italy
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Brainstorm-Cell TherapeuticsCalifornia Institute for Regenerative Medicine (CIRM)CompletedAmyotrophic Lateral Sclerosis (ALS)United States
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Washington University School of MedicineKaryopharm Therapeutics IncRecruitingMultiple Myeloma | Myeloma-Associated AmyloidosisUnited States
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Bronx VA Medical CenterCompletedAmyotrophic Lateral Sclerosis | Spinal Cord InjuriesUnited States
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SanofiDenali Therapeutics Inc.TerminatedAmyotrophic Lateral SclerosisUnited States, Netherlands
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Johns Hopkins UniversityALS AssociationCompletedAmyotrophic Lateral SclerosisUnited States
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University of Texas Southwestern Medical CenterNational Heart, Lung, and Blood Institute (NHLBI); Columbia University; The Cleveland... and other collaboratorsRecruitingAmyloidosis, Familial | Amyloidosis, Hereditary | Amyloidosis Cardiac | Transthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin Gene MutationUnited States
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BioCryst PharmaceuticalsCompletedHereditary Angioedema | HAEUnited States, Austria, Canada, Czechia, France, Germany, Hungary, North Macedonia, Romania, Spain, United Kingdom
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The University of Texas Health Science Center at...ALS AssociationCompletedAmyotrophic Lateral Sclerosis | Respiratory Muscle WeaknessUnited States