- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Congenital Abnormalities in Hong Kong
Total 351 results
-
PTC TherapeuticsCystic Fibrosis Foundation; ECFS-Clinical Trial Network (ECFS-CTN)CompletedCystic FibrosisUnited States, Spain, United Kingdom, Netherlands, Germany, France, Belgium, Italy, Australia, Argentina, Brazil, Bulgaria, Canada, Greece, Israel, Poland
-
Children's Oncology GroupNational Cancer Institute (NCI)Active, not recruitingStage I Kidney Wilms Tumor | Stage II Kidney Wilms Tumor | Stage III Kidney Wilms Tumor | Stage IV Kidney Wilms Tumor | Adult Kidney Wilms Tumor | Beckwith-Wiedemann Syndrome | Childhood Kidney Wilms Tumor | Diffuse Hyperplastic Perilobar Nephroblastomatosis | Rhabdoid Tumor of the Kidney | Stage V Kidney...United States, Canada, Australia, New Zealand, Puerto Rico, Israel
-
Biohaven Pharmaceuticals, Inc.Active, not recruitingSpinocerebellar Ataxia Type 3 | Spinocerebellar Ataxias | Spinocerebellar Ataxia Type 1 | Spinocerebellar Ataxia Type 2 | Spinocerebellar Ataxia Type 6 | Spinocerebellar Ataxia Type 10 | Spinocerebellar Ataxia Type 7 | Spinocerebellar Ataxia Type 8United States, China
-
Regeneron PharmaceuticalsSanofiCompletedEczema, Atopic | Atopic DisordersUnited States
-
Baxalta now part of ShireBaxter BioScienceCompleted
-
BioCryst PharmaceuticalsCompletedHereditary Angioedema | Prophylaxis | HAEAustria, Denmark, France, Germany, Hungary, Israel, Italy, North Macedonia, Poland, Switzerland, United Kingdom, United States, Australia, Hong Kong, Korea, Republic of, New Zealand, Serbia, Slovakia, South Africa, Spain
-
LLS PedAL Initiative, LLCNational Cancer Institute (NCI); Children's Oncology GroupRecruitingAcute Myeloid Leukemia | Juvenile Myelomonocytic Leukemia | Acute Lymphoblastic Leukemia | Myelodysplastic Syndrome | Myeloid Leukemia Associated With Down Syndrome | Mixed Phenotype Acute Leukemia | Acute Myeloid Leukemia Post Cytotoxic Therapy | Myelodysplastic Syndrome Post Cytotoxic TherapyUnited States, Canada, Australia, Puerto Rico, New Zealand
-
Incyte CorporationRecruiting
-
Neurocrine BiosciencesCompletedTourette SyndromeUnited States
-
Vertex Pharmaceuticals IncorporatedCystic Fibrosis FoundationTerminated
-
Baxalta now part of ShireBaxalta Innovations GmbH, now part of ShireCompletedHemophilia AUnited States, Spain, Netherlands, Australia, Czechia, Korea, Republic of, Taiwan, Poland, Bulgaria, United Kingdom, Germany, Turkey, Israel, Malaysia, Ukraine, Russian Federation, Austria, Switzerland, Japan, Hong Kong, Lithuania, Roman... and more
-
Seattle Children's HospitalNational Heart, Lung, and Blood Institute (NHLBI); Cystic Fibrosis Foundation; CF Therapeutics Development Network Coordinating CenterCompletedCystic FibrosisUnited States
-
PTC TherapeuticsCystic Fibrosis FoundationCompletedCystic FibrosisUnited States, France, Belgium, United Kingdom, Spain, Canada, Germany, Israel, Italy, Netherlands, Sweden
-
Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, United Kingdom, Germany, Spain, Switzerland, Canada, Netherlands, Italy, Ireland, Sweden, France, Denmark
-
Humacyte, Inc.California Institute for Regenerative Medicine (CIRM); CTI Clinical Trial and...Active, not recruitingRenal Failure | Hemodialysis | End Stage Renal Disease | Vascular AccessUnited States
-
Children's Oncology GroupNational Cancer Institute (NCI)Active, not recruitingAcute Lymphoblastic Leukemia | Down Syndrome | Philadelphia Chromosome Positive | Childhood B Acute Lymphoblastic Leukemia With t(9;22)(q34.1;q11.2); BCR-ABL1 | Childhood B Acute Lymphoblastic Leukemia | Adult B Lymphoblastic Lymphoma | Ann Arbor Stage I B Lymphoblastic Lymphoma | Ann Arbor Stage... and other conditionsUnited States, Canada, Puerto Rico, Australia, New Zealand, Switzerland, Ireland
-
Kastle Therapeutics, LLCCompletedHypercholesterolemia | Heterozygous FamilialUnited States, Italy, Poland, Ukraine, United Kingdom, Germany, Hong Kong, Taiwan, Spain, Argentina, Belgium, Israel, Malaysia, South Africa, Turkey, Netherlands, Korea, Republic of, Canada, New Zealand, Russian Federation, Brazil, Austral... and more
-
ShionogiIntegriumCompletedCombined HyperlipidemiaUnited States
-
Regeneron PharmaceuticalsSanofiCompletedAtopic DermatitisUnited States
-
Vertex Pharmaceuticals IncorporatedCystic Fibrosis FoundationCompletedCystic FibrosisUnited States
-
Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Belgium, Netherlands, United Kingdom
-
Glenmark Pharmaceuticals Ltd. IndiaCompleted
-
QuantumLeap Healthcare CollaborativeM.D. Anderson Cancer Center; University of Colorado, Denver; University of Pennsylvania and other collaboratorsRecruitingCOVID-19United States
-
Horizon Pharma USA, Inc.Forest LaboratoriesCompletedCystic FibrosisUnited States, Australia, Israel, New Zealand, Canada
-
Anthera PharmaceuticalsCompletedCystic Fibrosis | Exocrine Pancreatic InsufficiencyUnited States
-
Regeneron PharmaceuticalsSanofiCompletedDermatitis, AtopicUnited States, Germany, Poland, United Kingdom
-
Children's Oncology GroupNational Cancer Institute (NCI)RecruitingRenal Cell Carcinoma | Wilms Tumor | Clear Cell Sarcoma of the Kidney | Papillary Renal Cell Carcinoma | Kidney Medullary Carcinoma | Diffuse Hyperplastic Perilobar Nephroblastomatosis | Rhabdoid Tumor of the Kidney | Congenital Mesoblastic Nephroma | Renal Cell Carcinoma Associated With Xp11.2 Translocations... and other conditionsUnited States, Canada, Puerto Rico, Australia, New Zealand, Israel, Switzerland
-
Regeneron PharmaceuticalsSanofiTerminatedAtopic DermatitisUnited States, Korea, Republic of, Belgium, Czechia, Germany, Poland, Spain
-
Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Canada, Germany, United Kingdom
-
Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Belgium, Netherlands, Australia, Germany, Ireland, United Kingdom
-
AbbVieJanssen Research & Development, LLC; Forest LaboratoriesCompleted
-
Genentech, Inc.TerminatedCystic FibrosisUnited States
-
BayerCompleted
-
Galderma R&DCompleted
-
TakedaCompletedEffect of Febuxostat on Renal Function in Patients With Gout and Moderate to Severe Renal ImpairmentRenal ImpairmentUnited States
-
Anthera PharmaceuticalsUnknownCystic Fibrosis | Exocrine Pancreatic InsufficiencyUnited States, Hungary, Israel, Lithuania, Poland, Spain, United Kingdom
-
Vertex Pharmaceuticals IncorporatedCompletedCystic Fibrosis, Homozygous for the F508del CFTR MutationUnited States, Germany, Canada, Netherlands, Czech Republic, Italy, Ireland, Sweden, United Kingdom, Australia, France
-
AbbVieVIVUS LLC; Cystic Fibrosis Foundation; Digestive Care, Inc.; Nestle Health ScienceTerminated
-
Laurent Pharmaceuticals Inc.Cystic Fibrosis FoundationCompletedCystic FibrosisUnited States, Australia, Canada
-
PfizerNo longer availableAtopic DermatitisBelgium, United States, Spain, Taiwan, Australia, Austria, Canada, Switzerland, Russian Federation, Greece, Mexico, Netherlands
-
Regeneron PharmaceuticalsSanofiCompletedDermatitis, AtopicUnited States, Germany, Poland, Canada, Czechia, United Kingdom
-
Children's Oncology GroupNational Cancer Institute (NCI)CompletedSecondary Acute Myeloid Leukemia | Childhood Acute Erythroleukemia (M6) | Childhood Acute Megakaryocytic Leukemia (M7) | Childhood Acute Monoblastic Leukemia (M5a) | Childhood Acute Monocytic Leukemia (M5b) | Childhood Acute Myeloblastic Leukemia With Maturation (M2) | Childhood Acute Myeloblastic... and other conditionsUnited States, Canada, Australia, Puerto Rico
-
AOBiome LLCbioRASI, LLCCompletedAtopic DermatitisUnited States
-
Anthera PharmaceuticalsCompletedCystic Fibrosis | Exocrine Pancreatic InsufficiencyUnited States, Hungary, Israel, Poland, Spain, Canada, Czechia
-
CF Therapeutics Development Network Coordinating...Cystic Fibrosis FoundationCompleted
-
NovartisTerminatedCystic FibrosisUnited States, Argentina, Brazil, Bulgaria, Canada, Chile, Lithuania, Mexico
-
National Institute of Allergy and Infectious Diseases...Eunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedHIV Infections | Dyslipidemia | Osteoporosis | Osteopenia | Lipodystrophy | HIV-Associated Lipodystrophy Syndrome | HIV Lipodystrophy SyndromeUnited States, Puerto Rico
-
Dermavant Sciences GmbHCompletedAtopic DermatitisUnited States, Canada
-
Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, France, Germany
-
Satsuma Pharmaceuticals, Inc.CompletedMigraine | Migraine Without Aura | Migraine With AuraUnited States