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Clinical Trials on Congenital Aplastic Anemia in Austria
Total 498 results
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Hoffmann-La RocheCompletedAnemiaItaly, Spain, Mexico, Hungary, Singapore, Greece, United Kingdom, Austria, Thailand, Germany, Poland, Russian Federation, Denmark, Brazil, Sweden, Czech Republic, Finland
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Akebia TherapeuticsCompletedAnemia | Kidney DiseaseUnited States
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AlbireoEnrolling by invitationBiliary AtresiaSpain, United States, Netherlands, Malaysia, Canada, Germany, Turkey, Italy, France, Australia, Poland, New Zealand
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OctapharmaRecruitingCongenital Antithrombin DeficiencySpain, Italy, United States, Serbia, France, Hungary, Austria, Germany, United Kingdom, Israel
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Hoffmann-La RocheCompletedChronic Renal AnemiaBelgium, Brazil, United Kingdom, Serbia, Spain, Germany, Korea, Republic of, Turkey, Lithuania, Italy, Czechia, Argentina, Australia, Croatia, France, Greece, Israel, Malaysia, Mexico, Panama, Philippines, Poland, Russian Federation, ... and more
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Sydney Children's Hospitals NetworkJohns Hopkins University; Children's Hospital of Philadelphia; University of... and other collaboratorsUnknownCharcot-Marie-Tooth DiseaseUnited States, Australia, Italy
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Neurocrine BiosciencesActive, not recruitingCongenital Adrenal HyperplasiaUnited States, Spain, Belgium, Austria, Bulgaria, Canada, Czechia, France, Germany, Greece, Israel, Italy, Netherlands, Poland, Portugal, Serbia, Sweden, United Kingdom
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Otsuka Pharmaceutical Europe LtdUnknownAutosomal Dominant Polycystic Kidney DiseaseSpain, United Kingdom, Germany, France, Belgium, Switzerland, Austria
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Hoffmann-La RocheCompletedAnemiaItaly, Spain, France, Canada, Hungary, United States, Germany, Belgium, Poland, Australia, Israel, United Kingdom, Czech Republic
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Novartis PharmaceuticalsCompletedTumors Characterized by Genetic Abnormalities of ALKAustralia, Belgium, Germany, Netherlands, Spain, Italy, Singapore, Korea, Republic of, United Kingdom, United States, Canada
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedLeukemiaUnited States, Australia, Canada
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Ionis Pharmaceuticals, Inc.BiogenActive, not recruitingAngelman SyndromeUnited States, Israel, Italy, France, Australia, United Kingdom
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CelgeneRecruitingPrimary Myelofibrosis | Myeloproliferative Disorders | Anemia | Myelofibrosis | Post-Polycythemia Vera MyelofibrosisFrance, Belgium, Spain, Australia, Canada, United States, Korea, Republic of, Romania, Japan, Israel, Italy, Austria, China, Czechia, Germany, Greece, Ireland, Poland, United Kingdom, Hong Kong, Hungary, Lebanon, Argentina, Chile, Colombia and more
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Children's Oncology GroupNational Cancer Institute (NCI)Active, not recruitingLymphoma | Diffuse Large B-Cell Lymphoma | Hodgkin Lymphoma | Burkitt Lymphoma | Anaplastic Large Cell LymphomaUnited States, Canada
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Pierre Fabre DermatologyCompletedInfantile HemangiomaGermany, United States, France, Spain, Peru, Australia, Lithuania, Italy, Canada, Czech Republic, Hungary, Mexico, New Zealand, Poland, Romania, Russian Federation
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited States, Netherlands, Austria, Spain, Poland, United Kingdom, Croatia, Germany, Malaysia, Australia, France, Israel, Thailand, Ukraine, Turkey
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Ascend Biopharmaceuticals LtdCompletedBasal Cell Nevus Syndrome | Skin Neoplasm | Nodular Basal Cell Carcinoma of SkinAustralia
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Natera, Inc.Children's Hospital of Philadelphia; Montefiore Medical Center; University of... and other collaboratorsCompletedPrader-Willi Syndrome | DiGeorge Syndrome | 22q11 Deletion Syndrome | Angelman Syndrome | Trisomy 21 | Trisomy 18 | Trisomy 13 | Monosomy X | Sex Chromosome Abnormalities | 1p36 Deletion Syndrome | Cri-du-Chat SyndromeUnited States, Australia, Ireland, Spain, Sweden, United Kingdom
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LMU KlinikumUniversity of Pisa; German Federal Ministry of Education and Research; European...RecruitingMitochondrial Diseases | MDS | Mitochondrial Myopathies | MELAS Syndrome | MIDD | Kearns-Sayre Syndrome | MERRF Syndrome | Barth Syndrome | Leigh Syndrome | MNGIE | LHON | Pearson Syndrome | NARP Syndrome | Coenzyme Q10 Deficiency | SANDO | SCAE | MIRAS | CPEOAustria, Germany, Italy
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Spruce BiosciencesActive, not recruitingCongenital Adrenal HyperplasiaUnited States, Australia, Brazil, Estonia, Germany, Korea, Republic of, Latvia, Lithuania, Poland, Romania, Spain, Sweden, Turkey, Canada, Italy, United Kingdom
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European Organisation for Research and Treatment...Medical Research CouncilCompletedBrain and Central Nervous System TumorsFrance, Switzerland, Netherlands, United Kingdom, Belgium, Germany, Italy, Sweden, Finland, Portugal, Austria, Hungary
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University of Alabama at BirminghamMedtronic; The Children's Tumor FoundationTerminatedNF1 | Congenital Pseudarthrosis of TibiaUnited States, Australia
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Novo Nordisk A/SCompletedHealthy | Congenital Bleeding Disorder | Haemophilia A | Haemophilia BAustria, Sweden, Spain, Switzerland, United Kingdom, Germany, Malaysia, Denmark, South Africa, Thailand, Italy
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ReCode TherapeuticsRecruitingPrimary Ciliary DyskinesiaUnited Kingdom, United States, Australia, New Zealand
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Rhythm Pharmaceuticals, Inc.CompletedBardet-Biedl Syndrome | POMC Deficiency Obesity | PCSK1 Deficiency Obesity | LEPR Deficiency ObesityUnited States, Australia, Spain, United Kingdom
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AmgenCompletedHeart Failure | Cardiovascular Disease | Anemia | Ventricular Dysfunction | Congestive Heart FailureUnited States, France, Germany, Italy, Netherlands, Spain, United Kingdom, Belgium, Czechia, Denmark, Hungary, Canada, Australia, Hong Kong, South Africa, Chile, Austria, Puerto Rico, Slovakia, Argentina, Israel, Russian Federation, Polan... and more
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SandozCompletedAnemia | Chronic Kidney Disease (CKD)United States
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Krystal Biotech, Inc.CompletedDystrophic Epidermolysis Bullosa | Recessive Dystrophic Epidermolysis Bullosa | Dominant Dystrophic Epidermolysis Bullosa | DEB - Dystrophic Epidermolysis BullosaUnited States
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Akebia TherapeuticsCompletedAnemia | Chronic Kidney DiseaseUnited States
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Nationwide Children's HospitalNovartisNot yet recruitingGlioblastoma | Glioblastoma Multiforme | High Grade Glioma | Anaplastic Astrocytoma | Diffuse Intrinsic Pontine Glioma | Diffuse Midline Glioma, H3 K27M-Mutant | WHO Grade III Glioma | Metastatic Brain Tumor | WHO Grade IV GliomaUnited States, Australia, United Kingdom, Canada, Germany, Netherlands
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Nationwide Children's HospitalNot yet recruitingGlioblastoma | Glioblastoma Multiforme | High Grade Glioma | Anaplastic Astrocytoma | Diffuse Intrinsic Pontine Glioma | Diffuse Midline Glioma, H3 K27M-Mutant | WHO Grade III Glioma | Metastatic Brain Tumor | WHO Grade IV GliomaUnited States, Australia, United Kingdom, Canada, Germany, Netherlands
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Bristol-Myers SquibbRecruitingMyelodysplastic SyndromesCanada, United States, China, Australia, France, Greece, Hungary, Germany, Italy, Czechia, Poland, Mexico, Spain, Brazil, Colombia, India, Argentina, Puerto Rico
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Yale UniversityNational Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health...CompletedHypertrophic Cardiomyopathy | Long QT SyndromeUnited States, United Kingdom, Canada, Australia, New Zealand
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Healx LimitedWithdrawnFragile X SyndromeUnited States, Australia
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Glanzmann's DiseaseSpain, Bulgaria, Pakistan, Belgium, Germany, France, United Kingdom, Italy, Hungary, Netherlands, United States, Algeria, Austria, Sweden, Switzerland
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Akebia TherapeuticsCompletedAnemia | Dialysis-Dependent Chronic Kidney DiseaseUnited States, Italy, Canada, Korea, Republic of, United Kingdom, Australia, Germany, Israel, France, Portugal, Bulgaria, Russian Federation, Ukraine, Poland, Brazil, Argentina, Mexico, Serbia
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Icahn School of Medicine at Mount SinaiEunice Kennedy Shriver National Institute of Child Health and Human Development...Active, not recruitingCraniosynostosisUnited States, Germany, France, Spain, United Kingdom
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Nationwide Children's HospitalPfizerNot yet recruitingGlioblastoma | Glioblastoma Multiforme | High Grade Glioma | Anaplastic Astrocytoma | Diffuse Intrinsic Pontine Glioma | WHO Grade III Glioma | WHO Grade IV Glioma | Infant Type Hemispheric Glioma | Diffuse Midline Glioma, H3K27-alteredUnited States, Australia, Canada, Germany, Netherlands
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AmgenCompletedAnemia | Chronic Kidney DiseaseFrance, Italy, United Kingdom, Belgium, Hungary, Spain, Israel, Portugal, Bulgaria, Serbia, Poland, Romania, Greece, Australia, Denmark, Russian Federation, Slovakia, Germany, Latvia, Estonia, Slovenia, Czech Republic, Mexico
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited States, Austria, Serbia, Germany, Japan, France
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Columbia UniversityNational Institute of Neurological Disorders and Stroke (NINDS)CompletedArteriovenous Malformations, CerebralUnited States, Brazil, Canada, Australia, Austria, Finland, France, Germany, Italy, Korea, Republic of, Netherlands, Spain, Switzerland, United Kingdom
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Ovid Therapeutics Inc.CompletedPrimary Disease or Condition Being Studied: Angelman Syndrome (AS)United States, Australia, Germany, Israel, Netherlands
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Children's Oncology GroupPfizer; Erasmus Medical Center; Dutch Childhood Oncology Group; Innovative Therapies...Active, not recruitingAccelerated Phase Chronic Myelogenous Leukemia | Chronic Phase Chronic Myelogenous Leukemia | Blastic Phase Chronic Myelogenous Leukemia | Philadelphia Chromosome Positive CMLUnited States
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Zynerba Pharmaceuticals, Inc.RecruitingFragile X SyndromeUnited States, Australia, United Kingdom, Ireland
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Ultragenyx Pharmaceutical IncNot yet recruitingAngelman SyndromeUnited States, Australia, Canada, Germany, United Kingdom, Israel, France, Spain
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AffymaxTakedaCompletedAnemia | Chronic Kidney Disease | Chronic Renal FailureUnited States, Puerto Rico
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AMO Pharma LimitedRecruitingCongenital Myotonic DystrophyUnited States, Canada, Australia, New Zealand
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AlbireoRecruitingBiliary AtresiaNetherlands, United States, Spain, Italy, Taiwan, Korea, Republic of, France, Germany, United Kingdom, Canada, Belgium, China, Australia, Poland, Turkey, Malaysia, New Zealand, Hungary, Israel
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AMO Pharma LimitedCompletedCongenital Myotonic DystrophyUnited States, Canada, New Zealand, Australia, United Kingdom
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A | Haemophilia BBelgium, Germany, France, United Kingdom, Italy, Hungary, Austria, Sweden, Iran, Islamic Republic of, Argentina, Ireland, Poland, Portugal, Slovakia