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Clinical Trials on Congenital Fibrinogen Deficiency in Canada
Total 1082 results
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Fundación Española de Hematología y HemoterapíaRecruitingGaucher Disease | Acid SphingoMyelinase DeficiencySpain
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Astria Therapeutics, Inc.RecruitingHereditary AngioedemaUnited States, United Kingdom, Canada, Germany, Bulgaria, Czechia
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Johns Hopkins Bloomberg School of Public HealthNational Institute of Allergy and Infectious Diseases (NIAID)Completed
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Fundación Pública Andaluza Progreso y SaludCompletedArteriovenous Fistula Renal Dialysis Devices ObstructionSpain
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Sideris PharmaceuticalsTerminatedIron Overload | Beta-ThalassemiaUnited States, Canada, Lebanon, Thailand, Turkey
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI); Thalassemia Clinical Research...CompletedThalassemiaUnited States, Canada, United Kingdom
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QED Therapeutics, Inc.RecruitingHypochondroplasiaUnited States, Norway, Australia, Singapore, United Kingdom, Canada, France, Germany, Portugal, Spain, Sweden
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ShireCompletedHereditary Angioedema (HAE)United States, Canada, Jordan
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Italy, Canada, France, United Kingdom, Austria, Germany
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Ultragenyx Pharmaceutical IncTerminatedWilson Disease | Ornithine Transcarbamylase Deficiency | Glycogen Storage Disease Type IASpain, United Kingdom, Canada, United States, Brazil
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BioMarin PharmaceuticalRecruitingHypochondroplasiaUnited States, Spain, Canada, France, Japan, Australia, Italy, Argentina, Brazil, Germany, United Kingdom
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Gilead SciencesCompletedHIV InfectionsUnited States, United Kingdom, Panama
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsActive, not recruitingHematologic Diseases | Genetic Diseases, Inborn | Hemoglobinopathies | Thalassemia | Beta-ThalassemiaUnited States, United Kingdom, Canada, Germany, Italy
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Baxalta now part of ShireCompleted
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ViiV HealthcarePfizerTerminatedHIV InfectionsUnited States, Canada
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ShireTakeda Development Center Americas, Inc.No longer availableAngioedema | Hereditary Angioedema (HAE)United States, Canada, Germany, Hungary, Spain
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Novartis PharmaceuticalsTerminatedSickle Cell DiseaseBahrain, Kuwait, Qatar, Saudi Arabia
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PharmassetCompletedHIV InfectionsUnited States, Argentina, Mexico, Panama
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Arbor Research Collaborative for HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)RecruitingBiliary Atresia | Neonatal CholestasisUnited States, Canada
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CSL BehringCompletedEmphysema | Alpha1-proteinase Inhibitor DeficiencyAustralia, Russian Federation, United States, Denmark, Estonia, Finland, Germany, Ireland, Poland, Romania, Sweden, Canada, Czech Republic
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Ultragenyx Pharmaceutical IncRecruitingOTC DeficiencyUnited States, Portugal, Italy, Spain, United Kingdom, Japan, Canada, Germany, France, Argentina, Netherlands, Brazil
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Abbott Medical DevicesRecruitingStroke | Patent Foramen OvaleUnited States, Germany, Canada, Switzerland, Italy, Portugal, United Kingdom
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AbbottCompleted
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Cytheris SACompletedHIV Infections | LymphopeniaUnited States, France, Canada, Italy
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GLWL Research Inc.CompletedPrader-Willi SyndromeUnited States, Canada
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Boston Children's HospitalUniversity of California, San Diego; Food and Drug Administration (FDA); Angelman... and other collaboratorsRecruiting
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ShireTerminatedBeta-Thalassemia | Transfusional Iron OverloadUnited States, Lebanon, Canada, Italy, Turkey
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Novartis PharmaceuticalsCompletedMyelofibrosis | Sickle Cell Disease | Thalassemia | Diamond Blackfan AnemiaUnited States, Netherlands, Taiwan, Thailand, Italy, Germany, Spain, Canada, Belgium, Greece, Turkey, United Kingdom
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Ottawa Hospital Research InstituteOntario Lung AssociationWithdrawnHIV Infections | TuberculosisCanada, South Africa
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ShireCompletedHereditary Angioedema (HAE)United States, Jordan, Canada
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National Cancer Institute (NCI)WithdrawnHematopoietic and Lymphoid Cell Neoplasm | Lynch Syndrome | Refractory Lymphoma | Refractory Malignant Solid Neoplasm | Recurrent Lymphoma | Recurrent Malignant Solid Neoplasm | Recurrent Neuroblastoma | Refractory Neuroblastoma | Recurrent Primary Central Nervous System Neoplasm | Refractory Primary Central... and other conditionsUnited States, Canada
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GlaxoSmithKlineTerminatedTelangiectasia, Hereditary HemorrhagicUnited States, Canada
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Otsuka Canada Pharmaceutical Inc.RecruitingAutosomal Dominant Polycystic Kidney Disease (ADPKD)Canada
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AlbireoEnrolling by invitationBiliary AtresiaSpain, United States, Netherlands, Malaysia, Canada, Germany, Turkey, Italy, France, Australia, Poland, New Zealand
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Novartis PharmaceuticalsCompletedSickle Cell AnemiaTurkey, United States, Germany, Canada, United Kingdom, Israel, South Africa
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Baxalta now part of ShireCompleted
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University of California, DavisUniversity of Alberta; St. Justine's HospitalCompletedNeurobehavioral Manifestations | Genetic Diseases, X-Linked | Intellectual Disability | Fragile X Syndrome | Sex Chromosome Disorders | Fragile X Mental Retardation Syndrome | Trinucleotide Repeat Expansion | Fra(X) Syndrome | FXS | Mental Retardation, X LinkedUnited States, Canada
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OctapharmaCompletedPrimary and Secondary Immunodeficiency and Other Conditions Requiring Regular Administration of Octagam 5% or 10% IVIGCanada, Austria, France, Spain, United Kingdom
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Canada, United Kingdom, Portugal
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI)CompletedHepatitis C | ThalassemiaUnited States, United Kingdom, Canada
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Pediatric Spine FoundationColumbia UniversityRecruitingEarly-Onset Scoliosis Deformity of SpineUnited States, Canada, Finland, Hong Kong
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IrsiCaixaWithdrawnHIV InfectionSpain, Netherlands, Italy
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Forma Therapeutics, Inc.RecruitingSickle Cell Disease | ThalassemiaUnited States, Lebanon, Canada
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CSL BehringCompletedHereditary AngioedemaUnited States, Germany, Japan, Hungary, Canada, Netherlands, Israel
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National Institute of Allergy and Infectious Diseases...National Center for Advancing Translational Sciences (NCATS); Primary Immune...Enrolling by invitationADA-SCID | Omenn Syndrome | SCID | Reticular Dysgenesis | XSCID | Leaky SCIDUnited States, Canada
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McGill University Health Centre/Research Institute...RecruitingDiabetes Mellitus, Type 1 | Wolfram Syndrome | Neonatal Diabetes | Monogenic Diabetes | Maturity-onset Diabetes in the Young (MODY) | Wolcott-Rallison Syndrome | Mitochondrial DiabetesCanada
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Grifols Therapeutics LLCCompletedPrimary ImmunodeficiencyUnited States, Canada
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Richard Barohn, MDRare Diseases Clinical Research Network; Office of Rare Diseases (ORD)CompletedMyotonic Disorders | Myotonia Congenita | Nondystrophic MyotoniasCanada, United States, United Kingdom
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TakedaCompletedHereditary AngioedemaBelgium, Bulgaria, Estonia, Spain, Hungary, Israel, Germany, Czechia, Portugal, Greece, Lithuania, Poland, Latvia, Croatia, Slovakia, Austria, Canada, Ireland, North Macedonia, Romania, Serbia, Slovenia
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Hoffmann-La RocheCompletedHIV InfectionsCanada, United States, Puerto Rico