- ICH GCP
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Clinical Trials on Congenital Malformation in New Zealand
Total 850 results
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Boston Children's HospitalAgios Pharmaceuticals, Inc.CompletedPyruvate Kinase Deficiency | Congenital Non-Spherocytic Hemolytic AnemiaUnited States, Germany, Canada, Czechia, Italy, Netherlands
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Ann & Robert H Lurie Children's Hospital of ChicagoColumbia University; University of Illinois at Chicago; St. Jude Children's Research... and other collaboratorsRecruitingSickle Cell DiseaseUnited States
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Novartis PharmaceuticalsCompletedMyelofibrosis | Sickle Cell Disease | Thalassemia | Diamond Blackfan AnemiaUnited States, Netherlands, Taiwan, Thailand, Italy, Germany, Spain, Canada, Belgium, Greece, Turkey, United Kingdom
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New York Medical CollegeJohns Hopkins University; Baylor College of Medicine; University of California... and other collaboratorsRecruitingSickle Cell DiseaseUnited States
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IBSA Institut Biochimique SACromsourceActive, not recruitingCongenital HypothyroidismUnited States
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Weill Medical College of Cornell UniversityNational Institutes of Health (NIH); PWSAUSATerminatedPrader-willi SyndromeUnited States
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NYU Langone HealthWinthrop University HospitalWithdrawn
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The National Institute of LymphologyThe DrMarga Practice Group; The Center for Restorative Breast Surgery, LLCUnknownBreast Cancer | Hereditary Breast/Ovarian Cancer (brca1, brca2) | Congenital Lymphedema | Acquired LymphedemaUnited States
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New York Medical CollegeJohns Hopkins UniversityCompletedSickle Cell Disease | Acute Chest SyndromeUnited States
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Rowan UniversityUniversity of Pennsylvania; FRAXA Research FoundationUnknown
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Albert Einstein College of MedicineTerminatedSickle Cell Anemia | Acute Chest SyndromeUnited States
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Agios Pharmaceuticals, Inc.Active, not recruitingPyruvate Kinase DeficiencyUnited States, Canada, Netherlands, United Kingdom, France, Italy
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Medical College of WisconsinNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsCompletedSickle Cell DiseaseUnited States
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Mirum Pharmaceuticals, Inc.CompletedAlagille SyndromeFrance, Belgium, Poland, Australia, Spain, United Kingdom
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Montefiore Medical CenterRecruitingHyperphagia | Prader-Willi SyndromeUnited States
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Montefiore Medical CenterFoundation for Prader-Willi ResearchCompletedHyperphagia | Prader-Willi SyndromeUnited States
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Phoenix Tissue Repair, Inc.Phoenix Tissue Repair, a BridgeBio companyCompletedRecessive Dystrophic Epidermolysis BullosaUnited States
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Columbia UniversityInternational Agency for Research on CancerRecruitingAcute Lymphoblastic Leukemia | Nutrition Aspect of Cancer | Genetic Predisposition | MicrotiaUnited States, Guatemala, Brazil, Honduras, India, Tanzania
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AlbireoActive, not recruitingAlagille SyndromeUnited Kingdom, United States, France, Germany, Netherlands, Italy, Belgium, Malaysia, Poland, Turkey
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With InhibitorsUnited States
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI)Completed
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OctapharmaCompletedCongenital Fibrinogen Deficiency | AfibrinogenemiaIran, Islamic Republic of, United States, Bulgaria, India, Switzerland, United Kingdom
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W.L.Gore & AssociatesRecruitingStroke | PFO - Patent Foramen OvaleUnited States
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Scioderm, Inc.Amicus TherapeuticsCompletedEpidermolysis BullosaItaly, Spain, Serbia, United States, Australia, Netherlands, Austria, Germany, Israel, Lithuania, France, United Kingdom, Poland
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The Rogosin InstituteWeill Medical College of Cornell University; Rockefeller UniversityCompletedChronic Kidney Disease | Polycystic Kidney, Autosomal DominantUnited States
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Dartmouth-Hitchcock Medical CenterGenentech, Inc.TerminatedVon Hippel Lindau Disease | HemangioblastomasUnited States
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Roswell Park Cancer InstituteActive, not recruitingAcute Myeloid Leukemia | Polycythemia Vera | Myelofibrosis | Chronic Myelomonocytic Leukemia | Waldenstrom Macroglobulinemia | Acute Lymphoblastic Leukemia | Chronic Lymphocytic Leukemia | Secondary Acute Myeloid Leukemia | Sickle Cell Disease | Myelodysplastic Syndrome | Plasma Cell Myeloma | Chronic Granulomatous... and other conditionsUnited States
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Macfarlane Burnet Institute for Medical Research...PATH; UNITAID; University of Melbourne; Menzies School of Health Research; Medicines... and other collaboratorsRecruitingVivax Malaria | G6PD DeficiencyPapua New Guinea
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Children's Mercy Hospital Kansas CityEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedSickle Cell AnemiaUnited States
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Universal Skincare InstituteLavish BeautyCompletedWrinkle | Collagen Degeneration | Elastic SkinUnited States
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Emory UniversityCompletedSickle Cell Disease | Bone Marrow TransplantationUnited States
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State University of New York at BuffaloSuspendedCognitive Impairment | Cardiovascular Abnormalities | Spinal Cord Injuries | Cerebrovascular Disease; SequelaeUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia B | HaemostasisUnited States
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University of Alabama at BirminghamMedtronic; The Children's Tumor FoundationTerminatedNF1 | Congenital Pseudarthrosis of TibiaUnited States, Australia
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SanofiTerminatedCongenital Cystic Kidney DiseaseGermany, Spain, United States, Australia, Belgium, Japan, Korea, Republic of, Netherlands
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Columbia UniversityTerminatedEpidermolysis BullosaUnited States
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Abbott Medical DevicesCompleted
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI)CompletedThalassemiaUnited States, Canada
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Neurocrine BiosciencesActive, not recruitingCongenital Adrenal HyperplasiaUnited States, United Kingdom, France, Greece, Italy, Spain, Belgium, Canada, Germany, Poland
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International Spine Study Group FoundationNuVasiveRecruitingScoliosis | Kyphosis | Adult Spinal Deformity | Sagittal ImbalanceUnited States
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New York Medical CollegeWashington University School of Medicine; University of California, Los Angeles and other collaboratorsActive, not recruitingSickle Cell DiseaseUnited States
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Children's Hospital Medical Center, CincinnatiMemorial Sloan Kettering Cancer Center; Fred Hutchinson Cancer CenterRecruitingFanconi Anemia | Myelodysplastic Syndrome (MDS) | Acute Myelogenous Leukemia (AML) | Severe Marrow FailureUnited States
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Spruce BiosciencesActive, not recruitingCongenital Adrenal HyperplasiaUnited States, Australia, Brazil, Estonia, Germany, Korea, Republic of, Latvia, Lithuania, Poland, Romania, Spain, Sweden, Turkey, Canada, Italy, United Kingdom
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Verinata Health, Inc.CompletedPregnancy | Down Syndrome | Edwards Syndrome | Patau Syndrome | Turners SyndromeUnited States
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Phoenicia BioScienceNational Heart, Lung, and Blood Institute (NHLBI)RecruitingSickle Cell Disease | Beta Thalassemia IntermediaUnited States, Canada
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Roswell Park Cancer InstituteCompletedLymphoma | Myelodysplastic Syndromes | Leukemia | Chronic Myeloproliferative Disorders | Fanconi Anemia | Multiple Myeloma and Plasma Cell Neoplasm | Myelodysplastic/Myeloproliferative Diseases | Aplastic AnemiaUnited States
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Montefiore Medical CenterTerminatedAnemia, Sickle Cell | Nocturnal EnuresisUnited States
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RWTH Aachen UniversityAdvanced BionicsCompletedDeafness, Bilateral | Deafness Unilateral | Deafness Congenital | Deafness, AcquiredGermany
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Boston Children's HospitalChildren's Hospital Colorado; Cedars-Sinai Medical Center; Hospital for Special... and other collaboratorsRecruitingAdolescent Idiopathic Scoliosis | Idiopathic Scoliosis | Spondylolisthesis | Spine Deformity | Neuromuscular Scoliosis | Congenital ScoliosisUnited States
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Life Molecular Imaging SACompletedDown Syndrome | Amyloid Beta-proteinUnited States