- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Congenital Myotonic Dystrophy in Brazil
Total 194 results
-
ProQR TherapeuticsActive, not recruitingEye Diseases | Neurologic Manifestations | Eye Diseases, Hereditary | Sensation Disorders | Vision Disorders | Blindness | Leber Congenital Amaurosis | Leber Congenital Amaurosis 10 | Retinal Disease | Eye Disorders CongenitalUnited States, Belgium, Brazil, Canada, France, Germany, Italy, Netherlands, United Kingdom
-
Maria I. NewNational Center for Research Resources (NCRR); Office of Rare Diseases (ORD)Completed21-hydroxylase DeficiencyUnited States, Brazil
-
Hospital Sirio-LibanesCompletedCraniofacial MicrosomiaBrazil
-
NICHD Global Network for Women's and Children's...National Cancer Institute (NCI); University of Iowa; National Institute of Dental... and other collaboratorsCompleted
-
Millendo Therapeutics US, Inc.TerminatedCongenital Adrenal HyperplasiaSpain, Israel, France, Brazil, Czechia
-
Federal University of São PauloUnknownDepressive Disorder | Obesity | Obsessive-Compulsive Disorder | Prader-Willi SyndromeBrazil
-
Pontifícia Universidade Católica de Minas GeraisUnknownCleft Lip and Palate | Class III Malocclusion | Palatal Expansion Technique | Skeletal MalocclusionBrazil
-
PATHFundação de Medicina Tropical Dr. Heitor Vieira DouradoCompleted
-
PTC TherapeuticsTerminatedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Germany, Brazil, Bulgaria, Chile, Czechia, Poland, Sweden, Switzerland, Turkey
-
Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Haemophilia A | Haemophilia B | Relatives to/Carers of PatientsBrazil
-
PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Brazil, Chile, Czechia, Sweden, Switzerland, Turkey, Germany, Poland
-
University Hospitals Cleveland Medical CenterAlana USA FoundationCompletedIntellectual Disability | Down SyndromeUnited States, Brazil
-
Office of Rare Diseases (ORD)UnknownAdrenal Hyperplasia, CongenitalUnited States, Brazil, France
-
University of Sao PauloFundação de Amparo à Pesquisa do Estado de São PauloCompleted
-
SanofiBristol-Myers SquibbCompletedHeart Defects, CongenitalFrance, Canada, Brazil, Poland, Russian Federation, Germany, Italy, Netherlands, Portugal, Spain, Sweden, India, Malaysia, Singapore, Taiwan, Belgium, Mexico, Argentina, Denmark, Egypt, Finland, Hungary, Israel, Norway, Korea, Republic of, Hong Kong and more
-
University of FloridaUniversity of Sao PauloCompleted
-
Oswaldo Cruz FoundationConselho Nacional de Desenvolvimento Científico e Tecnológico; Rio de Janeiro...UnknownMicrocephaly | Child Development | ZIKA VIRUS INFECTIONBrazil
-
Fundação Educacional Serra dos ÓrgãosUnknownHyperandrogenism | Menstruation Disturbances | Amenorrhea | DysmenorrheaBrazil
-
Fundação de Medicina Tropical Dr. Heitor Vieira...Oswaldo Cruz Foundation; Conselho Nacional de Desenvolvimento Científico e...Active, not recruitingVivax Malaria | G6PD DeficiencyBrazil
-
InCor Heart InstituteNovartisCompletedTuberous Sclerosis | Angiomyolipoma | LymphangioleiomyomatosisBrazil
-
Hospital de Clinicas de Porto AlegreUnknown
-
Federal University of São PauloCompletedCarpal Tunnel Syndrome | Compression Neuropathy, Carpal Tunnel | Median Neuropathy, Carpal TunnelBrazil
-
Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); St. Jude Children's Research... and other collaboratorsTerminatedSickle Cell AnemiaUnited States, Brazil, Jamaica
-
Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...CompletedPreviously Treated Myelodysplastic Syndrome | Fanconi Anemia | de Novo Myelodysplastic Syndrome | Acute Myeloid Leukemia in RemissionUnited States, Brazil
-
Hospital de Clinicas de Porto AlegreUnknownObesity | Polycystic Ovary Syndrome | HyperandrogenismBrazil
-
KU LeuvenCompletedCongenital Heart DiseaseBotswana, United States, Korea, Republic of, Belgium, Sweden, France, Switzerland, Denmark, Pakistan, Norway, Taiwan, Malta, Brazil, Bulgaria, India, Austria, Argentina, Australia, Cameroon, Canada, Chile, Colombia, Ethiopia, Greece, Italy and more
-
Fundação de Medicina Tropical Dr. Heitor Vieira...Ministry of Health, Brazil; Medicines for Malaria Venture; Centro de Pesquisa... and other collaboratorsActive, not recruitingMalaria, Vivax | G6PD DeficiencyBrazil
-
Columbia UniversityInternational Agency for Research on CancerRecruitingAcute Lymphoblastic Leukemia | Nutrition Aspect of Cancer | Genetic Predisposition | MicrotiaUnited States, Guatemala, Honduras, India, Brazil, Tanzania
-
AO Foundation, AO SpineCompletedSpinal DeformityUnited States, Turkey, Hong Kong, United Kingdom, China, Australia, Netherlands, Canada, Japan, Brazil, India, Israel, Pakistan, Spain
-
Crinetics Pharmaceuticals Inc.RecruitingCongenital Adrenal Hyperplasia | Classic Congenital Adrenal HyperplasiaBrazil, India, United States, Argentina, Italy, United Kingdom
-
WestatNational Institute of Allergy and Infectious Diseases (NIAID); Eunice Kennedy... and other collaboratorsCompletedEye Abnormalities | Hearing Loss | Zika | Neurodevelopmental Abnormality | Growth DelayBrazil, Colombia, Peru, Puerto Rico
-
IpsenCompletedCervical DystoniaKorea, Republic of, Thailand, Belgium, Israel, Taiwan, Germany, Hungary, United States, Singapore, Slovenia, United Kingdom, Australia, Malaysia, Serbia, Estonia, Turkey, Italy, Poland, China, Sweden, Portugal, Algeria, Austria, Brazil, Czechi... and more
-
Jaeb Center for Health ResearchFoundation Fighting BlindnessRecruitingRetinitis Pigmentosa | Inherited Retinal DegenerationUnited States, United Kingdom, France, Finland, Israel, Netherlands, Switzerland, Australia, Canada, Brazil, Mexico
-
Aesculap AGActive, not recruitingRheumatoid Arthritis | Hip Dysplasia | Fractures, Hip | Necrosis, Femur Head | Coxarthrosis; Primary | Coxarthrosis; Post-TraumaticGermany
-
Merck Sharp & Dohme LLCActive, not recruitingPIK3CA-Related Overgrowth Spectrum (PROS)/Proteus Syndrome (PS)United States, Australia, Brazil, Italy, United Kingdom
-
IgenomixRecruitingInfertility | Aneuploidy | Chromosome AbnormalityFrance, Argentina, Spain, United States, Brazil, Italy
-
Mirum Pharmaceuticals, Inc.Active, not recruitingCholestatic Liver Disease | Alagille Syndrome | Progressive Familial Intrahepatic CholestasisUnited States, United Kingdom, France, Belgium, Poland, Brazil, Mexico
-
TakedaCompletedDravet Syndrome (DS)China, Canada, France, Hungary, Poland, United States, Spain, Greece, Australia, Brazil, Serbia, Germany, Italy, Japan, Latvia, Netherlands, Ukraine, Russian Federation
-
Kevin MunroGöteborg University; University of Copenhagen; National Institute of Dental and... and other collaboratorsCompletedCleft PalateNorway, United Kingdom, Sweden, Brazil, Denmark
-
WestatEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedSickle Cell Disease | Thalassemia | Pediatric CancerUnited States, Brazil
-
IgenomixCompletedInfertility | Aneuploidy | Chromosome AbnormalityMexico, Turkey, United States, Argentina, Spain, Brazil, Italy, Peru
-
NuVasiveCompletedSpinal Deformity | Spinal Trauma | Vertebra; DegenerationUnited States, Brazil
-
SangartWithdrawnSickle Cell Disease | Anemia, Sickle Cell | Sickle Cell Anemia | Hemoglobin SC Disease | Sickle Cell Disorders | Sickle Cell Hemoglobin C DiseaseFrance, United Kingdom, Netherlands, Turkey, Bahrain, Belgium, Brazil, Lebanon, Qatar
-
BioMarin PharmaceuticalRecruitingHypochondroplasiaUnited States, Spain, Canada, France, Japan, Australia, Italy, Argentina, Brazil, Germany, United Kingdom
-
Hospital de Clinicas de Porto AlegreUnknownTracheobronchomalaciaBrazil
-
Agios Pharmaceuticals, Inc.Active, not recruitingPyruvate Kinase DeficiencyUnited States, Spain, Japan, Canada, United Kingdom, Korea, Republic of, Ireland, Thailand, Italy, Turkey, Denmark, Brazil, France, Germany, Netherlands, Switzerland
-
Agios Pharmaceuticals, Inc.CompletedAnemia, Hemolytic | Pyruvate Kinase DeficiencyUnited States, Spain, Switzerland, Turkey, Germany, France, United Kingdom, Japan, Netherlands, Brazil, Canada, Czechia, Denmark, Italy, Korea, Republic of, Thailand
-
Hoffmann-La RocheRecruitingSickle Cell DiseaseUnited States, Brazil, Italy, Spain, Kenya, Netherlands, United Kingdom, France, South Africa
-
Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedMetabolic Diseases | Congenital Abnormalities | Infant, Newborn, Diseases | Genetic Diseases, Inborn | Dyslipidemias | Metabolism, Inborn Errors | Lipid Metabolism Disorders | Hypercholesterolemia | Hyperlipidemias | Hyperlipoproteinemias | Lipid Metabolism, Inborn Errors | Hyperlipoproteinemia Type II | Metabolic... and other conditionsUnited States, Taiwan, Brazil, Canada, South Africa, United Kingdom, Singapore
-
Gladwin, Mark, MDNational Heart, Lung, and Blood Institute (NHLBI)RecruitingSickle Cell DiseaseUnited States, France, Brazil