- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Congenital Myotonic Dystrophy
Total 10148 results
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ReveraGen BioPharma, Inc.University of Pittsburgh; Newcastle University; European Union; Cooperative International...CompletedDuchenne Muscular DystrophyUnited States, Belgium, Canada, United Kingdom, Spain, Netherlands, Sweden, Czechia, Australia, Greece, Israel
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Haukeland University HospitalExtrastiftelsenCompleted
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Phrixus Pharmaceuticals, Inc.Charley's FundTerminated
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Acceleron Pharma Inc. (a wholly owned subsidiary...Terminated
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Catabasis PharmaceuticalsCompletedMuscular Dystrophy, DuchenneUnited States
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Newcastle... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Germany, Italy
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ItalfarmacoSyneos HealthCompletedDuchenne Muscular DystrophyUnited States, Italy, Spain, Canada, Belgium, France, Germany, Israel, Netherlands, Serbia, United Kingdom
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Haukeland University HospitalOslo University Hospital; Norwegian School of Sport SciencesCompletedDuchenne Muscular DystrophyNorway
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NS Pharma, Inc.Cooperative International Neuromuscular Research Group; Nippon Shinyaku Co.... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada
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Santhera PharmaceuticalsTerminatedDuchenne Muscular DystrophyUnited States, Belgium, United Kingdom, Austria, France, Germany, Italy, Spain, Switzerland
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Charite University, Berlin, GermanyCompletedDuchenne Muscular DystrophyGermany
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Taiho Pharmaceutical Co., Ltd.Completed
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ReveraGen BioPharma, Inc.University of Pittsburgh; Cooperative International Neuromuscular Research...CompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Sweden, Australia, Israel
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Rare Disease Research, LLCSarepta Therapeutics, Inc.TerminatedDuchenne Muscular DystrophyUnited States
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Marmara UniversityUnknownDuchenne Muscular Dystrophy
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Children's Hospital Medical Center, CincinnatiIpsen; Charley's FundCompletedDuchenne Muscular DystrophyUnited States
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PfizerTerminatedDuchenne Muscular DystrophyUnited States, Australia, Canada, United Kingdom, Japan, Bulgaria, Italy, Poland
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Catabasis PharmaceuticalsTerminatedDuchenne Muscular DystrophyUnited States, Canada, Australia, United Kingdom, Germany, Sweden
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Processa PharmaceuticalsTerminatedDuchenne Muscular DystrophyUnited States
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Stem Cells ArabiaUnknownDuchenne Muscular DystrophyJordan
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National Center of Neurology and Psychiatry, JapanNippon Shinyaku Co., Ltd.Completed
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University Hospital, MontpellierHospital Clinical Research Project 2010; Association Amis FSH France; FSH Dutch...CompletedFacioscapulohumeral Muscular DystrophyFrance
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Cedars-Sinai Medical CenterCompletedBecker Muscular DystrophyUnited States
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Cedars-Sinai Medical CenterTerminatedMuscular DystrophyUnited States
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Cedars-Sinai Medical CenterParent Project Muscular DystrophyCompleted
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Valeria Sanchez-HuertaEmmecellUnknownCorneal Edema | Fuchs' Endothelial Dystrophy | Fuchs Dystrophy | Corneal Endothelial Dystrophy | Pseudophakic Bullous Keratopathy | Corneal Transplant FailureMexico
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Eli Lilly and CompanyTerminatedMuscular Dystrophy, DuchenneGermany, United States, Spain, Belgium, France, Italy, Taiwan, Netherlands, Turkey, Korea, Republic of, Argentina, Canada, Japan, Puerto Rico, Russian Federation, United Kingdom
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Wave Life Sciences Ltd.CompletedDuchenne Muscular DystrophyBelgium, United Kingdom, France, United States, Italy, Canada, Netherlands
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Ann & Robert H Lurie Children's Hospital of ChicagoCompletedDuchenne Muscular DystrophyUnited States
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Washington University School of MedicineUniversity of California, Davis; Nationwide Children's Hospital; University of... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States
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BioMarin PharmaceuticalCompletedDuchenne Muscular DystrophyBelgium, Netherlands, Italy, Sweden
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Children's Hospital of Eastern OntarioCompletedDuchenne Muscular DystrophyCanada
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Cooperative International Neuromuscular Research...UnknownBecker Muscular DystrophyUnited States, Canada, Italy, United Kingdom
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Hacettepe UniversityCompletedDuchenne Muscular Dystrophy | BalanceTurkey
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National Human Genome Research Institute (NHGRI)Completed
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Kevin FlaniganWithdrawnDuchenne Muscular DystrophyUnited States
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyNetherlands, Belgium, Italy, Sweden
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BioMarin PharmaceuticalNo longer availableDuchenne Muscular DystrophyUnited States, Germany, United Kingdom, Japan, Netherlands, France, Spain, Korea, Republic of, Italy, Belgium, Taiwan, Argentina, Australia, Bulgaria, Czechia, Israel, Norway, Poland, Russian Federation, Turkey
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Assiut UniversityUnknownDuchenne Muscular Dystrophy
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyUnited Kingdom, Italy, Belgium, Netherlands, France
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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University of Sao PauloCompletedDuchenne Muscular Dystrophy
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University of Sao PauloCompletedDuchenne Muscular DystrophyBrazil
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GenethonInstitute of MyologyUnknownDuchenne Muscular DystrophyUnited Kingdom, France
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Sarepta Therapeutics, Inc.British Medical Research CouncilCompletedDuchenne Muscular DystrophyUnited Kingdom
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Kobe UniversityNobelpharma; Japan Medical AssociationUnknownMuscular Dystrophy, DuchenneJapan
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Cooperative International Neuromuscular Research...UnknownDuchenne Muscular DystrophyUnited States, Canada
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Alan Neuromedical Technologies, LLCCompleted
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Acibadem UniversityUnknownDuchenne Muscular DystrophyTurkey