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Clinical Trials on Congenital Thrombocytopenia in Poland
Total 398 results
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Mirum Pharmaceuticals, Inc.CompletedAlagille SyndromeFrance, Belgium, Poland, Australia, Spain, United Kingdom
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Oregon Health and Science UniversityCompletedDown SyndromeUnited States
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Erasmus Medical CenterNot yet recruitingDisorder of Sex Development, 46,XYNetherlands
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Oregon Health and Science UniversityCompleted
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Women and Infants Hospital of Rhode IslandNatera, Inc.CompletedTrisomy 21 | Trisomy 18 | Trisomy 13 | Monosomy XUnited States
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Alexion Pharmaceuticals, Inc.RecruitingThrombotic MicroangiopathyUnited States, Italy, Spain, Korea, Republic of, United Kingdom, Belgium, Netherlands, Germany, Japan, Greece, Brazil, Israel, France, China, Sweden, Australia, Canada, Poland
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SI-BONE, Inc.RecruitingSpinal Fusion | Deformity of SpineUnited States
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Shay BessMedtronic; DePuy SpineCompletedSpinal DeformityUnited States
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The George Washington University Biostatistics...Eunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedCongenital Cytomegalovirus Infection | Maternal Cytomegalovirus InfectionUnited States
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Prothya BiosolutionsTerminated
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PTC TherapeuticsCompletedAniridiaUnited States, Canada
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Applied Genetic Technologies CorpOregon Health and Science University; University of Massachusetts, WorcesterCompletedLeber Congenital AmaurosisUnited States
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dr. Laura C. G. de Graaff-HerderRecruitingTurner Syndrome | Klinefelter SyndromeNetherlands
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Dr. Marjon H. Cnossen MD PhDAcademisch Medisch Centrum - Universiteit van Amsterdam (AMC-UvA)RecruitingSickle Cell Disease | Brain Development AbnormalityNetherlands
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KU LeuvenCompletedCongenital Heart DiseaseBotswana, United States, Korea, Republic of, Belgium, Sweden, France, Switzerland, Denmark, Pakistan, Norway, Taiwan, Malta, Brazil, Bulgaria, India, Austria, Argentina, Australia, Cameroon, Canada, Chile, Colombia, Ethiopia, Greece, Italy and more
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Atsena Therapeutics Inc.Active, not recruitingLeber Congenital Amaurosis | LCA | LCA1United States
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Erasmus Medical CenterDutch Heart FoundationActive, not recruitingCongenital Aortic StenosisNetherlands
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Pierre Fabre DermatologyCompletedInfantile HemangiomaSpain, France, Poland
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Nationwide Children's HospitalNational Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health... and other collaboratorsNot yet recruitingSickle Cell DiseaseUnited States
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OHSU Knight Cancer InstituteNational Cancer Institute (NCI)TerminatedLymphoma | Thrombocytopenia | Brain and Central Nervous System Tumors | Drug/Agent Toxicity by Tissue/OrganUnited States
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CelgeneCompletedMyelodysplastic SyndromeUnited States, Australia, Canada, Czechia, France, Germany, Italy, Korea, Republic of, Mexico, Poland, Sweden, United Kingdom, Belgium, Brazil, Denmark, Finland, Greece, Israel, Netherlands, Norway, Portugal, Spain, Turkey
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AlbireoActive, not recruitingAlagille SyndromeUnited Kingdom, United States, France, Germany, Netherlands, Italy, Belgium, Malaysia, Poland, Turkey
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Oregon Health and Science UniversityNational Heart, Lung, and Blood Institute (NHLBI)TerminatedSmith-Lemli-Opitz SyndromeUnited States
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Gilead SciencesCompletedLong QT SyndromeUnited States, Romania, Moldova, Republic of
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dr. Laura C. G. de Graaff-HerderNot yet recruitingCongenital Adrenal Hyperplasia | Hypogonadotropic Hypogonadism | Growth Hormone Deficiency | Turner Syndrome | Addison's Disease | Klinefelter Syndrome | Combined Pituitary Hormone Deficiency | Androgen Insensitivity Syndrome | Thyroid DysgenesisSpain, United Kingdom, Belgium, Netherlands
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Erasmus Medical CenterFoundation for Prader-Willi Research; Prader-Willi FondsNot yet recruiting
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Mirum Pharmaceuticals, Inc.RecruitingAlagille SyndromeUnited States
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Holterman, Ai-Xuan, M.D.T Rose Clinical, Inc.; Big Leap Research; Prometheus USARecruitingBiliary AtresiaUnited States, Vietnam, Pakistan
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PfizerCompletedHodgkin Disease | Thrombocytopenia | Non-Hodgkin LymphomaUnited States, Russian Federation, Singapore, Australia, France, Hong Kong, Greece, Poland
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Intercept PharmaceuticalsTerminatedBiliary AtresiaIsrael, United Kingdom, Poland, Belgium, France, Germany, Italy, Netherlands, Spain
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Academisch Medisch Centrum - Universiteit van Amsterdam...RecruitingInflammatory Bowel Diseases | Ostomy | Anorectal Malformations | Spina BifidaNetherlands
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Otto Bock Healthcare Products GmbHHanger Clinic: Prosthetics & OrthoticsActive, not recruitingLower Limb Amputation Above Knee (Injury) | Lower Limb Amputation Knee | Congenital Amputation of Lower LimbUnited States
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QLT Inc.CompletedLeber Congenital Amaurosis (LCA) | Retinitis Pigmentosa (RP)United States, Canada, Denmark, Germany, Netherlands, Switzerland, United Kingdom
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Academisch Medisch Centrum - Universiteit van Amsterdam...RecruitingSickle Cell Disease | Sickle Cell SC Disease | Sickle Cell-SS Disease | Sickle Cell RetinopathyNetherlands
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Edimer PharmaceuticalsCompletedHypohidrotic Ectodermal Dysplasia | X-Linked Hypohidrotic Ectodermal DysplasiaUnited States
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Children's Hospital Medical Center, CincinnatiRecruitingHypoplastic Left Heart Syndrome (HLHS)United States, United Kingdom, Canada
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OHSU Knight Cancer InstituteNational Heart, Lung, and Blood Institute (NHLBI)CompletedChronic Myeloproliferative Disorders | Fanconi Anemia | Multiple Myeloma and Plasma Cell Neoplasm | Myelodysplastic/Myeloproliferative NeoplasmsUnited States
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NovaSignal Corp.CompletedTransient Ischemic Attack | Patent Foramen Ovale | Embolic Stroke of Undetermined Source | Right-To-Left Atrial ShuntUnited States
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Mirum Pharmaceuticals, Inc.Active, not recruitingCholestatic Liver Disease | Alagille Syndrome | Progressive Familial Intrahepatic CholestasisUnited States, United Kingdom, France, Belgium, Poland, Brazil, Mexico
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National Heart, Lung, and Blood Institute (NHLBI)National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)CompletedMarfan Syndrome | Turner Syndrome | Ehlers-Danlos Syndrome | Loeys-Dietz Syndrome | Shprintzen-Goldberg Syndrome | FBN1, TGFBR1, TGFBR2, ACTA2 or MYH11 Genetic Mutation | Bicuspid Aortic Valve Without Known Family History | Bicuspid Aortic Valve With Family History | Bicuspid Aortic Valve With Coarctation and other conditionsUnited States
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Spruce BiosciencesActive, not recruitingCongenital Adrenal HyperplasiaUnited States, Australia, Brazil, Estonia, Germany, Korea, Republic of, Latvia, Lithuania, Poland, Romania, Spain, Sweden, Turkey, Canada, Italy, United Kingdom
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NICHD Neonatal Research NetworkNational Center for Research Resources (NCRR); Medical Research Council of...CompletedDuctus Arteriosus, Patent | Infant, Very Low Birth Weight | Infant, PrematureUnited States
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Oregon Health and Science UniversityCompletedMicrovascular and Cardiac Dysfunction in Paroxysmal Nocturnal Hemoglobinuria and Sickle Cell DiseaseSickle Cell Disease | Paroxysmal Nocturnal Hemoglobinuria | Rheologic DiseaseUnited States
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Erasmus Medical CenterRecruitingAutosomal Dominant Polycystic KidneyNetherlands
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Medtronic CardiovascularActive, not recruitingBicuspid Aortic ValveUnited States
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Mirum Pharmaceuticals, Inc.CompletedBiliary AtresiaUnited States, United Kingdom, China, Taiwan, Germany, Poland, Singapore, Vietnam
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Oregon Health and Science UniversityActive, not recruitingObstructive Sleep Apnea | Down SyndromeUnited States
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National University of Natural MedicineHealthy Living CommunityCompletedEhlers-Danlos Syndrome | Hypermobile EDS (hEDS) | Hypermobility Syndrome | EDSUnited States
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Radboud University Medical CenterRecruitingOvarian Diseases | Sex Chromosome Disorders | Infertility, Female | Turner Syndrome | Gonadal Dysgenesis | Premature Ovarian Failure | Premature MenopauseNetherlands, Germany, Poland, Sweden, Denmark
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ActelionCanadian Heart Research CentreCompleted