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Clinical Trials on Congenital in Canada
Total 578 results
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ProQR TherapeuticsTerminatedRetinitis Pigmentosa | Usher Syndrome Type 2United States, Canada, France
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Ultragenyx Pharmaceutical IncNot yet recruitingAngelman SyndromeUnited States, Australia, Canada, Germany, United Kingdom, Israel, France, Spain
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedMetabolic Diseases | Congenital Abnormalities | Infant, Newborn, Diseases | Genetic Diseases, Inborn | Dyslipidemias | Metabolism, Inborn Errors | Lipid Metabolism Disorders | Hypercholesterolemia | Hyperlipidemias | Hyperlipoproteinemias | Lipid Metabolism, Inborn Errors | Hyperlipoproteinemia Type II | Metabolic... and other conditionsUnited States, Taiwan, Brazil, Canada, South Africa, United Kingdom, Singapore
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AstraZenecaCompletedInvestigation of Platelet Aggregation in Paediatric Patients With Sickle Cell DiseaseUnited States, Canada, United Kingdom, South Africa, Lebanon, Kenya
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHematologic Diseases | Anemia, Sickle Cell | Beta-Thalassemia | Hematopoietic Stem Cell TransplantationUnited States, Canada
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University of California, Los AngelesUniversité de MontréalWithdrawnStroke | Epilepsy | Tuberous Sclerosis | Sturge-Weber Syndrome | Focal Cortical Dysplasia | Hemimegalencephaly | Polymicrogyria | Rasmussen Encephalitis | Gliosis | Tumor, BrainUnited States, Canada
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AMO Pharma LimitedCompletedCongenital Myotonic DystrophyUnited States, Canada, New Zealand, Australia, United Kingdom
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BayerCompletedHemophilia A, CongenitalSlovenia, Italy, Germany, France, United States, Belgium, Canada, Colombia, Greece, Luxembourg, Netherlands, Spain, Taiwan
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Natera, Inc.Eunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsTerminatedAneuploidy | Trisomy 21 | Trisomy 18 | Trisomy 13United States, Ireland, Canada, Italy, Korea, Republic of, Spain
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Hoffmann-La RocheCompletedDown SyndromeUnited States, Spain, Canada, New Zealand, Argentina, Mexico, Singapore
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AMO Pharma LimitedRecruitingCongenital Myotonic DystrophyUnited States, Canada, Australia, New Zealand
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Grifols Therapeutics LLCGrifols Biologicals, LLCTerminatedHemophilia A, CongenitalUnited States, Spain, Italy, India, Canada, Russian Federation
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Modus Therapeutics ABErgomedCompletedSickle-Cell DiseaseNetherlands, Oman, Jamaica, Lebanon, Bahrain, Saudi Arabia, Turkey
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AlbireoRecruitingBiliary AtresiaNetherlands, United States, Spain, Italy, Taiwan, Korea, Republic of, France, Germany, United Kingdom, Canada, Belgium, China, Australia, Poland, Turkey, Malaysia, New Zealand, Hungary, Israel
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Regeneron PharmaceuticalsRecruitingCongenital Hearing Loss Secondary to Biallelic Mutations of the Otoferlin Gene (OTOF)Spain, United Kingdom, United States
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GlycoMimetics IncorporatedCompletedSickle Cell Disease | Vaso-occlusive Crisis | Pain CrisisUnited States, Canada
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Anagnostou, Evdokia, M.D.The Hospital for Sick Children; Canadian Institutes of Health Research (CIHR); Alberta Health services and other collaboratorsNot yet recruitingAnxiety Disorders | Generalized Anxiety Disorder | Anxiety | Tuberous Sclerosis | ADHD | Neurodevelopmental Disorders | Autism Spectrum Disorder | Fragile X Syndrome | Social Anxiety | Social Anxiety Disorder | Agoraphobia | Tourette Syndrome | Tic Disorders | Autism | ADHD Predominantly Inattentive Type | ADHD - Combined... and other conditionsCanada
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Ultragenyx Pharmaceutical IncActive, not recruitingAngelman SyndromeUnited States, United Kingdom, Canada, Australia, France, Germany, Spain, Israel
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McMaster UniversityHarvard Medical School (HMS and HSDM); The Hospital for Sick Children; Canadian... and other collaboratorsTerminatedEpilepsy | Cerebral Palsy | Autism Spectrum Disorder | Spina Bifida | Fetal Alcohol Spectrum DisordersCanada
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HemaQuest Pharmaceuticals Inc.CompletedSickle Cell Disease | Sickle Cell Anemia | Sickle Cell Disorders | Hemoglobin S Disease | Sickling Disorder Due to Hemoglobin SUnited States, Lebanon, Canada, Egypt, Jamaica
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Novartis PharmaceuticalsCompletedSickle Cell DiseaseUnited States, Italy, United Kingdom, France, Canada
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Oregon Health and Science UniversityNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)RecruitingPancreatitis | Pancreatitis, Acute | Pancreas Divisum | Pancreatitis Idiopathic | Pancreas InflamedUnited States, Canada, Netherlands
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Hoffmann-La RocheCompletedDown SyndromeUnited States, Italy, Argentina, France, Spain, Mexico, Canada, New Zealand, Singapore, United Kingdom
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PfizerActive, not recruitingSickle Cell DiseaseUnited States, Lebanon, United Kingdom, Oman, Turkey, Canada, Egypt, Kenya, France, Italy, Netherlands
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PfizerCompletedSickle Cell DiseaseUnited States, Italy, France, United Kingdom, Netherlands, Turkey, Egypt, Canada, Jamaica, Kenya, Lebanon, Oman
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Pierre Fabre DermatologyCompletedInfantile HemangiomaGermany, United States, France, Spain, Peru, Australia, Lithuania, Italy, Canada, Czech Republic, Hungary, Mexico, New Zealand, Poland, Romania, Russian Federation
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Eli Lilly and CompanyDaiichi Sankyo, Inc.TerminatedSickle Cell DiseaseUnited Arab Emirates, Italy, United States, Egypt, United Kingdom, Belgium, Turkey, Brazil, Canada, Ghana, Kenya, Lebanon, Oman, Saudi Arabia
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HemaQuest Pharmaceuticals Inc.TerminatedSickle Cell Disease | Sickle Cell Anemia | Sickle Cell Disorders | Hemoglobin S Disease | Sickling Disorder Due to Hemoglobin SUnited States, Lebanon, Egypt, Canada, Jamaica
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Sequenom, Inc.CompletedDown Syndrome | Fetal AneuploidyUnited States, Canada
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SangartWithdrawnSickle Cell Disease | Anemia, Sickle Cell | Sickle Cell Anemia | Hemoglobin SC Disease | Sickle Cell Disorders | Sickle Cell Hemoglobin C DiseaseFrance, United Kingdom, Netherlands, Turkey, Bahrain, Belgium, Brazil, Lebanon, Qatar
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University Hospital, GenevaCompletedAfibrinogenemia, CongenitalFrance, Turkey, Switzerland, Netherlands, Spain, India, Poland, Canada, United States, Algeria, Egypt, Germany, Italy, Japan, Kuwait, Lebanon, Morocco, Pakistan, Serbia, Slovakia, Tunisia
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ApoPharmaTerminatedIron Overload | Sickle Cell Disease | Other AnemiasUnited States, Turkey, United Kingdom, Egypt, Saudi Arabia, Brazil, Canada, Tunisia
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GlycoMimetics IncorporatedCompletedAnemia, Sickle CellUnited States, Canada
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Centre hospitalier de l'Université de Montréal...Centre Hospitalier Régional et Universitaire de BrestRecruitingArteriovenous Malformations | Unruptured Brain Arteriovenous Malformation | Ruptured Brain Arteriovenous Malformation | AVM | BAVMFrance, United States, Canada, Brazil, Chile, Colombia
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Calliditas Therapeutics ABRecruitingAlport SyndromeUnited Kingdom, Spain, Czechia
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CephalonCompletedPain | Cancer | Sickle Cell Anemia | Severe BurnsUnited States, Canada, Puerto Rico
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Prof. Valérie Mc LinEuropean Society of Pediatric Gastroenterology, Hepatology and Nutrition; European... and other collaboratorsEnrolling by invitationCongenital Porto-Systemic Shunt (CPSS)Spain, United Kingdom, Canada, United States, Netherlands, France, Israel, Germany, Australia, Turkey, Switzerland, Japan, Belgium, Greece, Hungary, India, Italy
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GRIN Therapeutics, Inc.RecruitingTuberous Sclerosis Complex | Focal Cortical DysplasiaSpain, United Kingdom, Australia, Belgium, Canada, Italy, Poland
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Novo Nordisk A/SRecruitingSickle Cell DiseaseSpain, United States, United Kingdom, Canada, Italy, India, Turkey, Greece, South Africa, France, Lebanon, Oman
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Novartis PharmaceuticalsCompletedAnemia | HemosiderosisUnited States, Germany, Belgium, United Kingdom, Italy, Canada, France
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Women and Infants Hospital of Rhode IslandSequenom, Inc.CompletedDown Syndrome | Trisomy 21United States, Canada, Israel, Hungary, Ireland, Argentina, Australia, Czech Republic, Italy, Spain
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ACADIA Pharmaceuticals Inc.RecruitingHyperphagia in Prader-Willi SyndromeUnited States, Canada, United Kingdom
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Novo Nordisk A/SCompletedObesity | Metabolism and Nutrition DisorderFrance, United States, Turkey, Italy, Australia, New Zealand, Canada, Netherlands
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Levo Therapeutics, Inc.CompletedPrader-Willi SyndromeUnited States, Canada, Australia
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Forma Therapeutics, Inc.Novo Nordisk A/SRecruitingSickle Cell DiseaseUnited States, Italy, Spain, United Kingdom, France, Lebanon, Germany, Oman, Canada, Greece
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Roche Sequencing SolutionsPerinatal Quality Foundation: Nuchal Translucency Quality ReviewCompletedTrisomy 21United States, Belgium, Netherlands, Sweden, Italy, Canada
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Genzyme, a Sanofi CompanyCompletedAlport Syndrome Patients With eGFR Between 45-90 ml/Min/1.73 m2France, Germany, Australia, United States, United Kingdom, Canada
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CelgeneAcceleron Pharma Inc. (a wholly owned subsidiary of Merck Sharp and Dohme...CompletedBeta-Thalassemia | Erythrocyte TransfusionUnited States, Israel, Australia, Turkey, Taiwan, Malaysia, United Kingdom, Canada, Thailand, France, Lebanon, Italy, Bulgaria, Greece, Tunisia
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GlycoMimetics IncorporatedTerminatedSickle Cell Disease | Sickle Cell Anemia | Vaso-occlusive Crisis | Pain Crisis | Sickle Cell DisordersUnited States, Canada
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With InhibitorsSlovakia, Spain, Argentina, Germany, Croatia, Italy, Canada, United Kingdom, Ireland, Sweden, France, United States, Czech Republic, Switzerland