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Clinical Trials on Congenital Myasthenia (CM)
Total 9253 results
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Myasthenia Gravis Rare Disease NetworkRecruitingMyasthenia Gravis | MuSK Myasthenia Gravis | MuSK MGUnited States
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Kyverna TherapeuticsNot yet recruitingGeneralized Myasthenia Gravis | Myasthenia Gravis
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UCB Biopharma SRLNot yet recruitingGeneralized Myasthenia Gravis
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Tang-Du HospitalRecruitingMyasthenia Gravis, GeneralizedChina
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Alexion Pharmaceuticals, Inc.RecruitingGeneralized Myasthenia Gravis | gMGSpain, Italy, United States, France, Switzerland, Serbia, Japan, Netherlands
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argenxRecruitingGeneralized Myasthenia GravisUnited States, Netherlands, Belgium, Poland, United Kingdom
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Regeneron PharmaceuticalsRecruitingGeneralized Myasthenia GravisUnited States, Japan, Spain, Taiwan, Germany, Italy, Canada, Turkey, Georgia, Belgium, India, Poland, Australia, Denmark, France, United Kingdom, Korea, Republic of, Serbia, Czechia, Brazil
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Tang-Du HospitalRecruitingMyasthenia Gravis, GeneralizedChina
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Huashan HospitalRecruitingMyasthenia Gravis, GeneralizedChina
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Alexion Pharmaceuticals, Inc.RecruitingGeneralized Myasthenia GravisUnited States
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Tang-Du HospitalRecruitingOcular Myasthenia GravisChina
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Cartesian TherapeuticsRecruitingMyasthenia Gravis, GeneralizedUnited States, Canada
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UCB Biopharma SRLCompletedGeneralized Myasthenia GravisUnited States, Canada, Georgia, Germany, Italy, Japan, Poland, Serbia, Spain, United Kingdom
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argenxActive, not recruitingGeneralized Myasthenia GravisGeorgia, United States, Austria, Belgium, Canada, France, Germany, Italy, Netherlands, Poland, Spain
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Momenta Pharmaceuticals, Inc.CompletedGeneralized Myasthenia GravisUnited States, Belgium, Canada, Germany, Italy, Poland, Spain, United Kingdom
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Tianjin Medical University General HospitalCompletedDetection Autoantibody of Myasthenia GravisChina
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Fredrik PiehlUnknownA Study Evaluating the Safety and Efficacy of Rituximab in Patients With Myasthenia Gravis (Rinomax)Generalized Myasthenia GravisSweden
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Michael BenatarUniversity of Miami; University of RochesterTerminatedOcular Myasthenia GravisUnited States, Canada
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University of VermontGenentech, Inc.Completed
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PfizerRecruitingATTR-CM (Transthyretin Amyloid Cardiomyopathy)Korea, Republic of
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Novo Nordisk A/SActive, not recruitingTransthyretin Amyloid Cardiomyopathy (ATTR CM)United States, Netherlands, Spain, Portugal, Canada, Czechia, France, Germany, Italy, Japan
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Mahidol UniversityPfizerNot yet recruiting
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University of AlbertaWithdrawnHypoplastic Left Heart Syndrome | Congenital Heart Defect | TGA - Transposition of Great Arteries | Congential Absence of Heart Structure | Congenital Malformation of Heart, Unspecified | Hypoplastic Right Heart Syndrome | Congential Malformations of Aortic Valve | Congential Malformations of Great...Canada
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Zhejiang UniversityGracell Biotechnology Shanghai Co., Ltd.RecruitingRefractory Generalized Myasthenia GravisChina
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University of Missouri-ColumbiaUniversity of Kansas Medical CenterRecruitingGeneralized Myasthenia GravisUnited States
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Fondazione Policlinico Universitario Agostino Gemelli...Recruiting
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Alexion Pharmaceuticals, Inc.RecruitingGeneralized Myasthenia GravisChina, United States, Spain, United Kingdom, Korea, Republic of, Germany, Italy, Japan, Brazil, France, Netherlands, Taiwan, Turkey, Israel, Poland, Austria, Denmark, Portugal, Canada, Serbia, Argentina, Switzerland
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Immunovant Sciences GmbHRecruitingGeneralized Myasthenia GravisUnited States, Poland, Romania, Italy, Georgia, Korea, Republic of, Canada, Japan, Hungary, Spain, Serbia, Germany
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First Affiliated Hospital, Sun Yat-Sen UniversityRecruitingRefractory Myasthenia Gravis | RituximabChina
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Alexion Pharmaceuticals, Inc.CompletedGeneralized Myasthenia GravisUnited States, Italy, France, Germany, Korea, Republic of, Netherlands, Austria, Spain, Japan, Czechia, Canada, Portugal, Switzerland, Israel, Denmark
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Alexion Pharmaceuticals, Inc.TerminatedGeneralized Myasthenia Gravis | Myasthenia GravisUnited States, Italy, Spain, Canada, Germany, Korea, Republic of, Serbia, Taiwan
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argenxActive, not recruitingGeneralized Myasthenia GravisUnited States, Belgium, Czechia, Georgia, Germany, Hungary, Italy, Japan, Netherlands, Poland, Russian Federation, Spain
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RemeGen Co., Ltd.Completed
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UCB Biopharma SRLCompletedGeneralized Myasthenia GravisUnited States, Belgium, Canada, Czechia, Denmark, France, Georgia, Germany, Hungary, Italy, Japan, Poland, Russian Federation, Serbia, Spain, Taiwan, United Kingdom
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Momenta Pharmaceuticals, Inc.TerminatedGeneralized Myasthenia GravisUnited States, Belgium, Canada, Germany, Italy, Poland, Spain, United Kingdom
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argenxCompletedGeneralized Myasthenia GravisSpain, United States, Belgium, Georgia, Germany, Hungary, Italy, Japan, Netherlands, Poland, Russian Federation
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Novartis PharmaceuticalsCompletedMyasthenia Gravis, GeneralizedTaiwan, Germany, Russian Federation, Denmark, Canada
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Alexion PharmaceuticalsCompletedRefractory Generalized Myasthenia GravisItaly, United Kingdom, Spain, Belgium, Turkey, Japan, United States, Netherlands, Korea, Republic of, Argentina, Hungary, Sweden, Denmark, Brazil, Czechia, Finland, Canada
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Benesis CorporationCompletedGeneralized Myasthenia GravisJapan
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Hoffmann-La RocheAspreva PharmaceuticalsCompletedMyasthenia Gravis GeneralisedFrance, Ukraine, Germany, United States, Italy, United Kingdom, Former Serbia and Montenegro
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Ionis Pharmaceuticals, Inc.AstraZenecaRecruitingTransthyretin-Mediated Amyloid Cardiomyopathy (ATTR CM)United States, Austria, Belgium, Canada, France, Germany, Israel, Italy, Portugal, Spain, Sweden, United Kingdom, Australia, Greece
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Ionis Pharmaceuticals, Inc.Active, not recruitingTransthyretin-Mediated Amyloid Cardiomyopathy (ATTR CM)United States, Australia, Spain, Canada, Germany, Japan, Italy, Israel, Argentina, France, Portugal, Austria, Brazil, Greece, United Kingdom, Czechia, Sweden, Belgium, Denmark, Poland, Puerto Rico
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University Health Network, TorontoGrifols Therapeutics LLCCompleted
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Novo Nordisk A/SRecruitingTransthyretin Amyloid Cardiomyopathy (ATTR CM)United States, Netherlands, Germany, Canada, Czechia, France, Italy, Portugal, Spain
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XiaoYong LiuRecruitingCytomegalovirus Infections | Ocular Myasthenia GravisChina
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Fred Hutchinson Cancer CenterActive, not recruitingMyasthenia Gravis | Neuromyelitis Optica | Autoimmune Disease | Chronic Inflammatory Demyelinating Polyneuropathy | Lambert Eaton Myasthenic Syndrome | Cerebellar Degeneration | Stiff Person Syndrome | Opsoclonus Myoclonus Syndrome | Neurologic Autoimmune Disease | Autologous Transplant Autoimmune | Multiple... and other conditionsUnited States
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RemeGen Co., Ltd.Not yet recruitingGeneralized Myasthenia Gravis
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UCB Biopharma SRLNot yet recruiting
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NMD Pharma A/SNot yet recruitingSafety and Efficacy of 3 Dose Levels of NMD670 in Adult Patients With Myasthenia Gravis (SYNAPSE-MG)Myasthenia Gravis | Myasthenia Gravis, MuSK
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Dianthus TherapeuticsRecruitingMyasthenia Gravis, GeneralizedUnited States