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Clinical Trials on Congenital Myasthenic Syndrome
Total 40721 results
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Rigshospitalet, DenmarkCompletedEisenmenger SyndromeDenmark
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University Hospital, LilleGroupement Interrégional de Recherche Clinique et d'Innovation; french patient...Not yet recruiting
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CelgeneCompletedMyelodysplastic SyndromesUnited States, Germany
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Children's National Research InstituteEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationChild Development | Congenital Zika Syndrome | Zika Virus | Congenital InfectionUnited States, Colombia
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Joanne Kurtzberg, MDAldagenCompletedAnemia, Aplastic | MDS | Inborn Errors of Metabolism | Congenital Marrow Failure | Congenital Immunodeficiency SyndromeUnited States
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Centre Hospitalier Universitaire de la RéunionRecruitingArrhythmias, Cardiac | Cardiac Conduction System Disease | Brugada Syndrome | Long QT SyndromeRéunion
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Tel-Aviv Sourasky Medical CenterUnknownLong QT Syndrome Type 3Israel
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NYU Langone HealthWithdrawnEpilepsy | Tuberous Sclerosis | Dravet Syndrome | Focal Seizures | Lennox-Gastaut SyndromeUnited States
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National Cancer Institute (NCI)CompletedDyskeratosis Congenita | Telomere Biology DisordersUnited States
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Rigshospitalet, DenmarkAarhus University Hospital; Bispebjerg Hospital; ActelionCompletedTricuspid Atresia | Hypoplastic Left Heart Syndrome | Other Specified Congenital Anomalies of HeartDenmark, Sweden
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IRCCS Policlinico S. DonatoRecruitingMarfan Syndrome | Marfan's Syndrome With Cardiovascular ManifestationsItaly
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National Heart Centre SingaporeUnknown
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Gilead SciencesTerminatedLong QT Syndrome Type 3United States, Germany, Canada, Netherlands, Italy, France, Israel, United Kingdom
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Oslo University HospitalUniversity of BergenCompletedHeart Defects, Congenital | Hypoplastic Left Heart SyndromeNorway
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University Hospital, BordeauxRecruiting
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Mayo ClinicBlue Ox Health Corporation; Minnesota Health Solutions; iCardiac TechnologiesTerminated
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University of Maryland, BaltimoreNational Human Genome Research Institute (NHGRI)Terminated
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Tel-Aviv Sourasky Medical CenterTel Aviv Medical CenterCompleted
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PediatrixCompletedLong QT SyndromeUnited States
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University of Colorado, DenverUniversity of Oslo; Mayo Clinic; Children's Hospital Colorado; Vanderbilt University and other collaboratorsCompletedLong QT SyndromeUnited States
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Sykehuset TelemarkOslo University HospitalCompletedLong QT SyndromeNorway
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QT Medical, Inc.University of California, Irvine; Lundquist Institute for Biomedical Innovation...Unknown
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argenxRecruiting
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Ad scientiamRecruitingMyasthenia GravisUnited Kingdom, United States, Canada
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Nguyen Dang ThuHanoi Medical UniversityCompletedMyasthenia Gravis
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University of AlbertaCSL BehringCompleted
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Harbour BioMed (Guangzhou) Co. Ltd.CompletedMyasthenia GravisChina
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Barts & The London NHS TrustLiverpool Heart and Chest Hospital NHS Foundation Trust; Aortic Dissection...Not yet recruitingMarfan Syndrome | Marfan Syndrome Cardiovascular Manifestations
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University Hospital, ToulouseCompletedChild SyndromeFrance
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Children's Healthcare of AtlantaCompleted
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University Hospital, GrenobleRecruitingArthrogryposis Multiplex Congenita (AMC)France
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Thryv Therapeutics, Inc.Recruiting
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Istituto Auxologico ItalianoRecruiting
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Andrew KrahnCompleted
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Silence Therapeutics plcWithdrawnNon-transfusion-dependent Thalassemia | Low Risk Myelodysplastic SyndromeUnited Kingdom, Bulgaria
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Duke UniversityPatient-Centered Outcomes Research Institute; Beth Israel Deaconess Medical...CompletedAutoimmune Diseases | Neurological DisorderUnited States, Canada
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University Hospital, GrenobleNot yet recruitingArthrogryposis Multiplex Congenita (AMC)
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NovartisCompletedMyelodysplastic Syndromes | Hemoglobinopathies | Diamond-Blackfan Anemia | Transfusional Iron Overload | Other Inherited or Acquired Anaemia | MPD Syndrome | Other Rare AnaemiasAustralia
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dr. Laura C. G. de Graaff-HerderRecruitingDisorders of Sex Development | Congenital Adrenal Hyperplasia | Tuberous Sclerosis | Kallmann Syndrome | Prader-Willi Syndrome | Neurofibromatosis | Rett Syndrome | 22q11 Deletion Syndrome | Turner Syndrome | Noonan Syndrome | Allan-Herndon-Dudley Syndrome | Saethre-Chotzen Syndrome | Congenital Hypopituitarism | Cornelia... and other conditionsNetherlands
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University Hospital, BordeauxFondation Syndrome de Rubinstein-TaybiCompletedRubinstein-Taybi SyndromeFrance
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Silence Therapeutics plcCompletedNon-transfusion-dependent Thalassemia | Low Risk Myelodysplastic Syndrome | Very-Low Risk Myelodysplastic SyndromeThailand, Israel, Jordan, United Kingdom, Germany, Italy, Malaysia
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Ain Shams UniversityRecruitingWolf Parkinson White Syndrome | ArrythmiasEgypt
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University of AlbertaCompletedPhysical Activity | Hypoplastic Left Heart Syndrome | Congenital Heart DefectCanada
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Istanbul Medipol University HospitalUnknownCarpal Tunnel Syndrome | Palmaris Longus Muscle, Absence of | EMG SyndromeTurkey
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Qlaris Bio, Inc.CompletedOcular Hypertension | Glaucoma | Glaucoma Congenital | Sturge-Weber Syndrome (SWS)United States
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Anglia Ruskin UniversityMid and South Essex NHS Foundation TrustUnknownCataract | Pseudoexfoliation Syndrome | Ectopia Lentis | Marfan's Syndrome With Ocular Manifestations | PhakodonesisUnited Kingdom
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Jason Robert GotlibCelgene CorporationTerminatedLeukemia | Anemia | Myelodysplastic Syndromes (MDS) | Acute Myeloid Leukemia (AML)United States
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Diane GeorgeActive, not recruitingSickle Cell Disease | Hemoglobinopathies | Severe Congenital Neutropenia | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Macrophage Activation Syndrome | Bone Marrow Failure Syndrome | Amegakaryocytic Thrombocytopenia | Schwachman Diamond Syndrome | Primary Immunodeficiency Syndromes | Acquired Immunodeficiency... and other conditionsUnited States