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- US Clinical Trials Registry
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Clinical Trials on Congenital Myotonic Dystrophy
Total 10297 results
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Xiamen Ophthalmology Center Affiliated to Xiamen...Active, not recruitingBietti's Crystalline DystrophyChina
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University of Southern CaliforniaRecruitingRecessive Dystrophic Epidermolysis BullosaUnited States
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Stanford UniversityRecruitingEpidermolysis Bullosa DystrophicaUnited States
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Phoenix Tissue Repair, Inc.CompletedRecessive Dystrophic Epidermolysis BullosaUnited States
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Avidity Biosciences, Inc.RecruitingDuchenne Muscular Dystrophy | Exon 44United States
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PTC TherapeuticsTerminatedLimb-Girdle Muscular DystrophyUnited States, Norway, Canada, Sweden, Russian Federation, Denmark, France, Germany
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NS Pharma, Inc.Approved for marketingMuscular Dystrophy, Duchenne | DMD
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Hacettepe UniversityCompletedPerformance | Duchenne Muscular Dystrophy | FlexibilityTurkey
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Hacettepe UniversityCompletedPerformance | Duchenne Muscular Dystrophy | FlexibilityTurkey
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Cooperative International Neuromuscular Research...aTyr Pharma, Inc.; Muscular Dystrophy Canada; FSHD Global Research Foundation; FSH...CompletedFacioscapulohumeral Muscular DystrophyUnited States, Canada, Australia, Sweden, United Kingdom
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Rigshospitalet, DenmarkCompletedLimb-girdle Muscular DystrophyDenmark
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Stanford UniversityUniversity of Pennsylvania; University of California, Davis; Oregon Health and... and other collaboratorsRecruitingFuchs' Endothelial Dystrophy | Fuchs Dystrophy | FuchsUnited States
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Michael D. Straiko, MDLions VisionGift Research; Eye Bank Association of AmericaRecruitingFuchs Endothelial DystrophyUnited States
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Trefoil Therapeutics, Inc.CompletedFuchs' Endothelial Dystrophy | Fuchs Dystrophy | FuchsUnited States
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Nantes University HospitalCompletedLeber Congenital AmaurosisFrance
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Phoenicis TherapeuticsNot yet recruitingDystrophic Epidermolysis BullosaUnited States
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Thomas Jefferson UniversityOnconova Therapeutics, Inc.RecruitingRecessive Dystrophic Epidermolysis BullosaUnited States
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Castle Creek Biosciences, LLC.Active, not recruitingRecessive Dystrophic Epidermolysis BullosaUnited States
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Phoenix Tissue Repair, Inc.Phoenix Tissue Repair, a BridgeBio companyCompletedRecessive Dystrophic Epidermolysis BullosaUnited States
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RHEACELL GmbH & Co. KGFGK Clinical Research GmbH; Ticeba GmbH; Granzer Regulatory Consulting & ServicesCompletedRecessive Dystrophic Epidermolysis BullosaUnited States, Austria, France, Germany, United Kingdom
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Phoenix Tissue Repair, Inc.CompletedRecessive Dystrophic Epidermolysis BullosaUnited States
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Gangnam Severance HospitalDaewoong Pharmaceutical Co. LTD.CompletedRecessive Dystrophic Epidermolysis BullosaKorea, Republic of
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King's College LondonUniversity College, LondonCompletedRecessive Dystrophic Epidermolysis BullosaUnited Kingdom
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Stanford UniversityCompletedEpidermolysis Bullosa DystrophicaUnited States
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Universitaire Ziekenhuizen KU LeuvenFund for Scientific Research, Flanders, Belgium; Funds for Research in Ophthalmology... and other collaboratorsCompletedFuchs' Endothelial DystrophyBelgium
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Abeona Therapeutics, IncNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedEpidermolysis Bullosa | Epidermolysis Bullosa DystrophicaUnited States
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Holostem Terapie Avanzate s.r.l.Paracelsus Medical UniversityTerminatedRecessive Dystrophic Epidermolysis BullosaAustria
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Columbia UniversityTerminatedEpidermolysis BullosaUnited States
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University of Southern CaliforniaCompletedRecessive Dystrophic Epidermolysis Bullosa
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University of Southern CaliforniaCompleted
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King's College LondonUnknownRecessive Dystrophic Epidermolysis BullosaUnited Kingdom
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Stanford UniversityTerminatedEpidermolysis Bullosa DystrophicaUnited States
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Seoul National University HospitalRecruitingMuscular Dystrophy, Duchenne | Upper Extremity | Orthotic DevicesKorea, Republic of
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Benitec Biopharma, Inc.RecruitingOculopharyngeal Muscular DystrophyUnited States
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Assistance Publique - Hôpitaux de ParisNot yet recruitingDuchenne Muscular DystrophyFrance
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University of MalagaCompletedMuscular Dystrophy, Duchenne and Becker TypesSpain
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Sarepta Therapeutics, Inc.Active, not recruiting
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University of FloridaCompleted
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Cooperative International Neuromuscular Research...United States Department of Defense; National Institutes of Health (NIH); U.S... and other collaboratorsUnknownDuchenne Muscular DystrophyUnited States, Canada, Australia, India, Israel, Argentina, Italy, Sweden
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National Center for Research Resources (NCRR)National Institute of Neurological Disorders and Stroke (NINDS); University...CompletedDuchenne Muscular Dystrophy
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Başak Çağla ArslanHacettepe UniversityRecruitingDuchenne Muscular Dystrophy | Occupational Therapy | GamificationTurkey
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Assiut UniversityNot yet recruitingLimb-girdle Muscular Dystrophy
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Sarepta Therapeutics, Inc.RecruitingLimb-girdle Muscular DystrophyUnited States
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Edgewise Therapeutics, Inc.Worldwide Clinical TrialsCompletedBecker Muscular Dystrophy | Healthy VolunteerUnited States
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Dokuz Eylul UniversityCompletedDuchenne Muscular Dystrophy | Upper Extremity ProblemTurkey
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Hacettepe UniversityCompletedPerformance | Duchenne Muscular Dystrophy | Gait | EnergyTurkey
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Rigshospitalet, DenmarkCompleted
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Santhera PharmaceuticalsCompletedMuscular Dystrophy, Duchenne | Ambulatory CareUnited States, Spain, Austria, Belgium, France, Germany, Italy, Netherlands, Sweden, Switzerland
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University Hospital, GrenobleCompletedPediatric ALL | Arthrogryposis Multiplex Congenita | AMC-Arthrogryposis Multiplex CongenitaFrance
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingDuchenne Muscular Dystrophy | Natural History | Motor Function; RetardationItaly