- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Defect, Congenital in United States
Total 4960 results
-
Great Ormond Street Hospital for Children NHS Foundation...National Institute for Health Research, United KingdomRecruitingEsophageal Atresia With Tracheoesophageal FistulaUnited Kingdom
-
Vitaccess LtdPharnext SA; Charcot-Marie-Tooth Association; ACMT-Rete per la malattia di Charcot-Marie-Tooth... and other collaboratorsRecruitingCharcot-Marie-Tooth DiseaseUnited Kingdom
-
Cardiff UniversityNovartisUnknownTuberous SclerosisUnited Kingdom
-
ACADIA Pharmaceuticals Inc.RecruitingHyperphagia in Prader-Willi SyndromeUnited States, Canada, United Kingdom
-
Zimmer BiometRecruitingRheumatoid Arthritis | Osteoarthritis, Knee | Avascular Necrosis | Traumatic Arthritis | Varus Deformity | Valgus Deformity | Knee Pain Chronic | Polyarthritis | Flexion Deformity of KneeUnited States
-
Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited Kingdom, Malaysia
-
Washington University School of MedicineNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National...CompletedDiabetes Mellitus | Ataxia | Wolfram Syndrome | Optic Nerve AtrophyUnited States
-
Amylyx Pharmaceuticals Inc.Active, not recruiting
-
NHS Greater Glasgow and ClydePublic Health ScotlandRecruitingDrug Effect | Drug Use | Drug Abuse | Drug Toxicity | Illicit Drug Use | Overdose, Drug | Illicit Drug Overdose | Illicit Drug IntoxicationUnited Kingdom
-
Novartis PharmaceuticalsCompletedFragile X SyndromeUnited States, Belgium, Australia, Israel, Switzerland, Germany, France, Canada, Denmark, Indonesia, Italy, Netherlands, Spain, Sweden, Turkey, United Kingdom
-
National Heart, Lung, and Blood Institute (NHLBI)CompletedSickle Cell Anemia | Pulmonary Hypertension | Cerebrovascular Disease | Chuvash PolycythemiaUnited States, Russian Federation
-
Papworth Hospital NHS Foundation TrustRecruitingRespiratory Disease | Excessive Dynamic Airway Collapse | Tracheobronchomalacia | Excessive Central Airways CollapseUnited Kingdom
-
NHS Greater Glasgow and ClydeUnknownNeuropathic Pain | Arteriovenous FistulaeUnited Kingdom
-
Bangor UniversityBetsi Cadwaladr University Health BoardCompleted
-
Merck Sharp & Dohme LLCCompletedPneumococcal InfectionsUnited States, Brazil, Colombia, Dominican Republic, Greece, Italy, Panama
-
Jazz PharmaceuticalsRecruitingTuberous Sclerosis Complex Associated Neuropsychiatric DiseaseUnited States, United Kingdom, Poland
-
Avita MedicalCompletedCellulitis | Surgical Wound | Skin Cancer | Infection | Crush Injuries | Degloving Injuries | Gun Shot Wound | Necrotizing Fasciitis | Laceration of Skin | Full-thickness Skin DefectsUnited States
-
Sequenom, Inc.CompletedDown Syndrome | Aneuploidy | Noninvasive Prenatal ScreeningUnited States
-
ASH Research CollaborativeUniversity of Pennsylvania; American Society of HematologyCompleted
-
ActelionNational Heart, Lung, and Blood Institute (NHLBI)TerminatedSickle Cell Anemia | Pulmonary HypertensionUnited States, Netherlands, United Kingdom
-
Eunice Kennedy Shriver National Institute of Child...RecruitingNiemann-Pick Disease Type C1 | Juvenile Neuronal Ceroid Lipofuscinosis | Smith-Lemli-Opitz Syndrome | Creatine Transporter DeficiencyUnited States
-
Millendo Therapeutics SASTerminatedHyperphagia | Prader-Willi SyndromeUnited States, Belgium, Spain, France, Italy, United Kingdom, Australia, Netherlands
-
Novartis PharmaceuticalsCompletedTransfusional Iron Overload in β-thalassemiaUnited States, Greece, Argentina, Germany, Belgium, Italy, United Kingdom, France, Tunisia, Canada, Turkey, Brazil
-
Silence Therapeutics plcWithdrawnNon-transfusion-dependent Thalassemia | Low Risk Myelodysplastic SyndromeUnited Kingdom, Bulgaria
-
Boston Children's HospitalLymphatic Malformation InstituteRecruitingLymphangiomatosis | Kaposiform Lymphangiomatosis | Lymphatic Malformation | Generalized Lymphatic Anomaly (GLA) | Central Conducting Lymphatic Anomaly | CLOVES Syndrome | Gorham-Stout Disease ("Disappearing Bone Disease") | Blue Rubber Bleb Nevus Syndrome | Kaposiform Hemangioendothelioma/Tufted Angioma and other conditionsUnited States
-
HedgePath Pharmaceuticals, Inc.CompletedBasal Cell Carcinoma in Basal Cell Nevus SyndromeUnited States
-
Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
-
Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsRecruitingCongenital Amegakaryocytic Thrombocytopenia | Paroxysmal Nocturnal Hemoglobinuria | Diamond-Blackfan Anemia | Shwachman-Diamond Syndrome | Bone Marrow Failure Syndrome | Hereditary Sideroblastic Anemia | Hematologic Neoplasm With Germline GATA2 Mutation | Hematologic Neoplasm With Germline SAMD9... and other conditionsUnited States
-
Aldeyra Therapeutics, Inc.CompletedSjögren-Larsson SyndromeUnited States
-
Neuren Pharmaceuticals LimitedCompleted
-
SangartCompletedSickle Cell Disease | Anemia, Sickle Cell | Sickle Cell Anemia | Hemoglobin SC Disease | Sickle Cell Disorders | Sickle Cell Hemoglobin C DiseaseUnited Kingdom, France, Jamaica, Lebanon
-
Cytori TherapeuticsCompletedBreast Neoplasms | Carcinoma, Ductal, Breast | Mammaplasty | Mastectomy, Segmental, Lumpectomy, Breast Reconstruction,Spain, United Kingdom, Belgium, Italy
-
Mast Therapeutics, Inc.CompletedSickle Cell Disease | Vaso-occlusive CrisisUnited States, Belgium, Brazil, Dominican Republic, Jamaica, Jordan, Lebanon, Oman, Panama, Spain, Turkey
-
Novartis PharmaceuticalsCompletedAnemia, Sickle CellUnited States
-
Nemours Children's ClinicPotentials Foundation; Walking with Giants FoundationRecruitingMOPDII | RNU4atac-opathy (e.g. MOPDI/III, Lowry-Wood Syndrome, Roifman Syndrome) | Meier-Gorlin Syndrome | Saul-Wilson Syndrome | Ligase 4 Syndrome | Microcephalic Primordial DwarfismUnited States
-
HemaQuest Pharmaceuticals Inc.CompletedSickle Cell Disease | Sickle Cell Anemia | Sickle Cell Disorders | Hemoglobin S Disease | Sickling Disorder Due to Hemoglobin SUnited States, Lebanon, Canada, Egypt, Jamaica
-
Vesper Medical, Inc.Active, not recruitingDeep Vein Thrombosis | Chronic Venous Insufficiency | May-Thurner SyndromeUnited States, Poland
-
Nemours Children's ClinicRecruitingCharcot-Marie-Tooth Disease | Motor Neuron Disease | Amyotrophic Lateral Sclerosis | Muscular Dystrophy | Spinal Muscular Atrophy | Neuromuscular Disease | Spinal Muscular Atrophy With Respiratory Distress 1 | Peroneal Muscular AtrophyUnited States
-
University Hospitals Bristol and Weston NHS Foundation...University College, London; The Tuberous Sclerosis AssociationActive, not recruitingTuberous Sclerosis ComplexUnited Kingdom
-
Manchester University NHS Foundation TrustUniversity of Oxford; University of LiverpoolCompletedPremature Birth | Enterocolitis, Necrotizing | Gastroschisis | Meconium Ileus | Bowel Obstruction | Atresia; Bowel | Perforation BowelUnited Kingdom
-
University College London HospitalsKingston University; Charcot Marie Tooth United KingdomCompletedCharcot-Marie-Tooth Disease, Type IAUnited Kingdom
-
Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A | Haemophilia BUnited Kingdom
-
Hoffmann-La RocheCompletedFragile X SyndromeFrance, Spain, United States, Peru, Canada, United Kingdom, Chile, Argentina, Mexico, Sweden
-
Dana-Farber Cancer InstituteNational Cancer Institute (NCI); Wyeth is now a wholly owned subsidiary of... and other collaboratorsCompletedTuberous Sclerosis | Nonmalignant Neoplasm | Lymphangioleimyomatosis | Kidney AngiomyolipomaUnited States
-
Centre hospitalier de l'Université de Montréal...Centre Hospitalier Régional et Universitaire de BrestRecruitingArteriovenous Malformations | Unruptured Brain Arteriovenous Malformation | Ruptured Brain Arteriovenous Malformation | AVM | BAVMFrance, United States, Canada, Brazil, Chile, Colombia
-
Zynerba Pharmaceuticals, Inc.RecruitingFragile X SyndromeUnited States, Australia, United Kingdom, Ireland
-
King's College LondonUnknown
-
Agios Pharmaceuticals, Inc.Active, not recruitingTransfusion-dependent Alpha-Thalassemia | Transfusion-dependent Beta-ThalassemiaSpain, Taiwan, Thailand, United States, France, Canada, Malaysia, Germany, Netherlands, Bulgaria, United Kingdom, Turkey, Italy, Greece, United Arab Emirates, Brazil, Denmark, Lebanon, Saudi Arabia
-
Neurona TherapeuticsCalifornia Institute for Regenerative Medicine (CIRM)RecruitingMesial Temporal Lobe Epilepsy With Hippocampal SclerosisUnited States
-
Jesse NodoraNational Cancer Institute (NCI)TerminatedCoronary Artery Disease | Heart Failure | Obesity | Diabetes Mellitus, Type 2 | Cancer | Chronic Kidney Diseases | Sickle Cell Disease | COPDUnited States