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Clinical Trials on Deficiency Diseases in France
Total 34751 results
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyActive, not recruitingAlpha 1-Antitrypsin DeficiencyUnited Kingdom, United States, Ireland, Belgium, New Zealand, Spain, Netherlands, Portugal, Canada, Australia, France, Austria, Germany, Sweden
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Institut de Myologie, FranceAssociation Française contre les Myopathies (AFM), ParisNot yet recruitingMerosin Deficient Congenital Muscular DystrophyFrance
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Nantes University HospitalActive, not recruitingHIV Infections | Executive Dysfunction | Neurophysiologic Abnormality | Exposure During PregnancyFrance
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Ascendis Pharma Endocrinology Division A/SActive, not recruitingEndocrine System Diseases | Adult Growth Hormone Deficiency | Hormone DeficiencyUnited States, Armenia, Georgia, Greece, Ukraine, Australia, Canada, France, Israel, Italy, Japan, Malaysia, Poland, Romania, Serbia, Slovakia, Spain, Turkey, United Kingdom, Germany, Korea, Republic of
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BioCryst PharmaceuticalsActive, not recruitingHereditary Angioedema | PediatricSpain, Austria, Canada, France, Germany, Israel, Italy, Poland, Romania, United Kingdom
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ANRS, Emerging Infectious DiseasesViiV HealthcareCompleted
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ShireCompletedHereditary Angioedema (HAE)Germany, Spain, United Kingdom, France, Italy, Belgium
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Kyowa Kirin Pharmaceutical Development LtdCompletedX-linked Hypophosphatemia (XLH)Sweden, Spain, United Kingdom, Italy, Austria, France
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Ascendis Pharma A/SCompletedEndocrine System Diseases | Pituitary Diseases | Hormone Deficiency | Growth Hormone Deficiency, PediatricUnited States, Armenia, Belarus, Bulgaria, Georgia, Greece, Russian Federation, Ukraine, Australia, New Zealand, Poland
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencyFrance, United States, Israel, Spain, Switzerland, Germany, Canada, Japan, United Kingdom, Italy, Finland, Austria
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ANRS, Emerging Infectious DiseasesBristol-Myers SquibbCompleted
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Assistance Publique - Hôpitaux de ParisARC Foundation for Cancer ResearchCompleted
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Pharming Technologies B.V.RecruitingHereditary AngioedemaGermany, Bulgaria, Croatia, Czechia, France, Hungary, Italy, North Macedonia, Poland, Slovakia, Norway, Slovenia, Sweden
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Centre Hospitalier de CayenneUnknown
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University Paris 7 - Denis DiderotViiV HealthcareRecruiting
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Direction Centrale du Service de Santé des ArméesUnknownKaposi's DiseaseFrance
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CSL BehringCompletedPrimary Immunodeficiency (PID)Poland, Germany, France, Romania, Spain, Sweden, Switzerland, United Kingdom
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Bristol-Myers SquibbTerminated
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Objectif Recherche Vaccins SIDACompletedHIV InfectionUnited States, France, Germany, Spain
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Centre Hospitalier de CayenneEuropean Regional Development FundRecruitingChildren | Dengue Fever | AdultsFrance
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CSL BehringRecruitingHereditary Angioedema (HAE)United States, Israel
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DePuy InternationalTerminatedRheumatoid Arthritis | Cuff Tear Arthropathy | Osteoarthritis With Cuff Deficiency | Post Traumatic Injury to Shoulder | Revision Surgery of a Failed Anatomic Shoulder ProsthesisFrance, Belgium, Germany
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Centre Hospitalier de CayenneCompleted
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Centre Hospitalier de CayenneCompleted
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Centre Hospitalier de CayenneCompleted
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Centre Hospitalier de Cayenneuniversite de guyaneCompleted
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ANRS, Emerging Infectious DiseasesCompletedHIV InfectionFrance, Canada
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Theravectys S.A.Completed
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Centre Hospitalier de CayenneCompleted
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AbbottCompletedHIV InfectionsUnited States, France, Spain
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French National Agency for Research on AIDS and...Gilead Sciences; Hoffmann-La RocheCompletedHIV Infections | Leukoencephalopathy, Progressive MultifocalFrance
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ANRS, Emerging Infectious DiseasesUnknown
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University Hospital Center of MartiniqueUniversity Hospital of GuadeloupeTerminatedHIV Infections | Zika Virus InfectionGuadeloupe, Martinique
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Centre Hospitalier de CayenneUnknown
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FVII DeficiencySlovakia, Israel, Spain, India, Iran, Islamic Republic of, Pakistan, Turkey, Germany, Serbia, Italy, Greece, Thailand, France, United States, Hong Kong, Venezuela
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Ultragenyx Pharmaceutical IncRecruitingOTC DeficiencyUnited States, Portugal, Australia, Italy, Spain, United Kingdom, Japan, Canada, Germany, France, Argentina, Netherlands, Brazil
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NEAT ID FoundationPENTA Foundation; European Commission; VERDI ConsortiumRecruitingMonkeypox | HIV CoinfectionSpain, France, Poland, United Kingdom
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Novartis PharmaceuticalsRecruitingNLRC4-GOF, AIFEC (Autoinflammation With Infantile Enterocolitis), XIAP Deficiency, CDC42 MutationsSpain, France, United States, Canada, Japan, United Kingdom, Turkey, Czechia, Italy
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Grifols Therapeutics LLCCompletedPrimary ImmunodeficiencySpain, France, Germany, United Kingdom, Australia, Czechia, Hungary, Poland, Sweden
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ANRS, Emerging Infectious DiseasesRecruiting
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French National Agency for Research on AIDS and...Completed
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Hospital St. Joseph, Marseille, FranceWithdrawnFibrillation, Atrial | To Evaluate the Intraoperative Efficiency of the AIFIB Software in the Detection of Atrial Fibrillation Driver During an Ablation ProcedureFrance, Netherlands
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DNage B.V.TerminatedCockayne SyndromeUnited States, France, United Kingdom
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ANRS, Emerging Infectious DiseasesRecruiting
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BioCryst PharmaceuticalsCompletedHereditary Angioedema (HAE)Austria, Denmark, France, Germany, Hungary, Israel, Italy, North Macedonia, Poland, Romania, Switzerland, United Kingdom
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Children's Hospital of Orange CountyCSL BehringCompleted
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PedNet Haemophilia Research FoundationLund University HospitalRecruitingFactor IX Deficiency | Factor VIII DeficiencyNorway, Austria, Belgium, Canada, Czechia, Denmark, Finland, France, Germany, Greece, Ireland, Israel, Italy, Netherlands, Portugal, Spain, Sweden, Switzerland, United Kingdom
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Hoffmann-La RocheCompleted