- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Disability in United Kingdom
Total 698 results
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Stanford UniversityCompleted
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Rett Syndrome Research TrustVanderbilt University Medical CenterCompleted
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University of MichiganNational Institutes of Health (NIH)Completed
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Simons SearchlightBoston Children's Hospital; Geisinger Clinic; Simons FoundationRecruitingSMARCA4 Gene Mutation | DDX3X | 16P11.2 Deletion Syndrome | 16p11.2 Duplications | 1Q21.1 Deletion | 1Q21.1 Microduplication Syndrome (Disorder) | ACTL6B | ADNP | AHDC1 | ANK2 | ANKRD11 | ARID1B | ASH1L | BCL11A | CHAMP1 | CHD2 | CHD8 | CSNK2A1 | CTBP1 | CTNNB1 Gene Mutation | CUL3 | DNMT3A | DSCAM | DYRK1A | FOXP1 | GRIN2A | GRIN2B | HIVEP2-Related Intellectual... and other conditionsUnited States
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Neuren Pharmaceuticals LimitedRecruitingPitt Hopkins SyndromeUnited States
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Rowan UniversityUniversity of Pennsylvania; FRAXA Research FoundationUnknown
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Duke UniversityCanadian Institutes of Health Research (CIHR); National Institutes of Health... and other collaboratorsCompleted
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Children's Hospital Medical Center, CincinnatiCompleted
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Jett Foundation, Inc.Pfizer; Hoffmann-La Roche; Italfarmaco; Nationwide Children's Hospital; Capricor... and other collaboratorsCompletedDuchenne Muscular Dystrophy | Rare Diseases | Disability Physical | Burden, Dependency | Impairment | Disease ManagementUnited States
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Randi J. Hagerman, MDCompleted
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Indiana UniversityIndiana Clinical and Translational Sciences InstituteCompleted
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Indiana University School of MedicineCompletedFragile X SyndromeUnited States
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Zafgen, Inc.CompletedObesity | Prader-Willi Syndrome | Over-weightUnited States
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Stanford UniversityNational Institute of Mental Health (NIMH); Autism SpeaksCompleted
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ACADIA Pharmaceuticals Inc.Completed
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Life Molecular Imaging SACompletedDown Syndrome | Amyloid Beta-proteinUnited States
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TakedaAvailableHunter SyndromeUnited States, Australia, Mexico, Spain, United Kingdom
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Anavex Life Sciences Corp.International Rett Syndrome Foundation Rettsyndrome.orgCompleted
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Foundation for Prader-Willi ResearchRTI InternationalRecruitingPrader-Willi SyndromeUnited States
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Rutgers, The State University of New JerseyRecruitingPhysical Disability | Muscle Atrophy or Weakness | Muscle Loss | Physical Inactivity | Delirium in Old Age | Hospital Acquired Condition | Weakness, MuscleUnited States
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Rutgers, The State University of New JerseyCompletedObesity | Prader-Willi SyndromeUnited States
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Children's Hospital Medical Center, CincinnatiRush University Medical CenterCompleted
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University of UtahThe Hospital for Sick Children; Boston Children's HospitalCompletedAtherosclerosis | Down Syndrome | Cardiovascular Risk FactorUnited States
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Montefiore Medical CenterRecruitingHyperphagia | Prader-Willi SyndromeUnited States
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Montefiore Medical CenterFoundation for Prader-Willi ResearchCompletedHyperphagia | Prader-Willi SyndromeUnited States
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University of HartfordUniversita di VeronaTerminatedCerebral Palsy | Down Syndrome | Autism | Balance | PostureUnited States
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University of FloridaNational Institutes of Health (NIH)Completed
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Children's Hospital of PhiladelphiaEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedDown Syndrome | Subclinical HypothyroidismUnited States
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Children's Hospital of PhiladelphiaEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompleted
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NeuropharmCompleted
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Hoskinson Health and Wellness ClinicUniversity of Wyoming; Buck Institute for Research on AgingRecruitingDepression | Cardiovascular Diseases | Inflammation | Hypertension | Obesity | Cognitive Impairment | Insulin Resistance | Hyperlipidemias | Physical Disability | Physical Inactivity | Hormone Deficiency | OvereatingUnited States
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Icahn School of Medicine at Mount SinaiRecruitingAutism Spectrum Disorder | DDX3X | Mental Retardation, X-linked 102United States
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National Institute of Mental Health (NIMH)RecruitingWilliams Syndrome | DuplicationUnited States
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Weill Medical College of Cornell UniversityNational Institutes of Health (NIH); PWSAUSATerminatedPrader-willi SyndromeUnited States
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Stanford UniversityThe John Merck FundCompletedFragile X Syndrome | Disruptive BehaviorUnited States
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NYU Langone HealthWinthrop University HospitalWithdrawn
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University of Colorado, DenverCompletedCerebral Palsy | Spinal Cord Injuries | Physical Disability | Traumatic Brain InjuriesUnited States
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Stanford UniversityCompletedDevelopmental Disabilities | Fragile X SyndromeUnited States
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Massachusetts General HospitalCompleted
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University of FloridaFoundation for Prader-Willi ResearchCompleted
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Children's Healthcare of AtlantaTerminated
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Harmony Biosciences, LLCRecruiting
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University of Wisconsin, MadisonUltragenyx Pharmaceutical IncCompletedPrader-Willi Syndrome | Angelman SyndromeUnited States
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Guido A. Davidzon, MD, SMWithdrawn
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Tetra Discovery PartnersCompletedFragile X Syndrome | Fra(X) Syndrome | FXSUnited States
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University of Wisconsin, MilwaukeeCompletedWilliams SyndromeUnited States
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Sequenom, Inc.RecruitingDown Syndrome | Fetal AneuploidyUnited States, Canada
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Children's Hospital of PhiladelphiaNational Institute of Neurological Disorders and Stroke (NINDS); Vanderbilt...RecruitingRett Syndrome | Rett Syndrome, Atypical | RTTUnited States
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Hennepin Healthcare Research InstituteNational Health and Medical Research Council, Australia; National Cancer Institute... and other collaboratorsActive, not recruitingDepression | Stroke | Cancer | Bleeding | Dementia | Heart Disease | Functional DisabilityUnited States, Australia
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GLWL Research Inc.CompletedPrader-Willi SyndromeUnited States, Canada