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Clinical Trials on Diseases Genetic, Genetic in New Zealand
Total 44204 results
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Liggins InstituteRecruiting
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Tavotek BiotherapeuticsRecruiting
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Arcturus Therapeutics, Inc.CompletedOrnithine Transcarbamylase DeficiencyNew Zealand
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Ribon Therapeutics, Inc.RecruitingAtopic DermatitisAustralia, New Zealand
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Boston Children's HospitalBoston Medical Center; National Human Genome Research Institute (NHGRI); University... and other collaboratorsRecruitingGenetic Predisposition to Disease | Genetics Disease | Genetics/Birth DefectsUnited States
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ReCode TherapeuticsRecruitingCystic FibrosisNew Zealand
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Arcturus Therapeutics, Inc.Novotech CRORecruiting
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Arrowhead PharmaceuticalsRecruitingFacio-Scapulo-Humeral DystrophyNew Zealand
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Arthrosi TherapeuticsCompletedGout PatientsNew Zealand
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Dicerna Pharmaceuticals, Inc.WithdrawnAlpha 1-Antitrypsin DeficiencyNew Zealand
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Arrowhead PharmaceuticalsCompleted
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Akesobio Australia Pty LtdCompletedAtopic DermatitisNew Zealand, Australia
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyCompleted
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Regeneron PharmaceuticalsSanofiCompletedAtopic DermatitisGermany, New Zealand, Australia
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Arrowhead PharmaceuticalsRecruitingMyotonic Dystrophy 1New Zealand, Australia
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Columbia UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruitingGenetic Disease | Prenatal Diagnosis | Copy Number AbnormalityUnited States
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Verve Therapeutics, Inc.Enrolling by invitationHypercholesterolemia | Atherosclerotic Cardiovascular Disease | Heterozygous Familial HypercholesterolemiaNew Zealand, United Kingdom
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Verve Therapeutics, Inc.Active, not recruitingHypercholesterolemia | Atherosclerotic Cardiovascular Disease | Heterozygous Familial HypercholesterolemiaNew Zealand, United Kingdom
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Genomic Prediction Inc.RecruitingInfertility | Genetic Disease | IVFUnited States
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Columbia UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedGenetic DiseasesUnited States
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Vanderbilt University Medical CenterRecruitingGenetic DiseaseUnited States
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CSL LimitedCompletedPrimary Immune DeficiencyAustralia, New Zealand
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Arrowhead PharmaceuticalsCompletedDyslipidemias | Hypertriglyceridemia | Familial HypercholesterolemiaAustralia, New Zealand
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Memorial Sloan Kettering Cancer CenterMayo Clinic; University of Pennsylvania; Dana-Farber Cancer InstituteActive, not recruiting
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Cystetic Medicines, Inc.DevPro BiopharmaRecruitingCystic FibrosisAustralia, New Zealand
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Rutgers, The State University of New JerseyNational Cancer Institute (NCI); Georgetown UniversityRecruitingHereditary Cancer | Genetic TestingUnited States
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PharmaxisCompletedCystic FibrosisAustralia, New Zealand
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Alexion Pharmaceuticals, Inc.CompletedWilson DiseaseUnited States, New Zealand, United Kingdom
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Botanix PharmaceuticalsCompletedAtopic DermatitisUnited States, Australia, New Zealand
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Akesobio Australia Pty LtdRecruitingPhase 2 Study of Efficacy and Safety of AK120, in Subjects With Moderate-to-Severe Atopic DermatitisAtopic DermatitisUnited States, Australia, New Zealand
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Columbia UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompleted
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Murdoch Childrens Research InstituteUniversity of Sydney; Sydney Children's Hospitals Network; Women's and Children... and other collaboratorsActive, not recruitingAutosomal Recessive Disorder | X-Linked Genetic DiseasesAustralia
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Icahn School of Medicine at Mount SinaiAlbert Einstein College of Medicine; National Institute on Minority Health... and other collaboratorsCompletedGenetic Diseases, Inborn | Genetic Predisposition to DiseaseUnited States
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MedImmune LLCAmgenCompletedAtopic DermatitisUnited States, Germany, New Zealand, Hungary, Australia, Canada
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Memorial Sloan Kettering Cancer CenterPhenogen SciencesRecruitingGenetic Testing | BRCA1/2United States
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The University of QueenslandTelethon Kids InstituteCompletedBronchiectasis | Cystic FibrosisAustralia, New Zealand
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Yale UniversityCompletedSkin Diseases | Immune System Diseases | Hypersensitivity | Hypersensitivity, Immediate | Skin Diseases, Genetic | Dermatitis | Eczema | Skin Diseases, Eczematous | Dermatitis, Atopic | Genetic Disease, InbornUnited States
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Baxalta now part of ShireCompletedAlpha 1-Antitrypsin DeficiencyNew Zealand, Australia
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Zynerba Pharmaceuticals, Inc.CompletedFragile X SyndromeUnited States, New Zealand, Australia
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Virginia Commonwealth UniversityEdgewise Therapeutics, Inc.RecruitingMuscular Dystrophies | Becker Muscular Dystrophy | Muscular Dystrophy in Children | Muscular Dystrophy, BeckerUnited States, New Zealand, United Kingdom
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Intellia TherapeuticsEnrolling by invitationHereditary AngioedemaFrance, New Zealand, United Kingdom, Netherlands
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Intellia TherapeuticsRecruitingTransthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy | Wild-Type Transthyretin Cardiac AmyloidosisUnited Kingdom, New Zealand, Sweden
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CSL LimitedCompleted
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University of Medicine and Dentistry of New JerseyGenentech, Inc.Completed
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Arrowhead PharmaceuticalsTerminatedCystic Fibrosis, PulmonaryAustralia, New Zealand
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Atlantic Health SystemReproductive Medicine Associates of New JerseyCompletedPelvic Organ ProlapseUnited States
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Novo Nordisk A/SCompletedKidney Diseases | Urologic Diseases | Genetic Disease | Primary Hyperoxaluria Type 1 (PH1) | Primary Hyperoxaluria Type 2 (PH2)Poland, United States, United Kingdom, New Zealand, Australia, Canada, France, Germany, Israel, Italy, Japan, Lebanon, Netherlands, Romania, Spain
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Baxalta now part of ShireBaxter Healthcare, Ltd. (New Zealand), Baxter Healthcare Pty. Ltd. (Australia)CompletedAlpha 1-Antitrypsin DeficiencyAustralia, New Zealand
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PfizerTerminatedHemophilia AUnited States, New Zealand
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ThermiGen, LLCCompletedSkin LaxityUnited States