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Clinical Trials on Disorder of Bile Acid and Cholesterol Metabolism in New Zealand
Total 4488 results
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Intellia TherapeuticsRecruitingTransthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy | Wild-Type Transthyretin Cardiac AmyloidosisUnited Kingdom, New Zealand, Sweden
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Arcturus Therapeutics, Inc.Active, not recruitingOrnithine Transcarbamylase DeficiencyUnited States
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BioMarin PharmaceuticalApproved for marketing
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Genzyme, a Sanofi CompanyTerminatedNiemann-Pick Disease | Acid Sphingomyelinase DeficiencyUnited States
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BioMarin PharmaceuticalCompleted
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Eli Lilly and CompanyCompletedType 2 DiabetesIndia, Mexico, New Zealand, South Africa
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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Tulane UniversityCompletedCongenital Disorders of GlycosylationUnited States
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Anne Birgitte RabenUniversity of Nottingham; University of Helsinki; Wageningen University; University... and other collaboratorsCompletedObesity | Pre-diabetesSpain, Denmark, Australia, Bulgaria, Finland, Netherlands, New Zealand, United Kingdom
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SangartCompletedShock, Hemorrhagic | Acidosis, Lactic | Shock, TraumaticNorway, Singapore, Israel, France, United Kingdom, Germany, Switzerland, Australia, Brazil, South Africa, New Zealand, Colombia, Austria, Spain
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University of SouthamptonNational University Hospital, Singapore; Singapore Institute for Clinical Sciences and other collaboratorsEnrolling by invitationNeurobehavioral Manifestations | Allergy | Microbial Colonization | Growth Disorders | Atopic Dermatitis | Obesity, Childhood | Metabolic Disturbance | Cognition | Lifestyle | Breastfeeding | Nutrition, Healthy | AtopySingapore, United Kingdom, New Zealand
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Horizon Therapeutics, LLCCompletedUrea Cycle DisordersUnited States, Canada
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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Zealand University HospitalCenter of Surgical Science, Department of Surgery, Zealand University HospitalActive, not recruitingDepression | Quality of Life | Sleep | Colorectal Neoplasm | Circadian Rhythm Sleep DisorderDenmark
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SynlogicCompletedPhenylketonuriaUnited States
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Ultragenyx Pharmaceutical IncRecruitingLong-chain Fatty Acid Oxidation Disorders (LC-FAOD)United States, Canada
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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BioMarin PharmaceuticalCompletedPhenylketonuria | HyperphenylalaninaemiaUnited States
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Mendel TuchmanChildren's Hospital of Philadelphia; University of California, Los Angeles; Icahn... and other collaboratorsCompletedMethylmalonic Acidemia | Carbamoyl-Phosphate Synthase I Deficiency Disease | Propionic Acidemia, Type I and/or Type II | Ornithine Carbamoyltransferase DeficiencyUnited States
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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Yale UniversityNational Institutes of Health (NIH); National Institute on Aging (NIA); Trinity...CompletedDiabetes Mellitus | DiabetesUnited States
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Arbor Research Collaborative for HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University...RecruitingEnd Stage Liver Disease | Mitochondrial Diseases | Acute Liver Failure | Respiratory Chain Deficiencies, Mitochondrial | Disorder of Fatty Acid OxidationUnited States, Canada
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BioMarin PharmaceuticalCompleted
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SangartWithdrawnTrauma | Hemorrhagic Shock | Lactic AcidosisNew Zealand, United Kingdom, Israel, France, Switzerland, Australia, Belgium, Brazil, Germany, Norway, South Africa
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Genzyme, a Sanofi CompanyCompletedHuman Acid Sphingomyelinase DeficiencyUnited Kingdom, United States
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Boehringer IngelheimCompletedDiabetes Mellitus, Type 2United States
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BioMarin PharmaceuticalCompletedPhenylketonuria (PKU)United States
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State University of New York at BuffaloTerminatedDiabetic KetoacidosisUnited States
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Rockefeller UniversityCompletedGlucose Metabolism DisorderUnited States
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BioMarin PharmaceuticalRecruitingPhenylketonuria (PKU)United States, Germany, Italy
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Intellia TherapeuticsActive, not recruitingTransthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy | Wild-Type Transthyretin Cardiac AmyloidosisFrance, United Kingdom, New Zealand, Sweden
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Homology Medicines, IncTerminated
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Jnana TherapeuticsRecruitingPhenylketonuriaUnited States, Australia
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Arrowhead PharmaceuticalsActive, not recruitingMixed DyslipidemiaUnited States, Australia, Canada, New Zealand
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Travere Therapeutics, Inc.Active, not recruiting
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University Medical Center GroningenDutch Kidney Foundation; Innovation Fund of the Dutch Medical Insurance CompaniesCompletedMetabolic Syndrome | Kidney Transplant | Post-transplant Weight GainNetherlands
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Unity Health TorontoRoche Pharma AGCompletedDyspnea | Acute Heart Failure | Shortness of BreathCanada, United States, New Zealand
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Novartis PharmaceuticalsCompletedHypocalcemia | Paget's Disease of the BoneUnited States
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PTC TherapeuticsRecruitingPhenylketonuriaUnited States, Germany, Spain, Australia, Brazil, United Kingdom, Denmark, Mexico, Portugal, Turkey, Canada, Georgia, Italy, Netherlands, Japan
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Syneron MedicalCompleted
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BioMarin PharmaceuticalCompletedPhenylketonuria (PKU)United States
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Albert Einstein College of MedicineCompleted
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PTC TherapeuticsCompletedPhenylketonuriaSpain, United States, Australia, Germany, United Kingdom, Brazil, Denmark, Canada, France, Georgia, Italy, Mexico, Netherlands, Portugal, Turkey
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BioMarin PharmaceuticalCompletedTetrahydrobiopterin Deficiencies | Hyperphenylalaninemia, Non-PhenylketonuricGermany, United States
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CuraSen Therapeutics, Inc.Active, not recruitingMild Cognitive Impairment, Lewy Body Dementia, Parkinson's Disease Rapid Eye Movement Sleep Behavior Disorder, Parkinson's Disease DementiaAustralia, New Zealand, United Kingdom
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Italy, Canada, France, United Kingdom, Austria, Germany
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The George InstituteNot yet recruitingDiabetic KetoacidosisAustralia
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Ultragenyx Pharmaceutical IncRecruitingOTC DeficiencyUnited States, Portugal, Australia, Italy, Spain, United Kingdom, Japan, Canada, Germany, France, Argentina, Netherlands, Brazil
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Venus ConceptWithdrawn
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Boehringer IngelheimEli Lilly and CompanyCompletedDiabetes Mellitus, Type 2United States, Australia, Brazil, Canada, El Salvador, France, Korea, Republic of, New Zealand, Norway, Spain, Taiwan