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Clinical Trials on Duchenne Muscular Dystrophy (DMD)
Total 878 results
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Centre Hospitalier Universitaire de NiceCompletedFacio-Scapulo-Humeral DystrophyFrance
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Institut de Myologie, FranceAssociation Française contre les Myopathies (AFM), ParisNot yet recruitingMerosin Deficient Congenital Muscular DystrophyFrance
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Prothelia, Inc.Cure CMD; The Bönnemann Laboratory, NINDS, National Institutes of Health; Oscar... and other collaboratorsCompletedMerosin Deficient Congenital Muscular DystrophyUnited States
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University Medical Center NijmegenLeiden University Medical Center; Princess Beatrix Muscle FoundationCompletedPediatric Disorder | Facioscapulohumeral Muscular Dystrophy | Neurological ObservationsNetherlands
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Nationwide Children's HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedLimb-Girdle Muscular DystrophyUnited States
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McMaster UniversityCompletedMuscular Dystrophies | Myotonic Dystrophy 1Canada
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University Hospital, MontpellierHospital Clinical Research Project 2010; Association Amis FSH France; FSH Dutch...CompletedFacioscapulohumeral Muscular DystrophyFrance
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PTC TherapeuticsTerminatedLimb-Girdle Muscular DystrophyUnited States, Norway, Canada, Sweden, Russian Federation, Denmark, France, Germany
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Rigshospitalet, DenmarkCompletedLimb-girdle Muscular DystrophyDenmark
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Assiut UniversityNot yet recruitingLimb-girdle Muscular Dystrophy
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Sarepta Therapeutics, Inc.RecruitingLimb-girdle Muscular DystrophyUnited States
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Rigshospitalet, DenmarkCompleted
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Sarepta Therapeutics, Inc.Active, not recruiting
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National Institute of Neurological Disorders and...TerminatedMyotonic Dystrophy Type-1 | Myotonic Dystrophy Type-2United States
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Cure CMDRecruitingEmery-Dreifuss Muscular Dystrophy | Congenital Myasthenic Syndrome | Limb-Girdle Muscular Dystrophy | Congenital Muscular Dystrophy With ITGA7 (Integrin Alpha-7) Deficiency | Alpha-Dystroglycanopathy (Congenital Muscular Dystrophy and Abnormal Glycosylation of Dystroglycan With Severe Epilepsy) and other conditionsUnited States
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Hope Biosciences Stem Cell Research FoundationHope BiosciencesNo longer availableCongenital Muscular Dystrophy Due to Lamin A/C MutationUnited States
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Cooperative International Neuromuscular Research...aTyr Pharma, Inc.; Muscular Dystrophy Canada; FSHD Global Research Foundation; FSH...CompletedFacioscapulohumeral Muscular DystrophyUnited States, Canada, Australia, Sweden, United Kingdom
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Istituto Ortopedico RizzoliCompletedBethlem Myopathy | Ullrich Congenital Muscular DystrophyItaly
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The Emmes Company, LLCJain Foundation; Coalition to Cure Calpain 3 (C3)Terminated
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Benitec Biopharma, Inc.RecruitingOculopharyngeal Muscular DystrophyUnited States
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University of FloridaCompleted
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Bioblast Pharma Ltd.WithdrawnOculopharyngeal Muscular DystrophyCanada
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Wake Forest University Health SciencesMuscular Dystrophy AssociationCompletedMuscular Dystrophies, Limb-Girdle (GENETICALLY CONFIRMED)United States
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University of CalgaryMuscular Dystrophy CanadaEnrolling by invitationMuscular Dystrophies | Oculopharyngeal Muscular Dystrophy | Myopathy; HereditaryCanada
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Mayo ClinicNational Eye Institute (NEI)CompletedRetinal Disease | Best Vitelliform Macular Dystrophy | Bestrophinopathy | Adult Onset Vitelliform Macular Dystrophy | Autosomal Dominant VitreoretinalchoroidopathyUnited States
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Asklepios Biopharmaceutical, Inc.RecruitingMuscular Dystrophy | Limb Girdle Muscular Dystrophy | LGMD2I | LGMD | Limb-Girdle Muscular Dystrophy Type 2 | LGMD2 | FKRP | FKRP Mutation | Fukutin Related ProteinUnited States
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BayerRegeneron PharmaceuticalsCompletedDiabetic Macular Edema (DME) | Age-related Macular Degeneration (AMD) | Central Retinal Vein Occlusion (CRVO)Canada
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Nationwide Children's HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedMuscular DystrophiesUnited States
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GenethonCompletedLimb Girdle Muscular Dystrophy Type 2C | Gamma-sarcoglycanopathyFrance
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Laval UniversityCompleted
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Radboud University Medical CenterSolve FSHDRecruitingMuscular Dystrophy, FacioscapulohumeralNetherlands
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Centre Hospitalier Universitaire de NiceCompletedMuscular Dystrophy, FacioscapulohumeralFrance
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Centre Hospitalier Universitaire de NiceCompletedMuscular Dystrophy, FacioscapulohumeralFrance
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Santhera PharmaceuticalsCompleted
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National Eye Institute (NEI)National Cancer Institute (NCI)RecruitingStargardt-Like Macular DystrophyUnited States
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Centre for Human Drug Research, NetherlandsFacio TherapeuticsCompleted
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Centre Hospitalier Universitaire de Saint EtienneAssociation Française contre les Myopathies (AFM), ParisCompletedMuscular Dystrophy, FacioscapulohumeralFrance
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Virginia Commonwealth UniversityRadboud University Medical Center; University of California, Los Angeles; University... and other collaboratorsRecruitingMyotonic Dystrophy 1United States, Netherlands, United Kingdom, New Zealand, Germany, Italy, Canada, France
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Vrije Universiteit BrusselCompletedMyotonic Dystrophy 1Belgium
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Élise DuchesneFondation du Grand défi Pierre LavoieCompletedMyotonic Dystrophy 1Canada
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Assistance Publique - Hôpitaux de ParisAssociation Française contre les Myopathies (AFM), ParisCompletedMuscular Dystrophy, OculopharyngealFrance
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University of RochesterCompletedMyotonic Muscular Dystrophy
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Hillel Yaffe Medical CenterUnknown
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Rigshospitalet, DenmarkRecruitingLimb Girdle Muscular DystrophyDenmark
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Ohio State UniversityCompletedMuscular Dystrophy, Facioscapulohumeral
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Superior UniversityActive, not recruitingTibial Muscular DystrophyPakistan
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IRCCS Eugenio MedeaRecruiting
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Oslo University HospitalUniversity of Oslo; Haukeland University HospitalRecruitingMyotonic Dystrophy 1Norway
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Université de SherbrookeRare Disease FoundationCompletedMyotonic Dystrophy 1Canada
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LMU KlinikumCompleted