- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Dystrophy
Total 1129 results
-
Oslo University HospitalUniversity of Oslo; Haukeland University HospitalRecruitingMyotonic Dystrophy 1Norway
-
Avidity Biosciences, Inc.Enrolling by invitationDuchenne Muscular Dystrophy | DMD | Exon 44 | DuchenneUnited States
-
Children's Hospital Medical Center, CincinnatiActive, not recruitingMusculoskeletal Abnormalities | Duchenne Muscular DystrophyUnited States
-
Université de SherbrookeRare Disease FoundationCompletedMyotonic Dystrophy 1Canada
-
Hacettepe UniversityCompletedDuchenne Muscular Dystrophy | Gait Disorders in ChildrenTurkey
-
LMU KlinikumCompleted
-
Bioblast Pharma Ltd.WithdrawnOculopharyngeal Muscular DystrophyCanada
-
National Human Genome Research Institute (NHGRI)TerminatedCommunication | Genetic DiseaseUnited States
-
Cynthia GagnonFondation du Grand défi Pierre LavoieCompletedEffects of a Multiple Component Training Program on Muscles in Adults With Myotonic Dystrophy Type 1Myotonic Dystrophy 1Canada
-
Spark TherapeuticsActive, not recruitingInherited Retinal Dystrophy Due to RPE65 Mutations
-
Peter WiedemannInstitut für Angewandte TrainingswissenschaftUnknownPseudophakic Bullous Keratopathy | Fuchs Endothelial Corneal Dystrophy | Chemical Burn of Cornea | Posterior Polymorphous Corneal DystrophyGermany
-
PepGen IncRecruitingMyotonic Dystrophy 1United States, Canada
-
Norwegian School of Sport SciencesUniversity of Oslo; Oslo University Hospital; University of Copenhagen; University... and other collaboratorsCompleted
-
Craig McDonald, MDCardero Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
-
Benha UniversityCompletedDuchenne Muscular Dystrophy | Inflammatory MyopathyEgypt
-
BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyUnited States, Netherlands, Belgium, Germany, Argentina, Brazil, France, Italy, Sweden, Turkey
-
Pixium Vision SACompletedRetinitis Pigmentosa | Choroideremia | Cone Rod DystrophyAustria, France, Germany
-
University Hospital, BonnForschungszentrum Juelich; The Marigold Foundation; Life and Brain Center BonnCompletedMyotonic Dystrophy 1 | Myotonic Dystrophy 2
-
Shriners Hospitals for ChildrenCompletedDuchenne Muscular DystrophyUnited States
-
Vertex Pharmaceuticals IncorporatedRecruitingMyotonic Dystrophy Type 1 (DM1)Canada
-
Dyne TherapeuticsRecruitingMyotonic Dystrophy Type 1 (DM1)United Kingdom, France, Netherlands, Italy, Germany, New Zealand
-
The Emmes Company, LLCJain Foundation; Coalition to Cure Calpain 3 (C3)Terminated
-
Hacettepe UniversityCompletedDuchenne Muscular Dystrophy | Upper Limb Function | Respiratory Function Test
-
University of OsloOslo University Hospital; Vikersund Rehabilitation CenterRecruitingMyotonic Dystrophy Type 1 (DM1)Norway
-
Virginia Commonwealth UniversityRecruitingCongenital Myotonic Dystrophy | Childhood Myotonic Dystrophy | CDM | CHDMUnited States, Italy
-
Expansion Therapeutics, Inc.CompletedMyotonic Dystrophy | Myotonic Dystrophy, Type 1 (DM1)United States
-
Children's Hospital of Eastern OntarioJesse's Journey-The Foundation for Gene and Cell TherapyCompletedDuchenne Muscular DystrophyCanada
-
Monica Levy AndersenCompletedOther Diseases or ConditionsBrazil
-
PTC TherapeuticsMuscular Dystrophy AssociationCompletedDuchenne Muscular DystrophyUnited States
-
Centre Hospitalier Universitaire de Saint EtienneKyoto University, Graduate School of MedicineNot yet recruitingCorneal DystrophiesFrance
-
Université du Québec à ChicoutimiRecruitingMyotonic Dystrophy Type 1 (DM1)Canada
-
Sahra ŞirvanEnrolling by invitationDuchenne Muscular DystrophyTurkey
-
PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular DystrophyUnited States
-
University Hospital, ToulouseUnknownDuchenne Muscular DystrophyFrance
-
Hacettepe UniversityCompletedDuchenne Muscular DystrophyTurkey
-
Oslo University HospitalUniversity Hospital of North Norway; The Research Council of NorwayCompletedDuchenne Muscular DystrophyNorway
-
LMU KlinikumCompletedHealthy | Myotonic Dystrophy Type 2 | Pompe Disease (Late-onset) | Spinal Muscular Atrophy Type 3 | Myotonic Dystrophy Type 1 (DM1) | Facioscapulohumeral Muscular Dystrophy 1 | Inclusion Body Myositis, SporadicGermany
-
Lupin Ltd.WithdrawnMyotonic Dystrophy Type 1 and Type 2
-
University of CalgaryMuscular Dystrophy CanadaEnrolling by invitationMuscular Dystrophies | Oculopharyngeal Muscular Dystrophy | Myopathy; HereditaryCanada
-
University Hospital, MontpellierRecruitingPrimary Disease Fascioscapulohumeral Dystrophy (FSHD)France
-
Peking University Third HospitalRecruitingBietti's Crystalline DystrophyChina
-
Astellas Institute for Regenerative MedicineCompletedStargardt's Macular DystrophyUnited States
-
Astellas Institute for Regenerative MedicineCompletedStargardt's Macular DystrophyUnited States
-
Tissue Tech Inc.CompletedCorneal Dystrophy, Epithelial Basement MembraneUnited States
-
Retina Implant AGTerminatedRetinal Degeneration | Inherited Retinal Dystrophy Primarily Involving Sensory RetinaFrance
-
Klinikum Chemnitz gGmbHGerman Research Foundation; KKS NetzwerkUnknownPseudophakic Bullous Keratopathy | Fuch's Endothelial DystrophyGermany
-
Hacettepe UniversityCompletedDuchenne Muscular Dystrophy | Muscle Strength | Hamstring Contractures | Lower ExtremityTurkey
-
Charite University, Berlin, GermanyRecruitingVarious Forms of Skeletal Muscle DystrophyGermany
-
University Hospital, MontpellierTerminatedPrimary Disease Facioscapulohumeral Dystrophy (FSHD)France
-
PTC TherapeuticsEnrolling by invitationDuchenne Muscular DystrophyUnited States, Canada