- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on EPS
Total 213 results
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Ultragenyx Pharmaceutical IncCompletedMucopolysaccharidosis | Sly Syndrome | Mucopolysaccharidosis VII | MPS VIIUnited States, Brazil, Mexico, Portugal
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VA Office of Research and DevelopmentUniversity of WashingtonActive, not recruiting
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University of Colorado, DenverCompletedCerebral Palsy | Pes PlanusUnited States
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Alexion PharmaceuticalsCompletedMPS IIIB (Sanfilippo Syndrome)Spain, Netherlands, United Kingdom, United States, Brazil
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BioMarin PharmaceuticalApproved for marketingMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVAUnited States, Puerto Rico
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AbbVieWithdrawn
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University of Alabama at BirminghamPorphyria Rare Disease Clinical Research ConsortiumCompletedErythropoietic Protoporphyria (EPP)United States
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Icahn School of Medicine at Mount SinaiNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Rare... and other collaboratorsCompletedErythropoietic Protoporphyria | EPP | XLP | X-Linked Protoporphyria | XLPP | X-Linked Dominant Erythropoietic Protoporphyria | XLEPP | XLDPUnited States
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Calliditas Therapeutics ABCompletedPost Polio Syndrome, PPSSweden
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Uskudar UniversityCompletedCerebral Palsy | Pes PlanusTurkey
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Emory UniversityBioMarin PharmaceuticalCompletedMPS - Mucopolysaccharidosis | Morquio DiseaseUnited States
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BioMarin PharmaceuticalTerminatedMorquio A Syndrome | MPS IV A | Mucopolysaccharidosis IVAUnited Kingdom
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Italian Sarcoma GroupCompleted
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Huazhong University of Science and TechnologyNot yet recruitingAdvanced or Metastatic EP-NECChina
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BioMarin PharmaceuticalTerminatedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVAUnited States, United Kingdom, Canada, Germany
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Orchard TherapeuticsRecruitingMPS-IH (Hurler Syndrome)Netherlands, United States, Italy, United Kingdom
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CerecareCompletedEds, Unspecified TypeFrance
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Alexion PharmaceuticalsTerminatedMPS IIIB (Sanfilippo B Syndrome)Spain, United States, Brazil, United Kingdom, Portugal, Italy
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BioMarin PharmaceuticalCompletedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVATaiwan, United States, Italy, United Kingdom
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BioMarin PharmaceuticalICON plcCompletedMucopolysaccharidosis IV Type A | Morquio A Syndrome | MPS IVAUnited States, United Kingdom, Australia, Taiwan, Belgium, Malaysia, Austria, Canada, Portugal, France, Ireland, Czechia, Denmark, Italy, Netherlands, Poland, Puerto Rico
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BioMarin PharmaceuticalTerminatedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVAUnited Kingdom, United States, Germany
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REGENXBIO Inc.Active, not recruitingHurler Syndrome | Hurler-Scheie Syndrome | Mucopolysaccharidosis Type I (MPS I)United States, Brazil, Israel
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BioMarin PharmaceuticalCompletedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IV AUnited States, Canada, France, Taiwan, Argentina, Colombia, Spain, Turkey, Japan, Saudi Arabia, Netherlands, Denmark, Korea, Republic of, Brazil, United Kingdom, Germany, Norway, Portugal, Italy, Qatar
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ShireTerminatedMucopolysaccharidosis (MPS)United States, Canada, United Kingdom, Turkey, Italy, Mexico, Spain
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Nemours Children's ClinicEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingMucopolysaccharidosis IV Type A | Morquio A Syndrome | MPS IVAUnited States
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Janssen Research & Development, LLCCompletedErythroblastosis, Fetal | Early Onset Severe Hemolytic Disease of the Fetus and Newborn (EOS-HDFN)United States, Canada, Netherlands, Belgium, Australia, Germany, Spain, Sweden, United Kingdom
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University Health Network, TorontoEnrolling by invitationEhlers-Danlos Syndrome | Hypermobile EDS (hEDS) | Classical Ehlers-Danlos SyndromeCanada
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Afyonkarahisar Health Sciences UniversityCompletedSpondylitis, Ankylosing | Pes Planus | Posterior Tibial Tendon DysfunctionTurkey
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BioMarin PharmaceuticalTerminatedMorquio A Syndrome | MPS IV A | Mucopolysaccharidosis IVAFrance, United Kingdom, Taiwan, United States, Argentina, Netherlands, Canada, Brazil, Germany, Italy
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Sangamo TherapeuticsTerminatedMucopolysaccharidosis II | MPS IIUnited States
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TakedaCompletedMucopolysaccharidosis (MPS)Brazil
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Hansoh BioMedical R&D CompanyWithdrawnExtensive Stage Small Cell Lung Cancer (ES-SCLC)
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Duke UniversityRecruiting
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Talaris Therapeutics Inc.Duke UniversityTerminatedNiemann-Pick Disease | Alpha-mannosidosis | Tay Sachs Disease | Sandhoff Disease | Metachromatic Leukodystrophy (MLD) | Hurler-Scheie Syndrome | Hurler Syndrome (MPS I) | Hunter Syndrome (MPS II) | Sanfilippo Syndrome (MPS III) | Krabbe Disease (Globoid Leukodystrophy) | Adrenoleukodystrophy (ALD and AMN) | Pelizaeus...United States
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REGENXBIO Inc.Active, not recruitingMucopolysaccharidosis Type II (MPS II)United States, Brazil
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ShireCompletedHunter Syndrome | Mucopolysaccharidosis (MPS)United States, Argentina, Mexico, Spain, United Kingdom
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National Cancer Institute (NCI)WithdrawnMultiple Myeloma | Non-Hodgkin Lymphoma | Acute Leukemias | Chronic Myelogous Leukemia/Other Leukemia | MDS/MPS
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TakedaTakeda Development Center Americas, Inc.RecruitingHunter Syndrome | Mucopolysaccharidosis (MPS)United States
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SanofiCompletedPompe Disease | Mucopolysaccharidosis Type I (MPS I)Italy
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REGENXBIO Inc.Active, not recruitingMucopolysaccharidosis Type II (MPS II)United States, Canada
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ShireCovance; PRA Health Sciences; PharmaNetCompletedMucopolysaccharidosis II | Hunter Syndrome | MPS IIBrazil, Poland, Taiwan
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IGC Pharma LLCRecruitingAggression | Depression | Anxiety | Alzheimer Disease | Memory Impairment | Agitated; State, Acute Reaction to Stress | Agitation,Psychomotor | Care Giving Burden | NPS | Aggressive OutburstUnited States, Canada, Puerto Rico
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University Health Network, TorontoRecruitingHypermobile EDS (hEDS) | Hypermobility SyndromeCanada
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Wills EyeCenters for Disease Control and Prevention; Westat; Public Health Management... and other collaboratorsCompletedOcular Hypertension | Glaucoma | Macular Degeneration | Diabetic Retinopathy | Central Retinal Vein Occlusion | Cataract | Branch Retinal Vein Occlusion | Glaucoma Suspect | Central Retinal Artery Occlusion | Drusen | Branch Retinal Arterial Occlusion | Epi-retinal Membrane | Loss of VisionUnited States
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Universitätsmedizin MannheimUnknownVentricular Fibrillation | Ventricular Tachycardia | Sudden Cardiac Death | Coronary Angiography | Catheter Ablation | Percutaneous Coronary Intervention (PCI) | Electrophysiologic Testing (EP) | Internal Cardioverter Defibrillator (ICD)Germany
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ShireCompletedHunter Syndrome | Mucopolysaccharidosis II (MPS II)United States, France, United Kingdom, Germany, Sweden, Spain, Brazil, Canada, Italy, Romania
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National Human Genome Research Institute (NHGRI)RecruitingHermansky-Pudlak Syndrome (HPS)United States
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Kyowa Kirin, Inc.CompletedTumor Induced Osteomalacia (TIO) | Epidermal Nevus Syndrome (ENS)United States
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National Human Genome Research Institute (NHGRI)RecruitingPulmonary Fibrosis | Healthy Volunteers | Hermansky-Pudlak Syndrome (HPS)United States
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National Human Genome Research Institute (NHGRI)TerminatedPulmonary Fibrosis | Metabolic Disease | Oculocutaneous Albinism | Hermansky-Pudlak Syndrome (HPS) | Platelet Storage Pool DeficiencyUnited States