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Clinical Trials on Early-onset Cerebellar Ataxias
Total 410 results
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Hospices Civils de LyonRecruiting
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Samsung Medical CenterCompletedSpinocerebellar Ataxias | Multiple System Atrophy, Cerebellar Variant (Disorder)Korea, Republic of
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Centre Hospitalier Universitaire de NīmesCompletedCerebellar AtaxiaFrance
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Children's Hospital of Orange CountyActive, not recruitingNeuronal Ceroid-Lipofuscinoses | Neuronal Ceroid Lipofuscinosis CLN2 | Spinocerebellar Ataxia, Autosomal Recessive 7United States
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University of PlymouthRecruitingAtaxia Telangiectasia | Ataxia Telangiectasia in ChildrenUnited Kingdom
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IntraBio IncRecruitingAtaxia Telangiectasia | Louis Bar SyndromeSpain, United States, Germany, United Kingdom
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Radboud University Medical CenterA-T Children's Project; Twan foundation (https://twanfoundation.nl)CompletedAtaxia Telangiectasia | ATM Gene MutationNetherlands
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Federal Research Institute of Pediatric Hematology...CompletedAtaxia Telangiectasia | DysmetriaRussian Federation
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Hospices Civils de LyonRecruitingGAD-receptor Antibodies-associated EncephalitisFrance
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Université du Québec à ChicoutimiMcGill University; Université de Sherbrooke; University of Alberta; University... and other collaboratorsRecruitingAutosomal Recessive Spastic Ataxia of Charlevoix-Saguenay | Spastic Paraplegia 7Canada
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Cairo UniversityCompletedCerebellar AtaxiaEgypt
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Weill Medical College of Cornell UniversityJohns Hopkins University; Mayo Clinic; National Heart, Lung, and Blood Institute... and other collaboratorsRecruiting
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Dr. Rebecca SchuleGerman Research Foundation; German Center for Neurodegenerative Diseases (DZNE)RecruitingSpastic AtaxiaCanada, France, Germany, Italy, Netherlands, Turkey, United Kingdom
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Quince Therapeutics S.p.A.CompletedGenetic Syndrome | Nervous System DiseaseIndia, United States, Australia, Germany, Italy, Norway, Poland, Spain, Tunisia, United Kingdom, Israel, Belgium
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Centre Hospitalier Universitaire de NīmesCompletedNeurodegenerative Diseases | Cerebellar Ataxia | NeuropathyFrance
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Oregon Health and Science UniversityPortland VA Medical CenterTerminatedAtaxia | Essential Tremor | Cerebellar Diseases | Deep Brain StimulationUnited States
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Johann Wolfgang Goethe University HospitalUnknownAtaxia TelangiectasiaGermany
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Johann Wolfgang Goethe University HospitalUnknownGrowth Failure | Ataxia TelangiectasiaGermany
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Johns Hopkins UniversityVirginia Polytechnic Institute and State University; Johns Hopkins Discovery...Completed
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Sheba Medical CenterCompletedFatigue | Ataxia | Dystonia | Parkinsonism | ChoreaIsrael
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Azienda Socio Sanitaria Territoriale degli Spedali...CompletedAtaxia | Multiple System Atrophy | Spinocerebellar Ataxias | Ataxia With Oculomotor Apraxia | CANVASItaly
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Rabin Medical CenterInternational BFM Study Group; Israeli Society for Pediatric Hematology-OncologyRecruitingLymphoma | Leukemia | Ataxia TelangiectasiaIsrael
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University of Sao Paulo General HospitalUnknownCerebellar AtaxiaBrazil
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S. Andrea HospitalAgenzia Italiana del FarmacoCompleted
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Nantes University HospitalUniversity Hospital, Angers; University Hospital, Bordeaux; Poitiers University... and other collaboratorsCompletedEarly-onset Neonatal InfectionFrance
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Shenzhen Beike Bio-Technology Co., Ltd.The Affiliated Nanjing Drum Tower Hospital of Nanjing University Medical... and other collaboratorsUnknown
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Hugo W. Moser Research Institute at Kennedy Krieger...RecruitingLeukoencephalopathies | Genetic Disease | White Matter Disease | Ataxia, Cerebellar | LBSL | Leukoencephalopathy With Brainstem and Spinal Cord Involvement and Lactate ElevationUnited States
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Institut National de la Santé Et de la Recherche...Not yet recruiting
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PTC TherapeuticsEnrolling by invitationFriedreich AtaxiaUnited States, Australia, Brazil, Canada, France, Germany, Italy, New Zealand, Spain
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PTC TherapeuticsActive, not recruitingFriedreich AtaxiaUnited States
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PTC TherapeuticsCompletedFriedreich AtaxiaUnited States, Australia, Brazil, Canada, France, Germany, Italy, New Zealand, Spain
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Children's Hospital of PhiladelphiaFriedreich's Ataxia Research Alliance; Stealth BioTherapeutics Inc.Active, not recruitingFriedreich AtaxiaUnited States
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Metro International Biotech, LLCChildren's Hospital of PhiladelphiaCompleted
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Santhera PharmaceuticalsCompletedFriedreich's AtaxiaUnited States
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Design TherapeuticsCompleted
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Minoryx Therapeutics, S.L.CompletedFriedreich AtaxiaSpain, Belgium, France, Germany
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Larimar Therapeutics, Inc.Veristat, Inc.; Metrum Research Group, LLCCompletedFriedreich AtaxiaUnited States
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ShireCompletedFriedreich's AtaxiaUnited States
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National Institute of Neurological Disorders and...Completed
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University of South FloridaFriedreich's Ataxia Research Alliance; Edison Pharmaceuticals IncCompleted
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University of South FloridaUnknownFriedreich's AtaxiaUnited States
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Penwest Pharmaceuticals Co.CompletedFriedreich's AtaxiaUnited States
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Federico II UniversityCompleted
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National Institute of Neurological Disorders and...Completed
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Santhera PharmaceuticalsCompletedFreidreich's AtaxiaGermany, Netherlands, France, Austria, Belgium
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Fondation Ophtalmologique Adolphe de RothschildTerminatedChoroidal NeovascularizationFrance
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Rutgers, The State University of New JerseyRecruitingParkinson Disease | Movement Disorders | Huntington Disease | Essential Tremor | Spinocerebellar Ataxias | Dystonia, PrimaryUnited States
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Second Affiliated Hospital, School of Medicine,...Recruiting
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BiogenNot yet recruiting
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University of FloridaNational Institutes of Health (NIH); National Center for Advancing Translational... and other collaboratorsRecruiting