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Clinical Trials on Epidermolysis Bullosa Dystrophica in United States
Total 670 results
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Edgewise Therapeutics, Inc.CompletedNervous System Diseases | Genetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Healthy VolunteerUnited States
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Santhera PharmaceuticalsCompleted
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National Human Genome Research Institute (NHGRI)National Center for Advancing Translational Sciences (NCATS)Completed
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Cornea Associates of TexasCompletedKeratoconus | Corneal Ectasia | Pellucid Marginal Corneal Degeneration | Corneal DegenerationUnited States
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Duke UniversityCompleted
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Cornea Associates of TexasActive, not recruitingKeratoconus | Corneal Ectasia | Pellucid Marginal Corneal Degeneration | Corneal DegenerationUnited States
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Retina Foundation of the SouthwestCompletedRetinitis Pigmentosa | AMDUnited States
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The Cleveland ClinicNational Eye Institute (NEI)CompletedRetinal Detachment | Epiretinal Membrane | Fuchs Endothelial Dystrophy | Macular HoleUnited States
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Beacon TherapeuticsRecruitingX-Linked Retinitis PigmentosaUnited States
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National Eye Institute (NEI)RecruitingRetinal Degeneration | Stargardt Disease | ABCA4 Retinopathy | Retinal DystrophyUnited States
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Applied Genetic Technologies CorpCompletedX-Linked Retinitis PigmentosaUnited States
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National Eye Institute (NEI)CompletedCorneal Dystrophies, Hereditary | Corneal DiseaseUnited States, China, Italy
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Nationwide Children's HospitalRecruiting
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Massachusetts Eye and Ear InfirmaryRecruitingFuchs' Endothelial Corneal DystrophyUnited States
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National Human Genome Research Institute (NHGRI)CompletedHereditary Inclusion Body MyopathyUnited States
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Radtke, Norman D., M.D.Foundation Fighting BlindnessCompletedRetinitis Pigmentosa.United States
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Adam Fedyk, MD, FACSAlcon ResearchRecruitingCataract | Fuchs DystrophyUnited States
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Janssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaUnited States, United Kingdom
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SparingVisionActive, not recruitingRetinitis PigmentosaUnited States, France
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PTC TherapeuticsTerminatedLimb-Girdle Muscular DystrophyUnited States, Norway, Canada, Sweden, Russian Federation, Denmark, France, Germany
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Children's National Research InstituteActive, not recruitingGenetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Dystrophies | Cardiac FibrosisUnited States
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Editas Medicine, Inc.Active, not recruitingRetinal Degeneration | Eye Diseases, Hereditary | Vision Disorders | Leber Congenital Amaurosis 10 | Inherited Retinal Dystrophies | Retinal Disease | Eye Disorders CongenitalUnited States
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Massachusetts General HospitalHarvard Medical School (HMS and HSDM)RecruitingKeratoconus | Ectasia | Fuchs' Endothelial Dystrophy | CrosslinkingUnited States
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Hugo W. Moser Research Institute at Kennedy Krieger...Active, not recruitingFacioscapulohumeral Muscular DystrophyUnited States
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BiogenCompletedX-Linked Retinitis PigmentosaUnited States, United Kingdom
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Stealth BioTherapeutics Inc.CompletedFuchs' Corneal Endothelial Dystrophy (FCED)United States
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National Human Genome Research Institute (NHGRI)Therapeutics for Rare and Neglected Diseases (TRND)RecruitingGNE Myopathy | GNE Related DiseasesUnited States
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Eunice Kennedy Shriver National Institute of Child...National Institutes of Health Clinical Center (CC); National Institute of Neurological... and other collaboratorsActive, not recruitingGenetic DisorderUnited States
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National Eye Institute (NEI)Bausch & Lomb Incorporated; Eye Bank Association of America; Midwest Eye Banks; Tissue Banks International and other collaboratorsCompletedCorneal Disease | Fuch's Dystrophy | Pseudophakic Corneal EdemaUnited States
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AbbVieActive, not recruitingAdvanced Retinitis PigmentosaUnited States
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Stanford UniversityUniversity of Pennsylvania; University of California, Davis; Oregon Health and... and other collaboratorsRecruitingFuchs' Endothelial Dystrophy | Fuchs Dystrophy | FuchsUnited States
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Case Western Reserve UniversityNational Eye Institute (NEI); Jaeb Center for Health ResearchRecruitingFuchs' Endothelial Dystrophy | Corneal Endothelial DecompensationUnited States
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Second Sight Medical ProductsNational Eye Institute (NEI)CompletedRetinitis PigmentosaUnited States, United Kingdom, France, Mexico, Switzerland
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University of OxfordCompletedAge-related Macular Degeneration | Retinitis Pigmentosa | Inherited Retinal Dystrophies | Optic Nerve PathologyUnited Kingdom
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University of RochesterCompletedFacioscapulohumeral Muscular DystrophyUnited States
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National Institute of Arthritis and Musculoskeletal...CompletedIchthyosis | Ichthyosis, X-Linked | Ichthyosis, Lamellar | Darier Disease | Hailey-Hailey Disease | Hyperkeratosis, Epidermolytic | KeratodermaUnited States
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Prothelia, Inc.Cure CMD; The Bönnemann Laboratory, NINDS, National Institutes of Health; Oscar... and other collaboratorsCompletedMerosin Deficient Congenital Muscular DystrophyUnited States
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Retina Foundation of the SouthwestDSM Nutritional Products, Inc.; Foundation Fighting BlindnessCompletedRetinitis Pigmentosa | X-linked Genetic DiseasesUnited States
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Oxford University Hospitals NHS TrustRecruitingRetinal Degeneration | Retinal Dystrophies | Retinal DiseaseUnited Kingdom
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Foundation Fighting BlindnessUnited States Department of DefenseCompleted
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Hugo W. Moser Research Institute at Kennedy Krieger...Concord Hospital; FSHD Global Research FoundationCompletedFacioscapulohumeral Muscular DystrophyUnited States, Australia
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Retina Institute of HawaiiCompletedRetinal Diseases | Retinitis Pigmentosa | Stargardt's DiseaseUnited States
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.Not yet recruiting
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The Emmes Company, LLCUltragenyx Pharmaceutical Inc; Parent Project Muscular Dystrophy; Department...RecruitingDuchenne Muscular DystrophyUnited States
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National Institute of Neurological Disorders and...RecruitingMuscular Dystrophy | Peripheral Neuropathy | Normal Physiology | Motor Neuron DisorderUnited States
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Massachusetts General HospitalBoston Children's HospitalRecruitingDuchenne Muscular DystrophyUnited States
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University of PittsburghRecruitingDuchenne Muscular DystrophyUnited States
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Jerry R. MendellDuchenne Alliance; Milo TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
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Cure Rare Disease, IncUniversity of Massachusetts, WorcesterActive, not recruiting