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Clinical Trials on Factor VIII Deficiency, Congenital
Total 542 results
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National Center for Research Resources (NCRR)University of California, San DiegoCompletedFanconi Syndrome | Cystinosis
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Indiana UniversityChildren's Hospital Medical Center, Cincinnati; Makerere University; Doris Duke... and other collaboratorsCompletedMalaria | Sickle Cell Disease | Sickle Cell AnemiaUganda
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Novartis PharmaceuticalsCompletedMyelodysplastic Syndromes | Fanconi Syndrome | Anemia, Aplastic | Beta-thalassemia | Anemia, Diamond-BlackfanUnited States
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Cairo UniversityActive, not recruitingMaxillofacial Abnormalities | Skeletal Malocclusion | Mandible PrognathismEgypt
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Rambam Health Care CampusRecruitingBronchiectasis | Cystic Fibrosis | Bronchiolitis Obliterans | Primary Ciliary Dyskinesia | Primary Immune DeficiencyIsrael
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Indiana UniversityChildren's Hospital Medical Center, Cincinnati; Makerere University; Doris Duke... and other collaboratorsCompletedMalaria | Sickle Cell Disease | Sickle Cell AnemiaUganda
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University Hospital, ToulouseCompletedPrader-Willi Syndrome | Growth Hormone DeficiencyFrance
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Direction Centrale du Service de Santé des ArméesUnknownKaposi's DiseaseFrance
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Children's Hospital Los AngelesGenentech, Inc.CompletedGrowth Hormone Deficiency | Hypopituitarism | Septo-Optic DysplasiaUnited States
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Liverpool School of Tropical MedicineUniversity of Bergen; Indiana University; Makerere University; University of Malawi and other collaboratorsCompletedMalaria | Sickle Cell Anemia in ChildrenUganda, Malawi
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Hospital Infantil Universitario Niño Jesús, Madrid...Universitat Autonoma de Barcelona; Instituto de Investigación Sanitaria de... and other collaboratorsCompletedFanconi AnemiaSpain
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Cystinosis Research FoundationUnknownCystinosis | Nephropathic Cystinosis | Renal Fanconi SyndromeUnited States
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Laboratoire français de Fractionnement et de BiotechnologiesNo longer availableSurgery | Postpartum Hemorrhage | Wound; Rupture, Surgery, Cesarean SectionUnited States
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Porteus, Matthew, MDRecruiting
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National Heart, Lung, and Blood Institute (NHLBI)Recruiting
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Sanguine BiosciencesTerminated
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Children's Hospital Medical Center, CincinnatiFood and Drug Administration (FDA)Completed
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Fred Hutchinson Cancer CenterNational Heart, Lung, and Blood Institute (NHLBI); Rocket Pharma LimitedActive, not recruiting
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OHSU Knight Cancer InstituteNational Cancer Institute (NCI)CompletedUnspecified Childhood Solid Tumor, Protocol Specific | Unspecified Adult Solid Tumor, Protocol Specific | Fanconi AnemiaUnited States
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Novo Nordisk A/SCompletedHealthy | Congenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Acquired Bleeding Disorder | Acquired Haemophilia | Congenital FVII Deficiency | Glanzmann's DiseaseFrance
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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Foresee Pharmaceuticals Co., Ltd.Recruiting
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Rigshospitalet, DenmarkCompletedSpinal Muscular Atrophy | Merosin Deficient Congenital Muscular DystrophyDenmark
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Clinuvel Europe LimitedRecruitingXeroderma PigmentosumBelgium, Spain
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Guy's and St Thomas' NHS Foundation TrustKing's College London; Newcastle University; University of CambridgeCompletedXeroderma PigmentosumUnited Kingdom
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Clinuvel Europe LimitedRecruitingXeroderma PigmentosumGermany
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Walter Reed Army Institute of Research (WRAIR)CompletedGlucosephosphate Dehydrogenase Deficiency | FavismUnited States
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Duke UniversityNational Heart, Lung, and Blood Institute (NHLBI)Completed
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Fran AweekaCompletedHIV Infections | MalariaUnited States
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Inozyme PharmaGACI GlobalNot yet recruitingATP-Binding Cassette Subfamily C Member 6 Deficiency | Ectonucleotide Pyrophosphatase/Phosphodiesterase 1 Deficiency
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Indiana UniversityCompletedAutosomal Dominant Hypophosphatemic RicketsUnited States
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Sanaria Inc.Centre de Recherche Médicale de Lambaréné; Institute of Tropical Medicine,...CompletedMalaria | Plasmodium Falciparum MalariaGabon
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Children's Hospital Medical Center, CincinnatiRecruiting
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Rocket Pharmaceuticals Inc.Active, not recruitingFanconi Anemia Complementation Group AUnited States
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Rolfs Consulting und Verwaltungs-GmbH (RCV)Rhythm Pharmaceuticals, Inc.RecruitingCognitive Impairment | Hyperphagia | Obesity, Childhood | Bardet-Biedl Syndrome | Polydactyly | Retinopathy | Syndactyly | POMC DeficiencyGermany
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Zhizheng GeWithdrawnGastrointestinal Bleeding of Unknown Origin | Gastrointestinal Vascular Malformation | Thalidomide EfficiencyChina
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University of RochesterRecruitingLymphoma | Myelodysplastic Syndromes | Multiple Myeloma | Solid Tumor | Acute Leukemia | Aplastic Anemia | Chronic Leukemia | Immune Deficiency Disorder | Congenital Hematological Disorder | Metabolism DisorderUnited States
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Dong-A ST Co., Ltd.RecruitingGrowth Hormone Deficiency | Turner Syndrome | Small for Gestational Age | Idiopathic Short StatureKorea, Republic of
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Gilead SciencesCompletedHIV Infections | Renal Impairment | Fanconi Syndrome | Kidney DiseaseCanada, United States
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Merck KGaA, Darmstadt, GermanyCompletedGrowth Hormone Deficiency | Chronic Renal Failure | Turner Syndrome | Small for Gestational Age
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Stanford UniversityNot yet recruitingLiver Failure | Liver Cirrhosis | Hemophilia A | Hemophilia B | Hemophilia | Liver Transplant Disorder | Coagulation Factor DeficiencyUnited States
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Vastra Gotaland RegionOctapharmaWithdrawn
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National Cancer Institute (NCI)RecruitingFanconi Anemia | Dyskeratosis Congenita | Diamond Blackfan Anemia | Shwachman Diamond Syndrome | Inherited Bone Marrow Failure Syndrome, Aplastic AnemiaUnited States
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Massachusetts General HospitalAgios Pharmaceuticals, Inc.RecruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | Myeloproliferative Neoplasm | Myelodysplastic/Myeloproliferative Neoplasm | Clonal Cytopenia of Undetermined Significance | Pyruvate Kinase Deficiency | Pyruvate Kinase Deficiency Anemia | Hereditary Hemolytic Anemia | Clonal Myeloid Neoplasm | Other... and other conditionsUnited States
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Yonsei UniversityCompletedMandibular Retrognathism | Mandibular PrognathismKorea, Republic of
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University Hospital, Strasbourg, FranceRecruiting
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Massachusetts General HospitalCompletedKallmann Syndrome | Idiopathic Hypogonadotropic Hypogonadism | GnRH DeficiencyUnited States
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Applied GeneticsUnknownPrecancerous ConditionUnited States, Germany, United Kingdom