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Clinical Trials on Factor VIII Deficiency, Congenital
Total 543 results
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OctapharmaCompletedCongenital Fibrinogen DeficiencyIndia, Iran, Islamic Republic of, Lebanon
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University of PadovaCompletedCoronary Microvascular Disease | Factor XIII Deficiency | ST-Elevation Myocardial Infarction | Myocardial HaemorrhageItaly
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CSL BehringCompletedCongenital Fibrinogen DeficiencyUnited States, Canada
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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Bio Products LaboratoryCompletedFactor X DeficiencyUnited Kingdom
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Sheba Medical CenterUnknown
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Wageningen UniversityUniversity of California, Davis; Penn State University; University of Ibadan; Newcastle... and other collaboratorsCompletedInflammation | Malaria | Vitamin A DeficiencyNigeria
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Arbor Research Collaborative for HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Active, not recruitingPortal Hypertension | Cholestasis | Liver Fibrosis | Biliary Atresia | Alagille Syndrome | Alpha1 Anti-Trypsin DeficiencyUnited States, Canada
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Weibing TangRecruitingConstipation | Hirschsprung Disease | Incontinence | Risk Factor | Bowel DysfunctionChina
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Gary M Brittenham, MDActive, not recruitingRespiratory Tract Infections | Respiratory Tract Diseases | Respiration Disorders | Lung Diseases | Nutrition Disorders | Vitamin D Deficiency | Asthma | Sickle Cell Disease | Anemia, Sickle Cell | Anemia, Hemolytic, Congenital | Acute Chest Syndrome | Deficiency Diseases VitaminUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencyUnited States, Israel, Austria, Spain, Switzerland, Germany, Canada, France, United Kingdom, Italy, Finland
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University of ThessalyNot yet recruiting
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PATHFundação de Medicina Tropical Dr. Heitor Vieira DouradoCompleted
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Columbia UniversityNew York Blood CenterCompleted
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University of ThessalyCompleted
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University of North Carolina, Chapel HillCompletedDevelopmental Cochlear Nerve Deficiency | Acquired Cochlear Nerve Deficiency | Cochlear Aplasia | Post-meningitis Cochlear Ossification | Cochlear MalformationUnited States
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PATHFred Hutchinson Cancer CenterCompletedG6PD DeficiencyUnited States
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PATHCompletedG6PD DeficiencyUnited States
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Baebies, Inc.CompletedG6PD Deficiency | G6PDUnited States
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National Center for Research Resources (NCRR)Completed
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University of L'AquilaUnknownVon Willebrand Disease | Congenital Coagulation Factors Deficiency | Haemophilia CarriersItaly
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Hospices Civils de LyonCompletedVitamin D Deficiency | Sickle Cell DiseaseFrance
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Masonic Cancer Center, University of MinnesotaRecruitingMyelodysplastic Syndromes | Fanconi Anemia | Dyskeratosis Congenita | Severe Aplastic Anemia | Bone Marrow Failure | T Cell Receptor Alpha/Beta Depletion | Telomere Biology DisorderUnited States
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OctapharmaCompletedCongenital Fibrinogen DeficiencyUnited States, Bulgaria, India, Iran, Islamic Republic of, Lebanon, Russian Federation, Saudi Arabia, Turkey, United Kingdom
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University of Mississippi, OxfordUniversity of Colorado, Denver; Southern Research InstituteUnknown
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DBL -Institute for Health Research and DevelopmentCompletedMalaria | Iron Deficiency | Anaemia | Schistosomiasis InfectionKenya
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University of North Carolina, Chapel HillThe Hospital for Sick Children; Washington University School of Medicine; McGill... and other collaboratorsRecruitingPrimary Ciliary Dyskinesia | Kartagener Syndrome | Primary Immune DeficiencyUnited States, Canada
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Damascus UniversityCompletedClass III Malocclusion in Growing PatientsSyrian Arab Republic
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HaEmek Medical Center, IsraelUnknownIron Deficiency | ThalassemiaIsrael
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Assistance Publique - Hôpitaux de ParisUnknownAdrenal Hyperplasia, Congenital | 21-hydroxylase DeficiencyFrance
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Arbor Research Collaborative for HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)SuspendedLiver Diseases | Alpha 1-Antitrypsin Deficiency | Alagille SyndromeUnited States, Canada
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University of North Carolina, Chapel HillThe Hospital for Sick Children; Washington University School of Medicine; McGill... and other collaboratorsRecruitingPrimary Ciliary Dyskinesia | Kartagener Syndrome | Primary Immune DeficiencyUnited States, Canada
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Grace Science, LLCRecruitingNGLY1 DeficiencyUnited States
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St. Jude Children's Research HospitalBaylor College of Medicine; Children's Hospital of Philadelphia; Dana-Farber... and other collaboratorsRecruitingMyelodysplastic Syndromes | Sickle Cell Disease | Fanconi Anemia | Severe Congenital Neutropenia | Bone Marrow Failure Syndromes | Blood Coagulation Disorder | Erythrocyte Disorder | Leukocyte Disorder | Hemostasis | Dyskeratosis Congenita | Diamond-Blackfan Anemia | Congenital Thrombocytopenia | Myeloproliferative...United States
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Institut de Myologie, FranceAssociation Française contre les Myopathies (AFM), ParisNot yet recruitingMerosin Deficient Congenital Muscular DystrophyFrance
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Prothelia, Inc.Cure CMD; The Bönnemann Laboratory, NINDS, National Institutes of Health; Oscar... and other collaboratorsCompletedMerosin Deficient Congenital Muscular DystrophyUnited States
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Spruce BiosciencesCompletedCongenital Adrenal Hyperplasia | CAH - Congenital Adrenal Hyperplasia | CAH - 21-Hydroxylase DeficiencyUnited States
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Damascus UniversityCompletedClass III MalocclusionSyrian Arab Republic
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Cairo UniversityCompleted
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Damascus UniversityCompletedClass III MalocclusionSyrian Arab Republic
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Origin BiosciencesCompletedMolybdenum Cofactor DeficiencyUnited States, Australia, United Kingdom, Germany, Netherlands, Turkey
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University of MinnesotaEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedMalaria | Iron Deficiency | Nutrition | Global HealthUganda
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Boston Children's HospitalAgios Pharmaceuticals, Inc.CompletedPyruvate Kinase Deficiency | Congenital Non-Spherocytic Hemolytic AnemiaUnited States, Germany, Canada, Czechia, Italy, Netherlands
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Children's Hospital of PhiladelphiaPenn State University; Newcastle UniversityCompletedSickle Cell Anemia in Children | Vitamin A Deficiency in ChildrenUnited States
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Agios Pharmaceuticals, Inc.CompletedPyruvate Kinase DeficiencyUnited States, Italy, Netherlands
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CENTOGENE GmbH RostockCompletedPyruvate Kinase DeficiencyUnited States
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Agios Pharmaceuticals, Inc.CompletedAnemia, Hemolytic | Pyruvate Kinase DeficiencyUnited States, Spain, Switzerland, Turkey, Germany, France, United Kingdom, Japan, Netherlands, Brazil, Canada, Czechia, Denmark, Italy, Korea, Republic of, Thailand
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Cairo UniversityNot yet recruiting
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Cairo UniversityCompletedClass III MalocclusionEgypt
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Wroclaw Medical UniversityCompletedClass III Malocclusion