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Clinical Trials on Familial Paroxysmal Ataxia
Total 2059 results
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Medtronic Cardiac Rhythm and Heart FailureMedtronic Atrial Fibrillation SolutionsCompletedSymptomatic Paroxysmal Atrial Fibrillation Without Clinically Significant Heart DiseasesNetherlands, Australia, France, Norway, Germany, Croatia, Italy, Argentina, Belgium
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Hospices Civils de LyonNot yet recruitingAtaxia | Genetic Disease | Degenerative DiseaseFrance
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Alder Hey Children's NHS Foundation TrustUnknownAtaxia | Posterior Fossa TumorUnited Kingdom
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Alnylam PharmaceuticalsCompletedATTR Amyloidosis | Transthyretin (TTR)-Mediated Amyloidosis | Familial Amyloidotic Polyneuropathy (FAP) | Familial Amyloid NeuropathiesFrance, Germany, Portugal, United Kingdom, Sweden, Spain
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Longbio PharmaRecruitingParoxysmal Nocturnal Hemoglobinuria (PNH)China
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BioCryst PharmaceuticalsTerminatedBCX9930 for Treatment of PNH in Subjects With Inadequate Response to C5 Inhibitor Therapy (REDEEM-1)Paroxysmal Nocturnal Hemoglobinuria (PNH)United Kingdom, Hungary, France, Italy, Spain
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AKARI TherapeuticsRadboud University Medical CenterCompletedParoxysmal Nocturnal Haemoglobinuria (PNH)Netherlands
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Leiden University Medical CenterJacobijn Gussekloo, Prof. dr.; Simon P. Mooijaart, Prof. dr.RecruitingAging | Extreme Longevity | Longevity | Familial LongevityNetherlands
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National Taiwan University HospitalTerminatedMultiple System Atrophy | Ataxia, CerebellarTaiwan
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S. Andrea HospitalCompletedMultiple Sclerosis | Cerebellar Ataxia | Hereditary AtaxiaItaly
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Wuhan Createrna Science and Technology Co., LtdNot yet recruitingParoxysmal Nocturnal Hemoglobinuria (PNH)
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BioCryst PharmaceuticalsTerminatedParoxysmal Nocturnal Hemoglobinuria (PNH)Malaysia, South Africa, Korea, Republic of
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AKARI TherapeuticsEnrolling by invitationParoxysmal Nocturnal Hemoglobinuria (PNH)United States
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Ra Pharmaceuticals, Inc.TerminatedParoxysmal Nocturnal Hemoglobinuria (PNH)United States, Australia, Canada, Finland, Germany, Hungary, New Zealand, United Kingdom
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Hospices Civils de LyonUnknownAutoimmune Encephalitis | Imbic Encephalitis | Autoimmune Cerebellar Ataxia | Stiff-person SyndromeFrance
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Riphah International UniversityCompletedVertigo, ParoxysmalPakistan
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Milestone Pharmaceuticals Inc.Medpace, Inc.CompletedParoxysmal Supraventricular Tachycardia (PSVT)United States, Canada
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Milestone Pharmaceuticals Inc.TerminatedParoxysmal Supraventricular Tachycardia (PSVT)United States
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National Institute of Neurological Disorders and...CompletedHealthy | Celiac Disease | Cerebellar AtaxiaUnited States
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Poznan University of Physical EducationCompletedAging Problems | Coordination ImpairmentPoland
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The Opole University of TechnologyCompletedVirtual Reality | Coordination ImpairmentPoland
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Moser, HeleneUnknownPelvic Floor DyssynergiaSwitzerland
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Oregon Health and Science UniversityCompletedCerebral Palsy | Physical Impairments | Cerebral Ataxia | locked-in SyndromeUnited States
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Jordi Gol i Gurina FoundationPreventive Services and Health Promotion Research Network; Instituto de Salud... and other collaboratorsCompletedBenign Positional Paroxysmal VertigoSpain
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ADARx Pharmaceuticals, Inc.ADARx Australia Pty LtdRecruitingParoxysmal Nocturnal Hemoglobinuria (PNH)Australia
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NovelMed TherapeuticsNot yet recruitingPNH - Paroxysmal Nocturnal Hemoglobinuria
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Novartis PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)China, Germany, Singapore, Korea, Republic of, Italy, United Kingdom, Malaysia, France
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Novartis PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)Italy, Japan, Taiwan, Germany, France, United Kingdom, Spain, Korea, Republic of, Czechia, Brazil, Netherlands, United States
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Hoffmann-La RocheChugai PharmaceuticalActive, not recruitingParoxysmal Hemoglobinuria, NocturnalFrance, Korea, Republic of, Italy, Japan, Germany, Hungary, Netherlands
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Alexion Pharmaceuticals, Inc.Achillion, a wholly owned subsidiary of AlexionCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)United Kingdom, United States, Italy
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Regeneron PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)Hong Kong, Hungary, Korea, Republic of, Malaysia, United Kingdom
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Boston UniversityNational Institute of Neurological Disorders and Stroke (NINDS); Food and Drug...CompletedFamilial Amyloid Polyneuropathy | Familial AmyloidosisUnited States, Italy, Japan, Sweden, United Kingdom
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PfizerCompletedTransthyretin Familial Amyloid PolyneuropathyJapan
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CENTOGENE GmbH RostockAlnylam PharmaceuticalsRecruitingCardiomyopathies | Polyneuropathies | Transthyretin Amyloidosis | Transthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin-Related (ATTR) Familial Amyloid PolyneuropathyGermany, Austria, Switzerland
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University of British ColumbiaBritish Columbia Sports Medicine Research FoundationCompleted
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Regeneron PharmaceuticalsSanofiTerminatedHeterozygous Familial Hypercholesterolemia | Non-familial HypercholesterolemiaUnited States, Bulgaria, Estonia, Russian Federation, South Africa, Ukraine
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Merck Sharp & Dohme LLCTerminatedHypercholesterolemia, Familial | Heterozygous Familial Hypercholesterolemia
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University of Texas Southwestern Medical CenterMassachusetts General HospitalRecruitingDystonia | Dystonia; Idiopathic | Dystonia, Primary | Dystonia, Secondary | Dystonia, Familial | Dystonia Disorder | Dystonias, Sporadic | Dystonia; Orofacial | Dystonia Lenticularis | Dystonia, Paroxysmal | Dystonia 6 | Dystonia 5 | Dystonia 8 | Dystonia 9 | Dystonia 19 | Dystonia 10 | Dystonia 11 | Dystonia 20 | Dystonia 12 | Dystonia... and other conditionsUnited States
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The California Medical Innovations Institute, Inc.Scripps ClinicRecruiting
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Institut Investigacio Sanitaria Pere VirgiliRecruitingFamilial Hypercholesterolemia | Familial Hypercholesterolemia - Homozygous | Familial Hypercholesterolemia - HeterozygousSpain
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Novartis PharmaceuticalsActive, not recruitingFamilial Hypercholesterolemia - HomozygousGreece, Lebanon, Turkey, France, Canada, Malaysia, Netherlands, United States
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University of MinnesotaWithdrawnMild Cognitive Impairment (MCI) | Amyotrophic Lateral Sclerosis (ALS) | Dementia With Lewy Bodies (DLB) | Alzheimer Disease (AD) | Frontotemporal Lobar Degeneration (FTLD) | Parkinsons Disease With Dementia (PDD) | Transient Epileptic Amnesia (TEA) | Temporal Lobe Epilepsy (TLE) | Spinocerebellar Ataxias... and other conditionsUnited States
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Novartis PharmaceuticalsAvailableParoxysmal Nocturnal Hemoglobinuria (PNH) | C3 Glomerulopathy (C3G)
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MeddocRecruiting
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Eidos Therapeutics, a BridgeBio companyWithdrawnTransthyretin-Related (ATTR) Familial Amyloid Polyneuropathy
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ErydelCompletedGenetic Syndrome | Nervous System DisorderItaly
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Firat UniversityRecruitingIndividuals With Multiple Sclerosis | With Ataxia Symptoms | No Secondary Disease Affecting BalanceTurkey
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Eidos Therapeutics, a BridgeBio companyWithdrawnTransthyretin-Related (ATTR) Familial Amyloid PolyneuropathyUnited States
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SOM Innovation Biotech SAHospital Vall d'HebronCompleted
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Aplastic Anemia and MDS International FoundationNational Organization for Rare DisordersRecruiting