- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Fra(X) Syndrome in United States
Total 14831 results
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University of Texas Southwestern Medical CenterAdvanced Vision ResearchCompleted
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Mayo ClinicCompleted
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M.D. Anderson Cancer CenterNovartisCompletedMyelodysplastic Syndromes | MDSUnited States
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ALZAUnknownMyelodysplastic Syndromes | LeukemiaUnited States
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Bausch & Lomb IncorporatedCompletedDry Eye SyndromesUnited States
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University of ArizonaCompletedMyelodysplastic Syndromes | LeukemiaUnited States
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Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI)CompletedMyelodysplastic Syndromes | LeukemiaUnited States
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M.D. Anderson Cancer CenterGenzyme, a Sanofi CompanyCompleted
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M.D. Anderson Cancer CenterThe Vaccine CompanyTerminated
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Sirion Therapeutics, Inc.CompletedDry Eye SyndromesUnited States
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)CompletedMyelodysplastic Syndromes | LeukemiaUnited States
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Gillette Children's Specialty HealthcareTerminatedDravet Syndrome | Lennox-Gastaut SyndromeUnited States
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University of California, San DiegoBioMarin PharmaceuticalWithdrawnBehavioral Manifestations of Lesch-Nyhan DiseaseUnited States
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BioLineRx, Ltd.CompletedAplastic Anemia | Hypoplastic Myelodysplastic SyndromeUnited States
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NYU Langone HealthWithdrawnEpilepsy | Tuberous Sclerosis | Dravet Syndrome | Focal Seizures | Lennox-Gastaut SyndromeUnited States
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Masonic Cancer Center, University of MinnesotaMayo ClinicCompletedMyelodysplastic SyndromeUnited States
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Washington University School of MedicineCompletedMyelodysplastic SyndromesUnited States
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Jonsson Comprehensive Cancer CenterNational Cancer Institute (NCI)UnknownMyelodysplastic SyndromesUnited States
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Duke UniversityCelgene CorporationCompletedMyelodysplastic SyndromesUnited States
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Paul SzabolcsEnrolling by invitationChronic Granulomatous Disease (CGD) | Wiskott-Aldrich Syndrome | Severe Chronic Neutropenia | Severe Combined Immunodeficiency (SCID) | Immunodeficiency With Predominant T-cell Defect, Unspecified | Hyper IgE Syndromes | Hyper IgM Deficiencies | Mendelian Susceptibility to Mycobacterial Disease | Common...United States
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Edimer PharmaceuticalsActive, not recruitingX-linked Hypohidrotic Ectodermal DysplasiaUnited States, United Kingdom, France, Germany, Italy
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Memorial Sloan Kettering Cancer CenterCompletedAcute Myeloid Leukemia | Advanced Myelodysplastic SyndromesUnited States
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National Institute of Arthritis and Musculoskeletal...Completed
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ShireCompletedHunter SyndromeSpain, United States, Canada, United Kingdom, France, Australia, Mexico
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Cook Children's Health Care SystemEncoded TherapeuticsRecruiting
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9 Meters Biopharma, Inc.Unknown
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Great Ormond Street Hospital for Children NHS Foundation...WithdrawnGranulomatous Disease, Chronic, X-linked, VariantUnited Kingdom
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Bausch & Lomb IncorporatedCompletedDry Eye SyndromeUnited States
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H. Lee Moffitt Cancer Center and Research InstituteCelgene CorporationCompletedMyelodysplastic Syndrome | MDSUnited States
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St. Louis UniversityEpharmix, Inc.TerminatedShort Bowel SyndromeUnited States
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Cedars-Sinai Medical CenterAbbottCompletedMyelodysplastic Syndromes | LeukemiaUnited States
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Duke UniversityAgency for Healthcare Research and Quality (AHRQ)CompletedAcute Coronary SyndromesUnited States
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NYU Langone HealthPerlmutter Cancer CenterCompletedMyelodysplastic SyndromesUnited States
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Kura Oncology, Inc.Terminated
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Catalyst Pharmaceuticals, Inc.No longer availableLambert-Eaton Myasthenic Syndrome | Congenital Myasthenic Syndrome | Nystagmus, AcquiredUnited States
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Denali Therapeutics Inc.Active, not recruitingMucopolysaccharidosis IIUnited States, Netherlands, Canada, United Kingdom
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University of RochesterTerminatedHealthy | Dry Eye SyndromeUnited States
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TelikTerminatedMyelodysplastic Syndrome (MDS)United States
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AllerganCompleted
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Stanford UniversityNot yet recruitingPTEN Gene Mutation | PTEN Hamartoma Tumor Syndrome | PTEN Hamartoma SyndromeUnited States
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Jonsson Comprehensive Cancer CenterCelgene Corporation; CTI BioPharmaTerminatedMyelodysplastic Syndromes | LeukemiaUnited States
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University of California, Los AngelesAvailableDravet SyndromeUnited States
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Arkansas Children's Hospital Research InstituteBaylor College of Medicine; USDA Grand Forks Human Nutrition Research CenterWithdrawn
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EspeRare FoundationIqvia Pty Ltd; Pierre Fabre MedicamentRecruitingX-Linked Hypohidrotic Ectodermal Dysplasia (XLHED)United States, Spain, France, Germany, Italy, United Kingdom
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Zogenix International Limited, Inc., a subsidiary...CompletedDravet Syndrome | Lennox Gastaut SyndromeUnited States
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ShireCompletedHunter SyndromeUnited States, United Kingdom, Canada
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H. Lee Moffitt Cancer Center and Research InstituteNovartis PharmaceuticalsRecruitingMyelodysplastic SyndromesUnited States
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National Heart, Lung, and Blood Institute (NHLBI)WithdrawnMyelodysplastic SyndromesUnited States
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Onconova Therapeutics, Inc.CompletedMyelodysplastic SyndromeUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoThrasher Research FundUnknownWest SyndromeUnited States