- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Genetic Disease
Total 377929 results
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4D Molecular TherapeuticsTerminated
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University of OxfordUniversity College, London; Moorfields Eye Hospital NHS Foundation TrustCompleted
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STZ eyetrialUniversity Hospital TuebingenCompleted
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Zhejiang UniversityCompletedColorectal Neuroendocrine Carcinomas (CRNEC); Genomic Landscape; Genetic Landscape; Prognosis; CCL5; PAX5
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Fudan UniversityRecruitingBreast Cancer | Genetic SusceptibilityChina
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King Faisal Specialist Hospital & Research CenterSaudi National Comprehensive Plan for Science & TechnologyCompletedGeneric Drug Quality | Generic Formulation InterchangeabilitySaudi Arabia
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The Cleveland ClinicCompletedHypertrophic Cardiomyopathy | Genetic Disease | Gene Product Sequence VariationUnited States
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Medical University of South CarolinaCompletedActinic PorokeratosisUnited States
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Edimer PharmaceuticalsCompleted
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National Human Genome Research Institute (NHGRI)Enrolling by invitation
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National Institute of Mental Health (NIMH)CompletedPolymorphism- Genetic | Reward Mediating SystemUnited States
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European HospitalUnknownEmbryo's Genetic and Chromosomal QualityItaly
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New York Blood CenterTerminatedLymphoma | Leukemia | Myelodysplasia | Genetic Disease | Severe Aplastic AnemiaUnited States
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Children's Hospital of Fudan UniversityRecruitingGenetic Predisposition to Disease | Newborn | Defect, Congenital | Hereditary DiseaseChina
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M.D. Anderson Cancer CenterRecruitingDepression | Hematopoietic and Lymphoid Cell Neoplasm | Malignant Solid Neoplasm | Anxiety Disorder | Genetic DisorderUnited States
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Chinese University of Hong KongRecruiting
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BiogenCompleted
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University of AberdeenRecruitingTakotsubo CardiomyopathyUnited Kingdom
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National Cancer Institute (NCI)Completed
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Gangnam Severance HospitalCompleted
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Daniel DobererCompletedHealthy Subjects | Genetic Polymorphism | Heme OxygenaseAustria
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Chungnam National UniversityKorea Healthcare Technology R&D Project; Korea Advanced Institute of Science...CompletedSingle-nucleotide Polymorphism (SNP) for GlaucomaKorea, Republic of
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University of UlsterDSM Nutritional Products, Inc.UnknownParticipants With the MTHFR 677TT GenotypeUnited Kingdom
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McMaster UniversityUniversity of Manitoba; St. Joseph's Healthcare Hamilton; University of British... and other collaboratorsUnknownAsthma in Children | Environmental Exposure | Genetic Predisposition | Allergy in Children
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University of California, DavisCompletedFragile X Syndrome | Genetic DiseasesUnited States
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Maastricht University Medical CenterCompletedHailey Hailey DiseaseNetherlands
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Assistance Publique - Hôpitaux de ParisRecruitingHypohidrotic Ectodermal DysplasiaFrance
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Kedrion S.p.A.CompletedLigneous ConjunctivitisUnited States, Italy
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PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Brazil, Chile, Czechia, Sweden, Switzerland, Turkey, Germany, Poland
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University of HelsinkiUnknownCoronary Disease | InflammationFinland
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ScitonRecruiting
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Goldman, Butterwick, Fitzpatrick and GroffGalderma R&DNot yet recruitingSkin Laxity
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FA CorporationUniversity of Texas Southwestern Medical CenterEnrolling by invitation
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University of California, IrvineCompletedSkin LaxityUnited States
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Sofwave Medical LTDCompleted
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Candela CorporationWithdrawn
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ThermiGen, LLCCompletedSkin LaxityUnited States
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Ulthera, IncCompleted
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CHU de ReimsUnknownBullous PemphigoidFrance
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PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, Duchenne | Musculoskeletal DiseaseUnited States, Taiwan, India, Korea, Republic of, Thailand, Australia, Brazil, Bulgaria, Canada, China, Hong Kong, Malaysia, Mexico, Poland, Puerto Rico, Russian Federation, Turkey, Japan
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Novo Nordisk A/SCompletedNoonan Syndrome | Genetic DisorderSweden
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Tulane UniversityAllerganCompleted
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University of Colorado, DenverCompletedFocal Dermal Hypoplasia
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TESS Research FoundationStanford UniversityEnrolling by invitationEpilepsy | Movement Disorders | Rare Diseases | Genetic Disorder | Citrate Transporter Deficiency | SLC13A5 Deficiency | EIEE25 | Kohlschutter-Tonz Syndrome (Non-ROGDI) | 17p13.1 Deletions Confined to SLC13A5 Gene | Citrate Transporter DisorderUnited States
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National Institute of Environmental Health Sciences...Massachusetts General HospitalRecruitingInfertility | Hypogonadism | Amenorrhea | Genetic DisorderUnited States
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Edimer PharmaceuticalsCompletedHypohidrotic Ectodermal DysplasiaUnited States
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Edimer PharmaceuticalsCompletedHypohidrotic Ectodermal DysplasiaUnited States
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Hugo W. Moser Research Institute at Kennedy Krieger...RecruitingLeukoencephalopathies | Genetic Disease | White Matter Disease | Ataxia, Cerebellar | LBSL | Leukoencephalopathy With Brainstem and Spinal Cord Involvement and Lactate ElevationUnited States