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Clinical Trials on Genetic Disorder
Total 151205 results
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Scripps HealthWest Virginia UniversityCompletedCardiovascular Diseases | Heart Failure | Hypertension | Atrial Fibrillation | Metabolic Syndrome | Genetic DiseaseUnited States
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PTC TherapeuticsTerminatedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Germany, Brazil, Bulgaria, Chile, Czechia, Poland, Sweden, Switzerland, Turkey
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PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Brazil, Chile, Czechia, Sweden, Switzerland, Turkey, Germany, Poland
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AJapan
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AItaly, Sweden, Netherlands, Austria, Spain, United States, Switzerland, Germany, France, Hungary, Greece, Slovenia, Czechia, Slovakia, Poland
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Antonio PersicoUniversity of Bari; Associazione Italiana Sindrome di Phelan-McDermid (AISPHEM)Enrolling by invitationAutism Spectrum Disorder | Phelan-McDermid SyndromeItaly
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Novo Nordisk A/SCompletedComparison of the Action of Drugs in the Body and Safety of N8 and Advate® in Haemophilia A SubjectsCongenital Bleeding Disorder | Haemophilia ASpain, Germany, Switzerland, Italy, Israel
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited States, Germany, Switzerland, United Kingdom, Italy, Japan, Turkey
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia ASpain, Germany, Malaysia, Latvia
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited Kingdom, Malaysia
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FVII DeficiencySlovakia, Israel, Spain, India, Iran, Islamic Republic of, Pakistan, Turkey, Germany, Serbia, Italy, Greece, Thailand, France, United States, Hong Kong, Venezuela
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Hospices Civils de LyonNot yet recruiting
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Bowdoin CollegeMassachusetts General HospitalCompletedTourette Syndrome | Persistent Tic DisorderUnited States
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Otsuka Pharmaceutical Development & Commercialization...TerminatedTourette's Disorder (TD)United States, Canada, Hungary
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Hospices Civils de LyonUnknownCancer | Paraneoplastic Syndromes | Neurologic Disorder | Immune System and Related Disorders | Tumor GeneticsFrance
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University Hospital, MontpellierRecruitingHemophilia A | Hemophilia B | ArthropathyFrance
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Novo Nordisk A/SActive, not recruitingHaemophilia A Without Inhibitors | Haemophilia B Without InhibitorsSpain, United States, Korea, Republic of, United Kingdom, Australia, Lithuania, France, Turkey, India, Estonia, Russian Federation, Ukraine, Mexico, Japan, South Africa, Serbia, Canada, Croatia, Algeria, Bosnia and Herzegovina, ... and more
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Laboratoire français de Fractionnement et de BiotechnologiesLFB USA, Inc.CompletedA Phase III Study on the Safety, Pharmacokinetics and Efficacy of Coagulation Factor VIIa (PERSEPT2)Hemophilia A With Inhibitors | Hemophilia B With InhibitorsBulgaria, Ukraine, Czechia, United States, Georgia, South Africa
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedFragile X SyndromeUnited States
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Bioverativ Therapeutics Inc.Swedish Orphan BiovitrumCompletedSevere Hemophilia BSweden, United States, France, Italy, Russian Federation, United Kingdom, Germany, China, Poland, Japan, Australia, Brazil, Canada, India, South Africa, Hong Kong, Belgium
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Bioverativ Therapeutics Inc.CompletedSevere Hemophilia BUnited States, Italy, Belgium, Australia, Brazil, Hong Kong, India, Ireland, Japan, South Africa, United Kingdom, Netherlands, Sweden, Canada, Poland, China, France, Germany
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.National Institutes of Health (NIH)CompletedFragile X SyndromeUnited States
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University Hospital, AngersRecruitingRare Diseases | Genetic DiseaseFrance
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VA Boston Healthcare SystemCompletedRare Diseases | Genetic DiseaseUnited States
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Hacettepe UniversityCompletedMusculoskeletal Diseases | Genetic Disease | Metabolic Disease | Delays DevelopmentalTurkey
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Marquette UniversityUniversity of UtahRecruitingTourette Disorder | Persistent Tic DisordersUnited States
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Swedish Orphan BiovitrumCompletedHaemophilia A | Haemophilia BSweden, Finland, Denmark
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Karolinska University HospitalKarolinska Institutet; The Swedish Society of MedicineUnknownHemophilia A | Hemophilia B | Von Willebrand's DiseaseSweden
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Virginia Commonwealth UniversityCSL BehringCompletedHemophilia A | Hemophilia B | Vitamin D DeficiencyUnited States
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Suzhou Alphamab Co., Ltd.RecruitingHemophilia A With Inhibitor | Hemophilia B With InhibitorChina
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Children's Hospital Medical Center, CincinnatiRecruitingFragile X SyndromeUnited States
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Novo Nordisk A/SActive, not recruitingHaemophilia A With Inhibitors | Haemophilia B With InhibitorsSpain, Korea, Republic of, India, Australia, United Kingdom, Russian Federation, Poland, Ukraine, Thailand, Mexico, United States, Turkey, Japan, South Africa, Serbia, France, Croatia, Denmark, Algeria, Bulgaria, Malaysia, Portugal, Slovaki... and more
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AryoGen Pharmed Co.CompletedHemophilia A With Inhibitor | Hemophilia B With InhibitorIran, Islamic Republic of
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Chia Tai Tianqing Pharmaceutical Group Co., Ltd.UnknownHemophilia A With Inhibitor | Hemophilia B With InhibitorChina
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedHemophilia A | Hemophilia BUnited States, Canada, France, Italy
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rEVO BiologicsLaboratoire français de Fractionnement et de BiotechnologiesCompletedHemophilia A With Inhibitors | Hemophilia B With InhibitorsUnited States, Bulgaria, Poland, Russian Federation, Belarus, Georgia, Israel, Romania, Ukraine, United Kingdom
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BayerCompletedHemophilia A, Hemophilia BItaly, China, New Zealand, Russian Federation, Taiwan, Singapore, Bulgaria, United States, Denmark, Germany, Hungary, South Africa, United Kingdom, Romania, Colombia, Mexico, Turkey, France, India, Japan, Australia, Netherlands, Poland and more
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New York Presbyterian HospitalCompletedHemophilia A | Hemophilia BUnited States
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Esoterix Genetic Laboratories, LLCUnknownFragile X SyndromeUnited States
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Wyeth is now a wholly owned subsidiary of PfizerCompletedHemophilia B | Allergic ReactionsFrance, Italy, United States, Austria, Belgium, Spain, United Kingdom, Canada, Germany
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Universidad de GranadaUniversity of La LagunaCompleted
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Institute for Neurodegenerative DisordersCompletedParkinson Disease | Alzheimer Disease | Mild Cognitive Impairment | Fragile X Syndrome | Huntington Disease | Autistic Spectrum DisordersUnited States
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Parkinson's Disease and Movement Disorders CenterOrtho-McNeil Neurologics, Inc.TerminatedTourette's Syndrome | Motor Tic Disorder | Vocal Tic DisorderUnited States
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Rett Syndrome Research TrustNot yet recruitingRett SyndromeUnited States
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National Human Genome Research Institute (NHGRI)RecruitingGenetic DiseaseUnited States
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University of California, Los AngelesNational Institute of Mental Health (NIMH)CompletedTourette's DisorderUnited States
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University of MinnesotaTerminated
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Stanford UniversityNot yet recruitingLiver Failure | Liver Cirrhosis | Hemophilia A | Hemophilia B | Hemophilia | Liver Transplant Disorder | Coagulation Factor DeficiencyUnited States
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Andrea GropmanNational Center for Research Resources (NCRR); Rare Diseases Clinical Research... and other collaboratorsCompletedBrain Diseases, Metabolic, Inborn | Ornithine Transcarbamylase Deficiency | Urea Cycle DisorderUnited States