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Clinical Trials on Genetic Alteration in Australia
Total 960 results
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Flatley Discovery Lab LLCCompletedCystic FibrosisAustralia
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CSL BehringRecruiting
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ModernaTX, Inc.RecruitingPhenylketonuriaUnited States, Australia
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LEO PharmaCompletedAtopic DermatitisAustria
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The AlfredUnknown
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Medical University of ViennaCompleted
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Stefan WoehrlMedical University of ViennaCompletedAtopic DermatitisAustria
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PfizerPfizerCompletedSickle Cell DiseaseAustralia, United States
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Medical University of ViennaCompleted
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Baxalta now part of ShireBaxter Healthcare, Ltd. (New Zealand), Baxter Healthcare Pty. Ltd. (Australia)CompletedAlpha 1-Antitrypsin DeficiencyAustralia, New Zealand
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Foundation for Angelman Syndrome Therapeutics,...Queensland University of TechnologyRecruiting
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Medical University of ViennaCompletedMacular Degeneration | Ocular Physiology | Regional Blood Flow | Genetic PolymorphismAustria
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Regeneron PharmaceuticalsSanofiCompletedAtopic DermatitisGermany, New Zealand, Australia
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The University of QueenslandTelethon Kids InstituteCompletedBronchiectasis | Cystic FibrosisAustralia, New Zealand
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Bayside HealthUnknown
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The AlfredUnknown
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Gilead SciencesCompletedCystic FibrosisAustralia
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Spark TherapeuticsChildren's Hospital of Philadelphia; University of Pittsburgh; St. James's Hospital... and other collaboratorsTerminated
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Premier Specialists, AustraliaUnknownEpidermolysis Bullosa Simplex | Epidermolysis Bullosa Simplex Kobner | Weber-Cockayne SyndromeAustralia
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Gilead SciencesWithdrawnCystic Fibrosis | Mucociliary ClearanceAustralia
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Barwon HealthNational Health and Medical Research Council, Australia; University of MelbourneCompleted
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Medical University of ViennaCompleted
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Amicus TherapeuticsCompleted
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4D Molecular TherapeuticsActive, not recruiting
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Amicus TherapeuticsCompletedFabry DiseaseAustralia, Brazil
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Bayside HealthNational Health and Medical Research Council, Australia; Monash University; Cystic...Completed
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Gilead SciencesCompletedCystic Fibrosis | Mucociliary Clearance | Airway HydrationAustralia
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Gilead SciencesCompletedCystic Fibrosis | Mucociliary Clearance | Airway HydrationAustralia
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Bayside HealthNational Health and Medical Research Council, Australia; Monash University; Cystic...UnknownCystic FibrosisAustralia
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Medical University of GrazCompletedPsoriasis | Atopic Eczema | Polymorphic Light EruptionAustria
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AceLink Therapeutics, Inc.Novotech (Australia) Pty LimitedCompletedAutosomal Dominant Polycystic KidneyAustralia
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Glycomine, Inc.Recruiting24-Week Study to Assess the PD, Safety, Tolerability, and PK of GLM101 in Participants With PMM2-CDGPmm2-CDGSpain, Australia, United States
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Hospital RudolfstiftungOesterreichische MuskelforschungCompletedCarrier of Duchenne Muscular DystrophyAustria
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Western Sydney Local Health DistrictRecruitingVentricular Tachycardia | Cardiomyopathy, Dilated | Heart Disease Structural Disorder | Sarcoidosis | Cardiomyopathy, Hypertrophic | Cardiomyopathy, Familial | Cardiomyopathy Ischemic | Arrhythmogenic Right Ventricular Cardiomyopathy 1 | Arrhythmogenic Left Ventricular CardiomyopathyAustralia
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Murdoch Childrens Research InstituteMelbourne Health; Austin Health; Royal Brisbane and Women's Hospital; The University... and other collaboratorsCompletedHereditary HaemochromatosisAustralia
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Holostem Terapie Avanzate s.r.l.Paracelsus Medical UniversityTerminatedRecessive Dystrophic Epidermolysis BullosaAustria
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Krystal Biotech, Inc.Novotech (Australia) Pty LimitedWithdrawn
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CSL LimitedCompletedPrimary Immune DeficiencyAustralia, New Zealand
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncEnrolling by invitationMucopolysaccharidosis III-AUnited States, Australia, Spain
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Melbourne HealthSanofiWithdrawnLysosomal Storage Diseases | Fabry Disease | Niemann-Pick Disease, Type C | Gaucher DiseaseAustralia
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University College, LondonUniversity of Sydney; University Hospital BirminghamUnknownFabry DiseaseUnited Kingdom, Australia
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Bayside HealthMonash University; The AlfredUnknown
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National Eye Institute (NEI)RecruitingCone-Rod Degeneration | Rod-Cone DegenerationUnited States, Australia
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BayerTerminatedHemophilia A and BAustralia, United Kingdom, Taiwan, Japan, Korea, Republic of, Austria, Bulgaria, Hungary, Italy, France, New Zealand
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AlgiPharma ASAlgiPharma Australia Pty. Ltd.UnknownCystic FibrosisAustralia
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OctapharmaTerminatedImmunologic Deficiency SyndromesAustria
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Prof. Johann BauerRecruiting
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Arrowhead PharmaceuticalsCompletedDyslipidemias | Hypertriglyceridemia | Familial HypercholesterolemiaAustralia, New Zealand
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Medical University of ViennaCompleted
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CSL BehringCompletedHemophilia BGermany, Australia, Italy, Israel, Czech Republic, Spain, France, Canada, Austria, Russian Federation