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Clinical Trials on Genetic Alteration in Australia
Total 960 results
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Hugo W. Moser Research Institute at Kennedy Krieger...Concord Hospital; FSHD Global Research FoundationCompletedFacioscapulohumeral Muscular DystrophyUnited States, Australia
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Medical University of ViennaRecruiting
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Academisch Medisch Centrum - Universiteit van Amsterdam...UnknownHemophiliaNetherlands, Austria, Australia, Belgium, Canada, Finland, Germany, Italy, Spain, United Kingdom
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TWi Biotechnology, Inc.RecruitingGeneralized Epidermolysis Bullosa SimplexUnited States, Taiwan, Australia, Philippines, Austria, Italy, Poland
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Eli Lilly and CompanyIncyte CorporationCompletedAtopic DermatitisSpain, Australia, Switzerland, Israel, Korea, Republic of, Japan, Poland, Argentina, Austria, Hungary
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncTerminatedMucopolysaccharidosis III | Sanfilippo Syndrome | MPS IIIA | Sanfilippo AUnited States, Spain, Australia
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Technische Universität DresdenCompleted
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OctapharmaTerminatedImmunologic Deficiency SyndromesAustria
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Apollomics (Australia) Pty. Ltd.Novotech (Australia) Pty Limited; Apollomics Inc. (formerly CBT Pharmaceuticals...CompletedSolid Tumor | Microsatellite Instability | Mismatch Repair Deficiency | Cancer of Unknown Primary SiteAustralia
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Prof. Johann BauerRecruiting
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Bayside HealthThe AlfredUnknownAsthma | Cystic Fibrosis | Bronchiolitis Obliterans | Lung TransplantationAustralia
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Novilla PharmaceuticalsNot yet recruitingAcute Pain | Gout Flare | Acute Gouty ArthritisAustralia
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Murdoch Childrens Research InstituteCompletedTourette Syndrome in AdolescenceAustralia
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BioMarin PharmaceuticalActive, not recruitingAchondroplasiaAustralia, United Kingdom
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PharmaxisCompletedCystic FibrosisAustralia, New Zealand
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Arrowhead PharmaceuticalsCompletedHypertriglyceridemia | Familial ChylomicronemiaAustralia, Canada, New Zealand
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Arrowhead PharmaceuticalsTerminatedCystic Fibrosis, PulmonaryAustralia, New Zealand
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BioMarin PharmaceuticalCompletedMucopolysaccharidosis IVA (Morquio A Syndrome)Australia
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Arrowhead PharmaceuticalsRecruitingMyotonic Dystrophy 1New Zealand, Australia
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Murdoch Childrens Research InstituteCompleted
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Ascend Biopharmaceuticals LtdCompletedBasal Cell Nevus Syndrome | Basal Cell CarcinomaAustralia
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Medical University of ViennaCompletedFuchs' Endothelial DystrophyAustria
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Bioverativ Therapeutics Inc.Swedish Orphan BiovitrumCompletedHemophilia BUnited States, United Kingdom, South Africa, Netherlands, Ireland, Australia
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Garvan Institute of Medical ResearchCompletedPrader-Willi SyndromeAustralia
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Murdoch Childrens Research InstituteFriedreich's Ataxia Research AllianceCompleted
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PYC TherapeuticsNot yet recruitingOptic Atrophies, Hereditary | Autosomal Dominant Optic Atrophy | Optic Atrophy, Autosomal Dominant | Kjer Optic AtrophyAustralia
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Amicus TherapeuticsCompletedFabry DiseaseFrance, Austria, United States, Belgium, Japan, United Kingdom, Denmark, Brazil, Australia, Italy
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Cooperative International Neuromuscular Research...Washington University School of Medicine; Children's National Research Institute and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Australia, Italy
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The University of QueenslandRecruitingAutosomal Dominant Polycystic Kidney DiseaseAustralia
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The University of QueenslandNot yet recruitingAtaxia TelangiectasiaAustralia
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The University of QueenslandNational Health and Medical Research Council, AustraliaCompletedAtaxia TelangiectasiaAustralia
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Western Sydney Local Health DistrictMonash University; University of Sydney; University of Melbourne; The University... and other collaboratorsNot yet recruiting
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Novartis PharmaceuticalsCompletedAtopic DermatitisGermany, Austria, France
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Newron Pharmaceuticals SPATerminatedRett SyndromeUnited States, India, United Kingdom, Australia, Italy
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PYC TherapeuticsRecruitingRetinitis Pigmentosa | Eye Diseases, Hereditary | Retinal Dystrophies | Retinal Dystrophy Rod | Retinal Dystrophy Rod ProgressiveUnited States, Australia
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ISU Abxis Co., Ltd.CompletedGaucher DiseaseAustralia
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Castle Creek Pharmaceuticals, LLCTerminatedEpidermolysis Bullosa SimplexUnited States, Israel, Australia, Austria, France, Germany, Netherlands, United Kingdom
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncActive, not recruitingMucopolysaccharidosis III | Sanfilippo Syndrome | MPS IIIA | Sanfilippo AUnited States, Australia, Spain
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PfizerCompletedAtopic DermatitisUnited States, Canada, Australia, Germany, Hungary
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Akesobio Australia Pty LtdCompletedAtopic DermatitisNew Zealand, Australia
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Murdoch Childrens Research InstituteCompletedHypertension | Blood Pressure | Neurofibromatosis 1Australia
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Percheron TherapeuticsActive, not recruitingDuchenne Muscular DystrophyUnited Kingdom, Australia, Serbia, Turkey, Bulgaria
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Ionis Pharmaceuticals, Inc.RecruitingPelizaeus-Merzbacher DiseaseFrance, Australia, Germany, Netherlands
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Sydney Children's Hospitals NetworkChildren's Hospital Colorado; Women's and Children's Hospital, Adelaide; John... and other collaboratorsCompletedDiabetes | Cystic FibrosisAustralia, United States
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Jiangsu Atom Bioscience and Pharmaceutical Co.,...CompletedHyperuricemia | GoutAustralia
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Eisai LimitedCompletedCognitive ImpairmentUnited States, Spain, Australia
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ACELYRIN Inc.RecruitingThyroid Eye DiseaseUnited States, Australia
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Arrowhead PharmaceuticalsActive, not recruitingHomozygous Familial HypercholesterolemiaAustralia, Canada, United States, South Africa
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Beyond Air Inc.UnknownCystic Fibrosis | Mycobacterium Avium Complex | Non-Tuberculous Mycobacterial Pneumonia | Mycobacterial Pneumonia | Mycobacterium Abscessus InfectionAustralia