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Clinical Trials on Genetic Alteration in Australia
Total 960 results
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BioCeryxUniversity of British Columbia; University College London Hospitals; Brugmann... and other collaboratorsUnknownTrisomy 21 and Other Fetal AneuploidyAustralia, United Kingdom, Spain, Canada, Belgium, Portugal
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Origin BiosciencesCompletedMolybdenum Cofactor DeficiencyUnited States, Australia, United Kingdom, Germany, Netherlands, Turkey
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Hoffmann-La RocheRecruitingAngelman SyndromeAustralia, United States, Spain, Italy, France, Germany
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Akesobio Australia Pty LtdRecruitingPhase 2 Study of Efficacy and Safety of AK120, in Subjects With Moderate-to-Severe Atopic DermatitisAtopic DermatitisUnited States, Australia, New Zealand
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Perminder SachdevMelbourne Health; Royal Brisbane and Women's Hospital; The University of Queensland and other collaboratorsRecruiting
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ApoPharmaCompletedFriedreich's AtaxiaCanada, Australia, Belgium, France, Italy, Spain
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Medical University InnsbruckQueen's University, Belfast; Cystic Fibrosis Foundation; European Cystic Fibrosis...Active, not recruiting
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Medical University of ViennaRecruitingPompe Disease | McArdle DiseaseAustria
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ProtalixChiesi Farmaceutici S.p.A.CompletedFabry DiseaseAustralia, Netherlands, United Kingdom, Canada, Czechia, Norway, Slovenia
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Baxalta now part of ShireCompletedVon Willebrand DiseaseNetherlands, Spain, United States, Belgium, Australia, United Kingdom, Austria, Italy, Bulgaria, Japan, Poland, Germany, India, Canada, Russian Federation, Sweden
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Jnana TherapeuticsRecruitingPhenylketonuriaUnited States, Australia
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Bioverativ Therapeutics Inc.Swedish Orphan BiovitrumCompletedSevere Hemophilia AUnited States, Australia, New Zealand
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PfizerCompletedHemophilia BGermany, Austria
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MedImmune LLCAmgenCompletedAtopic DermatitisUnited States, Germany, New Zealand, Hungary, Australia, Canada
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Zynerba Pharmaceuticals, Inc.Completed22Q Deletion SyndromeUnited States, Australia
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BioMarin PharmaceuticalTerminatedPompe DiseaseUnited States, United Kingdom, Australia, France, Germany, New Zealand
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Pixium Vision SACompletedRetinitis Pigmentosa | Choroideremia | Cone Rod DystrophyAustria, Spain, United Kingdom, France, Germany
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Leiden University Medical CenterZonMw: The Netherlands Organisation for Health Research and Development; Horizon...RecruitingSevere Combined Immunodeficiency Due to RAG1 DeficiencySpain, Netherlands, Italy, Poland, Australia, Turkey, United Kingdom
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ShireCompletedFabry DiseaseUnited States, Slovenia, Australia, Finland, Poland, Czechia, United Kingdom
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Amicus TherapeuticsCompletedFabry DiseaseCanada, Belgium, United States, Australia, Netherlands
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Medical University of ViennaCompletedDry Eye Syndrome | Thyroid-associated OphthalmopathyAustria
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Medical University of ViennaUnknownPolycystic Kidney, Type 1 Autosomal Dominant Disease | Polycystic Kidney, Type 2 Autosomal Dominant DiseaseAustria
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Ascend Biopharmaceuticals LtdCompletedBasal Cell Nevus Syndrome | Skin Neoplasm | Nodular Basal Cell Carcinoma of SkinAustralia
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LEO PharmaCompletedAtopic DermatitisUnited States, Canada, Australia
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LEO PharmaCompletedAtopic DermatitisUnited States, Denmark, United Kingdom, Korea, Republic of, Canada, Italy, Australia, Poland, Russian Federation
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Bioverativ Therapeutics Inc.CompletedSevere Hemophilia AUnited States, United Kingdom, Australia
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Merck KGaA, Darmstadt, GermanyCompletedGrowth Hormone Deficiency | Turner SyndromeArgentina, Australia, Austria, Canada, France, Germany, Italy, Norway, Russian Federation, Singapore, Spain, Sweden, United Kingdom
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisAustralia, United Kingdom
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Astellas Pharma IncCompletedDermatitis, AtopicFrance, Germany, Spain, Belgium, Netherlands, Finland, Austria, United Kingdom, Italy, Czech Republic, Switzerland, Portugal, Denmark
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Bioverativ Therapeutics Inc.CompletedSevere Hemophilia BUnited States, Italy, Belgium, Australia, Brazil, Hong Kong, India, Ireland, Japan, South Africa, United Kingdom, Netherlands, Sweden, Canada, Poland, China, France, Germany
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BayerCompletedHemophilia AGermany, Spain, Austria, Italy, Slovenia, Greece, Netherlands
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BayerActive, not recruitingHemophilia ASpain, Germany, Austria, Greece, Italy, Slovenia
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Medical University of ViennaCompletedBreast Cancer | Hereditary Breast and Ovarian Cancer SyndromeAustria
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BioMarin PharmaceuticalActive, not recruitingAchondroplasiaUnited States, Australia, France, United Kingdom
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BioMarin PharmaceuticalCompletedAchondroplasiaUnited States, Australia, France, United Kingdom
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PfizerActive, not recruitingHemophilia A | Hemophilia BUnited States, Canada, Spain, Australia, Korea, Republic of, Taiwan, Brazil, Italy, Japan, Turkey, Germany, United Kingdom, Saudi Arabia, France, Sweden, Belgium, Greece, Israel
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Botanix PharmaceuticalsCompletedAtopic DermatitisUnited States, Australia, New Zealand
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PTC TherapeuticsRecruitingHuntington DiseaseAustralia, France, Germany, Netherlands, United Kingdom, Spain, Austria, Canada, Italy, New Zealand
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Amicus TherapeuticsCompletedOpen-Label Extension Study of the Long-Term Effects of Migalastat HCL in Patients With Fabry DiseaseFabry DiseaseUnited States, Austria, United Kingdom, Argentina, Australia, Belgium, Brazil, Canada, Denmark, Egypt, France, Italy, Japan, Spain, Turkey
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Sangamo TherapeuticsEnrolling by invitationFabry Disease | Fabry Disease, Cardiac VariantUnited States, Australia, United Kingdom
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PfizerActive, not recruitingDuchenne Muscular DystrophyUnited States, Spain, Belgium, Korea, Republic of, Taiwan, Canada, Australia, Germany, Japan, France, Italy, United Kingdom, Russian Federation, Israel, Switzerland
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Hoffmann-La RocheActive, not recruitingSevere Hemophilia ACanada, United States, United Kingdom, Belgium, Australia, Austria, Brazil, France, Germany, Israel, Italy, South Africa, Spain, Turkey
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Hoffmann-La RocheCompletedAtopic DermatitisUnited States, Korea, Republic of, Canada, United Kingdom, Germany, Australia, Poland, Finland, France, Spain, Switzerland, Czechia, Netherlands, Taiwan
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AmgenActive, not recruitingAtopic DermatitisKorea, Republic of, United States, Turkey, Hong Kong, United Kingdom, Australia, Brazil, Canada, Argentina
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Sydney Children's Hospitals NetworkJohns Hopkins University; Children's Hospital of Philadelphia; University of... and other collaboratorsUnknownCharcot-Marie-Tooth DiseaseUnited States, Australia, Italy
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PTC TherapeuticsCompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | DystrophinopathyUnited Kingdom, Canada, Germany, Spain, Sweden, Italy, Australia, Belgium, France, Israel
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Respirion Pharmaceuticals Pty LtdRecruitingPseudomonas Aeruginosa | Cystic Fibrosis Lung | Respiratory Infections, Recurrent, ChronicUnited States, Australia
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FibroGenTerminatedDuchenne Muscular DystrophyUnited States, Belgium, Israel, Spain, Canada, Australia, Switzerland, United Kingdom, France, China, Netherlands, Italy, Austria, Czechia
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PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, Duchenne | Musculoskeletal DiseaseUnited States, Taiwan, India, Korea, Republic of, Thailand, Australia, Brazil, Bulgaria, Canada, China, Hong Kong, Malaysia, Mexico, Poland, Puerto Rico, Russian Federation, Turkey, Japan
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Shire Regenerative Medicine, Inc.TerminatedEpidermolysis BullosaUnited States, Spain, Austria, Canada, France, Germany, Poland, Portugal