- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Genetic Diseases, Inborn in China
Total 31698 results
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Children's Hospital of Fudan UniversityThe First Affiliated Hospital of Zhengzhou University; Shanghai Children's... and other collaboratorsActive, not recruitingSevere Combined Immunodeficiency DiseaseChina
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Institute of Hematology & Blood Diseases Hospital...EdiGene Inc.; The Affiliated Hospital Of Guizhou Medical University; Zunyi Medical...Active, not recruitingTransfusion Dependent Beta-ThalassaemiaChina
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EdiGene (GuangZhou) Inc.Active, not recruitingTransfusion Dependent Beta-ThalassaemiaChina
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AbbVieActive, not recruiting
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Novo Nordisk A/SEnrolling by invitation
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The 923rd Hospital of Joint Logistics Support Force...Guangzhou Reforgene Medicine Co., Ltd.RecruitingHemoglobinopathies | Hereditary Diseases | Alpha Thalassemia Hemoglobin H Constant SpringChina
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Beijing Pins Medical Co., LtdQilu Hospital of Shandong University; Qingdao University; Yantai Yuhuangding... and other collaboratorsUnknownLennox-Gastaut SyndromeChina
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SanofiRecruitingGlycogen Storage Disease Type IIBelgium, United States, China, Germany, Italy, Netherlands, Spain, Taiwan, United Kingdom
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Ning Wang, MD., PhD.Recruiting
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Chia Tai Tianqing Pharmaceutical Group Co., Ltd.RecruitingHemophilia A | Hemophilia BChina
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.CompletedDuchenne Muscular DystrophySpain, United States, Russian Federation, Italy, China, Turkey
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Sun Yat-sen UniversityRecruitingImmune System Diseases | Autoimmune Diseases | Endocrine System Diseases | Thyroid Diseases | Eye Diseases, Hereditary | Graves Ophthalmopathy | Graves Disease | Hyperthyroidism | Thyroid-associated OphthalmopathyChina
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Zhi-Hong Liu, M.D.Terminated
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Eyecure Therapeutics Inc.Beijing Tongren HospitalUnknownLeber Congenital Amaurosis, Retinitis PigmentosaChina
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Bioray LaboratoriesXiangya Hospital of Central South University; Sun Yat-Sen Memorial Hospital... and other collaboratorsNot yet recruiting
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Shanghai Belief-Delivery BioMed Co., LtdActive, not recruiting
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Jiangsu Gensciences lnc.RecruitingHemophilia | Hemophilia A With Inhibitor | Male | Hemophilia B With InhibitorChina
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Shenzhen Beike Bio-Technology Co., Ltd.The Affiliated Nanjing Drum Tower Hospital of Nanjing University Medical... and other collaboratorsUnknown
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Second Affiliated Hospital, School of Medicine,...Recruiting
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Sun Yat-sen UniversityUnknown
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Sun Yat-sen UniversityRecruitingBreast Cancer | Cognitive Impairment | Brain Metastases | Radiotherapy Side Effect | Gangliosidosis, GM1China
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Translational Research Center for Medical Innovation...RecruitingNeutral Lipid Storage DiseaseChina, United States, France, Austria, Germany, Italy, Japan, Netherlands, United Kingdom
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Bioray LaboratoriesXiangya Hospital of Central South University; First Affiliated Hospital of... and other collaboratorsEnrolling by invitation
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Shanghai Public Health Clinical CenterMerck Sharp & Dohme LLCUnknownHIV Infection | Hemophilia AChina
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AkesoNot yet recruiting
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Second Affiliated Hospital, School of Medicine,...RecruitingHereditary AtaxiaChina
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Qianfoshan HospitalNot yet recruiting
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General Hospital of Chinese Armed Police ForcesUnknownHereditary Cerebellar Ataxia.China
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Reistone Biopharma Company LimitedActive, not recruiting
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Reproductive & Genetic Hospital of CITIC-XiangyaCompletedThalassemia,Embryonic Development,Reproductive Sterility and InfertilityChina
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SanofiRecruitingOsteochondrodysplasiaAustralia, Spain, Korea, Republic of, China, Italy
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Keymed Biosciences Co.LtdCompletedModerate-to-severe Atopic DermatitisChina
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Shenzhen Geno-Immune Medical InstituteUnknown
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Guang'anmen Hospital of China Academy of Chinese...Unknown
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Zenas BioPharma (USA), LLCActive, not recruiting
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Kaifeng Pharmaceutical (Group) Co., Ltd.Beijing Furen Biomedical Research Institute Co., Ltd.Unknown
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Shanghai Pulmonary Hospital, Shanghai, ChinaRecruitingCystic Fibrosis, PulmonaryChina
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Dermavant Sciences GmbHCompleted
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Guangzhou Women and Children's Medical CenterRecruitingPregnancy | Intrauterine Growth Restriction | Fetal Anomaly | Chromosomal AnomaliesChina
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Otsuka Beijing Research InstituteCompletedTourette SyndromeChina
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Eli Lilly and CompanyCompletedSkin Diseases | Skin Diseases, Genetic | Dermatitis | Eczema | Dermatitis, AtopicJapan
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Jiangsu Gensciences lnc.Completed
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Chia Tai Tianqing Pharmaceutical Group Co., Ltd.Unknown
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BayerCompleted
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Shenzhen Ausa Pharmed Co.,LtdPeking University First Hospital; China Medical University, China; Fudan University and other collaboratorsUnknownEssential HypertensionChina
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Ning Wang, MD., PhD.Recruiting
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Beijing Children's HospitalUnknownKallmann Syndrome | Hypogonadotropic HypogonadismChina
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Peking Union Medical College HospitalUnknown
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Shanghai Jiao Tong University School of MedicineCompletedKallmann Syndrome | Hypogonadotropic HypogonadismChina
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Novartis PharmaceuticalsCompletedTransfusional Hemosiderosis | Transfusional Iron OverloadTaiwan, Turkey, Egypt, United Kingdom, Thailand, Canada, China, Italy, Cyprus, Lebanon, United Arab Emirates