- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Genetic Diseases, Inborn in Ireland
Total 8115 results
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Regeneron PharmaceuticalsTerminated
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Swedish Orphan BiovitrumCerner EnvizaCompletedHemophilia A With InhibitorFrance, Ireland, Italy, Norway, Germany, Kuwait, Saudi Arabia, Switzerland
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ASLAN PharmaceuticalsRecruitingAtopic DermatitisUnited States, Canada
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Queen's University, BelfastCystic Fibrosis FoundationRecruiting
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Mylan Inc.DPT Laboratories, Ltd.CompletedAtopic DermatitisUnited States, Dominican Republic, Honduras
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AmgenCompletedGout | Chronic Uncontrolled Gout | Uncontrolled GoutUnited States
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Daiichi Sankyo, Inc.CompletedAtopic DermatitisUnited States
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ShionogiCompletedAtopic DermatitisUnited States
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PfizerTerminatedMixed HyperlipidemiaUnited States, Canada, Czech Republic, Finland, France, Netherlands
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AstraZenecaCompletedAtopic DermatitisUnited States, Germany, Australia, Spain, United Kingdom, Poland
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Regeneron PharmaceuticalsCompleted
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PfizerCompletedHeterozygous Familial HypercholesterolemiaCanada, Netherlands, United Kingdom, United States, Spain, Poland, Finland, Norway, South Africa, Italy, Bulgaria
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Swedish Orphan BiovitrumIQVIA Pvt. LtdTerminatedHemophilia A | Hemophilia BBulgaria, Croatia, Czechia, France, Hungary, Ireland, Italy, Romania, Slovenia, Spain, United Kingdom
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Eli Lilly and CompanyActive, not recruiting
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Q32 Bio Inc.RecruitingAtopic DermatitisUnited States
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Children's Cancer and Leukaemia GroupUnknown
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Ascendis Pharma A/SActive, not recruitingAchondroplasiaUnited States, Australia, Austria, Denmark, Germany, Ireland, New Zealand, Portugal
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University of UlsterDSM Nutritional Products, Inc.UnknownParticipants With the MTHFR 677TT GenotypeUnited Kingdom
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Novartis PharmaceuticalsTerminatedAtopic DermatitisUnited Kingdom, Germany, Russian Federation, Taiwan, Belgium, Netherlands, Japan, Finland, Slovakia, United States, Iceland, Canada, Poland
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PfizerRecruitingAtopic DermatitisUnited States, Canada
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Daiichi Sankyo, Inc.CompletedAtopic DermatitisUnited States
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Seaside Therapeutics, Inc.TerminatedFragile X SyndromeUnited States
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Ralexar Therapeutics, Inc.CompletedAtopic Dermatitis | Eczema, AtopicUnited States
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Ardea Biosciences, Inc.CompletedGoutUnited States, South Africa, Canada, Belgium, New Zealand, Australia, Germany
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TakedaCompleted
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Ardea Biosciences, Inc.CompletedGoutUnited States, Germany, New Zealand, South Africa, Spain, Canada, Switzerland, Australia, Belgium, Poland, Ukraine
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Regeneron PharmaceuticalsCompletedGoutUnited States, Taiwan, South Africa, India, Germany, Indonesia
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Genzyme, a Sanofi CompanyTerminatedPompe DiseaseUnited States
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Synspira, Inc.TerminatedLung Diseases | Cystic Fibrosis | Pulmonary Disease | Antibiotic Resistant Infection | Respiratory Tract Disease | Cystic Fibrosis Pulmonary Exacerbation | Lung Inflammation | Burkholderia Infections | Lung Infection | Multi-antibiotic Resistance | Pulmonary Inflammation | Lung Infection Pseudomonal | Cystic Fibrosis... and other conditionsUnited Kingdom
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PharmaxisCompletedCystic FibrosisAustralia, New Zealand
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Pfizer's Upjohn has merged with Mylan to form Viatris...CompletedArthritis, GoutyCanada, United States, Spain, Russian Federation, Colombia, Costa Rica, Peru, Taiwan, Korea, Republic of, Mexico, Philippines, Thailand
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Catabasis PharmaceuticalsCompletedMuscular Dystrophy, DuchenneUnited States, Canada, Australia, United Kingdom, Germany, Ireland, Israel, Sweden
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Ardea Biosciences, Inc.CompletedCombination Treatment Study in Subjects With Tophaceous Gout With Lesinurad and Febuxostat (CRYSTAL)Tophaceous GoutPoland, United States, Canada, Australia, New Zealand, Switzerland
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TakedaCompleted
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Incyte CorporationCompletedAtopic DermatitisUnited States, Canada
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Actavis Inc.CompletedAtopic DermatitisUnited States
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Bioverativ, a Sanofi companySwedish Orphan BiovitrumCompletedHemophilia BUnited States, Italy, Ireland, New Zealand, United Kingdom, Australia, Netherlands, Denmark, Poland, Sweden, France
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis I | Scheie Syndrome | Hurler's Syndrome | Hurler-Scheie SyndromeUnited States, Canada, United Kingdom, Brazil, Germany, Italy, Netherlands
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GlaxoSmithKlineCompletedDermatitis, AtopicUnited States, Canada, Japan
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Eli Lilly and CompanyDermira, Inc.CompletedAtopic DermatitisUnited States
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Sarepta Therapeutics, Inc.Active, not recruitingMuscular Dystrophy, DuchenneUnited States, Korea, Republic of, India, Slovenia, Turkey, United Kingdom, Germany, Switzerland, Spain, Czechia, France, Serbia, Taiwan, Netherlands, Mexico, Colombia, Denmark, New Zealand, Norway, Greece, Hungary, Ireland, Italy, Jo... and more
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National Center for Complementary and Integrative...Completed
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Novartis PharmaceuticalsCompletedAcute GoutUnited States, Canada, Russian Federation, Netherlands, China
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Acrotech Biopharma Inc.Active, not recruitingAtopic DermatitisUnited States
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Eli Lilly and CompanyDermira, Inc.CompletedAtopic DermatitisUnited States, Canada, Germany, Poland
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PedNet Haemophilia Research FoundationLund University HospitalRecruitingFactor IX Deficiency | Factor VIII DeficiencyNorway, Austria, Belgium, Canada, Czechia, Denmark, Finland, France, Germany, Greece, Ireland, Israel, Italy, Netherlands, Portugal, Spain, Sweden, Switzerland, United Kingdom
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Dermavant Sciences GmbHCompletedAtopic DermatitisUnited States, Canada
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Eli Lilly and CompanyIncyte CorporationTerminatedAtopic DermatitisUnited States, Puerto Rico, Canada
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States